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Glasdegib

Phase 2

Acute Myelogenous Leukemia (AML) Due to Therapy | Small molecule | Oncology |Jazz Pharmaceuticals plc|Last Updated: Mar 6, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment30
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04231851CPX-351 and Glasdegib for Newly Diagnosed Acute Myelogenous Leukemia With MDS Related Changes or Therapy-related Acute Myeloid LeukemiaPHASE2 ACTIVE NOT_RECRUITING 30Feb 19, 2020Jun 30, 2027Mar 6, 20264 United States
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Study Endpoints
Primary Endpoints
Percentage of Participants With Event-Free Survival at 6 Months
6 months

This is defined as the percentage of subjects with event-free survival (EFS) at 6 months. EFS is defined as the number of months where patients are in a remission state.

Secondary Endpoints
Percentage of Grade 3-5 Adverse Events
From the start date of treatment until 4 weeks after removal of treatment due to disease progression, toxicity, delay of treatment, or withdrawal of treatment, whichever came first, an average of 1 year.
Overall Response Rate
From the start date of treatment until first date of CR/CRi or an average of 1 year.
Durability of Response
From the start date of treatment until first date of CR/CRi or an average of 1 year.
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
CPX-351 and GlasdegibEXPERIMENTALIn Induction, subjects receive 44mg/m2/100mg/m2 IV on days 1, 3 and 5 and Glasdegib 100mg PO daily on days 6 to 28. If re-induction is needed: Subjects receive 44mg/m2/100mg/m2 IV on days 1 and 3 and Glasdegib 100mg PO daily on days 4 to 28. In consolidation: Subjects receive 29mg/m2/65mg/m2 IV on days 1 and 3 and Glasdegib 100mg PO daily on days 4 to 28. If maintenance is required, Subjects receive Glasdegib 100mg PO daily for up to one year
Interventions
NameTypeDescription
GlasdegibDRUGGiven PO
CPX-351DRUGGiven IV
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites4

Inclusion Criteria: * Previously untreated therapy-related AML or AML with myelodysplastic related changes as described by World Health Organization (WHO) 2016 1. AML arising in MDS (including CMML) or MDS/MPN syndrome 2. AML with MDS-related cytogenetic abnormalities (Appendix A, metaphase FI...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 24, 2026NCT04231851studyFirstPostDate: changed