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Brepocitinib

Phase 3

Dermatomyositis | Small molecule | Immunology |Roivant Sciences Ltd.|Last Updated: Aug 27, 2026

Target and mechanism

Molecular targetTYK2, JAK1
Target classInhibitor
ModalitySmall molecule

Also known as Brepocitinib PO QD, Oral Brepocitinib

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials2
Total Enrollment246

FDA Designations

BREAKTHROUGH_THERAPYPRIORITY_REVIEW

Clinical trial landscape

Brepocitinib · 6 trials · 10 indications

Phase 3 2Phase 2 4
NCT06431373A Study of Brepocitinib in Adults With Active, Non-Infectious, Non-Anterior UveitisUveitis, Posterior
ACTIVE NOT_RECRUITING371 Analytics
NCT05437263A Study to Investigate the Efficacy and Safety of Brepocitinib in Adults With DermatomyositisDermatomyositis
ACTIVE NOT_RECRUITING241 Analytics
PHASE3ACTIVE NOT_RECRUITING
A Study of Brepocitinib in Adults With Active, Non-Infectious, Non-Anterior Uveitis
Uveitis, PosteriorUnlock trial analytics
PHASE3ACTIVE NOT_RECRUITING
A Study to Investigate the Efficacy and Safety of Brepocitinib in Adults With Dermatomyositis
DermatomyositisUnlock trial analytics

Study Endpoints

Primary Endpoints

Time to treatment failure on or after Period 1 Week 6 up to Period 1 Week 48
48 weeks
Total Improvement Score (TIS) at Week 52
52 weeks

TIS is a composite endpoint based on improvement in the 6 Disease Activity Core Set Measure (CSM) scores and ranges from 0 to 100 (2016 American College of Rheumatology \[ACR\] Myositis Response Criteria/European League Against Rheumatism \[EULAR\]) where a higher score indicates more improvement

Proportion of participants achieving IGA score 0/1 and ≥ 2-step reduction from baseline at Week 24
Week 24
Part 1: Number of participants with Treatment Emergent Adverse Events and Serious Adverse Events as assessed by CTCAE v5.0
Week 16
Part 2: Proportion of participants achieving a reduction in Cutaneous Sarcoidosis Activity and Morphology Instrument Activity (CSAMI-A) from baseline to Week 16.
16 Weeks
The primary endpoint is the change in CDASI-A score from baseline through Week 12
12 weeks
Incidence of Treatment-emergent Adverse Events (TEAEs) and Serious Adverse Events (SAEs)
Screening up to 28 days after the last dose of study drug at 52 weeks

Safety assessments will consist of monitoring and recording all adverse events (AEs) and SAEs, laboratory evaluation for hematology, blood chemistry, and urinalysis; vital signs; electrocardiograms (ECGs); and physical examinations. The investigator will determine whether the change is clinically meaningful.

Secondary Endpoints

Proportion of participants meeting treatment failure criteria on or after Period 1 Week 6 up to Period 1 Week 24
24 weeks
Change in logMAR BCVA in each eye from best state achieved at or prior to Period 1 Week 6 up to Period 1 Week 24
24 weeks
Change in central subfield thickness from best state achieved in each eye at or prior to Period 1 Week 6 up to Period 1 Week 24
24 weeks
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Arm 1EXPERIMENTAL -
Arm 2PLACEBO_COMPARATOR -
Brepocitinib Dose Level 1 PO QDEXPERIMENTAL -
Brepocitinib Dose Level 2 PO QDEXPERIMENTAL -
Placebo PO QDPLACEBO_COMPARATOR -
Brepocitinib Dose Level 1EXPERIMENTAL -
PlaceboPLACEBO_COMPARATOR -
Part 1: Brepocitinib Dose Level 1EXPERIMENTALOral Brepocitinib
Part 1: Brepocitinib Dose Level 2EXPERIMENTALOral Brepocitinib
Part 1: PlaceboPLACEBO_COMPARATOR -
Part 2: Brepocitinib Dose Level 1EXPERIMENTALOral Brepocitinib
Part 2: PlaceboPLACEBO_COMPARATOR -
BrepocitinibEXPERIMENTAL -
Brepocitinib Dose Level 1 by mouth (PO) once daily (QD)EXPERIMENTAL -
Brepocitinib Dose Level 2 by mouth (PO) once daily (QD)EXPERIMENTAL -

