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Brepocitinib

Phase 3

Dermatomyositis | Small molecule | Other |Roivant Sciences Ltd.|Last Updated: Sep 29, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials2
Total Enrollment246
FDA Designations
BREAKTHROUGH_THERAPYPRIORITY_REVIEW
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05437263A Study to Investigate the Efficacy and Safety of Brepocitinib in Adults With DermatomyositisPHASE3 ACTIVE NOT_RECRUITING 241Oct 31, 2022Jul 1, 2026Sep 29, 2025109 United States, Argentina +20
NCT06433999A 12-Week Open-Label Study to Investigate the Efficacy and Safety of Brepocitinib in Adults With Skin-Predominant DermatomyositisPHASE2 COMPLETED 5Aug 28, 2024Feb 28, 2025May 20, 20251 United States
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Study Endpoints
Primary Endpoints
Total Improvement Score (TIS) at Week 52
52 weeks

TIS is a composite endpoint based on improvement in the 6 Disease Activity Core Set Measure (CSM) scores and ranges from 0 to 100 (2016 American College of Rheumatology \[ACR\] Myositis Response Criteria/European League Against Rheumatism \[EULAR\]) where a higher score indicates more improvement

The primary endpoint is the change in CDASI-A score from baseline through Week 12
12 weeks
Secondary Endpoints
Change from baseline in Cutaneous Dermatomyositis Disease Area and Severity Index (CDASI) Activity Score at Week 52
52 weeks
Dermatomyositis Outcomes for Muscle and Skin (DMOMS) at Week 52
52 weeks
The proportion of participants achieving TIS ≥ 40 points (moderate improvement) at Week 52
52 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Brepocitinib Dose Level 1 PO QDEXPERIMENTAL -
Brepocitinib Dose Level 2 PO QDEXPERIMENTAL -
Placebo PO QDPLACEBO_COMPARATOR -
BrepocitinibEXPERIMENTAL -
Interventions
NameTypeDescription
BrepocitinibDRUGOral Brepocitinib
PlaceboDRUGOral Placebo
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Eligibility Criteria
Age Range18 Years — 75 Years
SexALL
Healthy VolunteersNo
Study Sites109

Inclusion Criteria: * A diagnosis of dermatomyositis according to 2017 EULAR/ACR Classification Criteria for Idiopathic Inflammatory Myopathies * Adult subjects (18-75 years old) * Active muscle and skin disease at screening and baseline * Prior therapy OR current therapy with corticosteroids, hydr...

Countries:United StatesArgentinaBelgiumBulgariaCanadaChileCzechiaGermanyHungaryIsraelItalyMexicoNetherlandsPolandPortugalRomaniaSerbiaSouth KoreaSpainTaiwanTurkey (Türkiye)United Kingdom
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT05437263primaryCompletionDate: changed
LOWMay 24, 2026NCT05437263studyFirstPostDate: changed