Interventions

NameTypeDescription
Brepocitinib PO QDDRUGBrepocitinib PO QD
Placebo PO QDDRUGPlacebo PO QD
BrepocitinibDRUGOral Brepocitinib
PlaceboDRUGOral Placebo
Oral BrepocitinibDRUGOral
Oral PlaceboDRUGPlacebo
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Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites107

Inclusion Criteria: * Adult subjects (18-75 years old) * Diagnosis of non-infectious uveitis (intermediate uveitis, posterior uveitis, or panuveitis) * Active uveitic disease in at least 1 eye * Weight \> 40 kg with a body mass index ≤ 40 kg/m2 Exclusion Criteria: Has confirmed or suspected curre...

Countries:United StatesArgentinaAustraliaAustriaBelgiumCzechiaGermanyGreeceHungaryIsraelItalySpainUnited KingdomBulgariaCanadaChileMexicoNetherlandsPolandPortugalRomaniaSerbiaSouth KoreaTaiwanTurkey (Türkiye)
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Recent Changes (Last 90 Days)

LOWAug 27, 2026NCT06978725lastUpdatePostDate: changed
LOWAug 27, 2026NCT06978725lastUpdatePostDate: changed
MEDIUMAug 21, 2026NCT06978725Enrollment: 28 → 168
MEDIUMAug 21, 2026NCT06978725Enrollment: 28 → 168
LOWJul 17, 2026NCT05437263lastUpdatePostDate: changed
LOWJul 17, 2026NCT05437263lastUpdatePostDate: changed
LOWJul 8, 2026NCT07532603lastUpdatePostDate: changed
LOWJul 8, 2026NCT07532603lastUpdatePostDate: changed

Frequently asked questions about Brepocitinib

What is Brepocitinib used for?

Brepocitinib is an investigational oral small molecule being studied for dermatomyositis, lichen planopilaris, posterior uveitis, cutaneous sarcoidosis, and non-infectious intermediate uveitis. It is in clinical development for these immunology indications, with active trials in dermatomyositis, uveitis, and cutaneous sarcoidosis.

What does Brepocitinib target?

Brepocitinib targets TYK2 and JAK1, acting as an inhibitor of these kinases. By inhibiting TYK2 and JAK1, it is designed to modulate signaling pathways involved in inflammatory and autoimmune conditions.

Who makes Brepocitinib?

Brepocitinib is being developed by Roivant Sciences Ltd., a biopharmaceutical company traded under the ticker ROIV. The company is conducting clinical trials to evaluate the drug's safety and efficacy across multiple immunology indications.

What phase is Brepocitinib in?

Brepocitinib is in Phase 2 and Phase 3 clinical development. It has received FDA Breakthrough Therapy designation and Priority Review designation, though it remains investigational and is not yet approved. Active trials include Phase 3 studies in dermatomyositis and uveitis.

What clinical trials is Brepocitinib in?

Brepocitinib is being studied in several trials, including NCT05437263 for dermatomyositis (Phase 3, active), NCT06431373 for non-infectious non-anterior uveitis (Phase 3, active), NCT06433999 for skin-predominant dermatomyositis (Phase 2, completed), and NCT06978725 for cutaneous sarcoidosis (Phase 2, recruiting).

Is Brepocitinib the same as Oral Brepocitinib?

Yes, Brepocitinib is also known as Brepocitinib PO QD and Oral Brepocitinib. These names refer to the same drug, which is administered orally once daily in clinical trials.