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Decartes-08

Phase 3

Myasthaenia Gravis | Monoclonal antibody | Other |Cartesian Therapeutics, Inc.|Last Updated: Mar 24, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment100
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT06799247Investigating an mRNA CAR T-cell Therapy, Known as Descartes-08, as a Potential Approach to Treat Myasthenia GravisPHASE3 RECRUITING 100May 6, 2025Sep 30, 2027Mar 24, 202634 United States, Canada +6
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Study Endpoints
Primary Endpoints
Myasthenia Gravis Activities of Daily Living (MG-ADL)
assessment at 4 months of study

To evaluate the efficacy of Descartes-08 as assessed by the proportion of Myasthenia Gravis Activities of Daily Living (MG-ADL) responders at Month 4.

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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelCROSSOVER
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Decartes-08EXPERIMENTALThis group will undergo leukapheresis and receive manufactured Decartes-08
PlaceboPLACEBO_COMPARATORThis group will receive placebo
Interventions
NameTypeDescription
Decartes-08BIOLOGICALAutologous mRNA CAR T-cell therapy
Placebo DrugOTHERinfusion without Decartes-08
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites34

Inclusion Criteria: * Patient must be at least 18 years of age. * Patient must have generalized myasthenia gravis (gMG), Myasthenia Gravis Foundation of America (MGFA) clinical classification grades 2-4 at the time of Sscreening. * MG-Activities of Daily Living (MG ADL) total score ≥ 6. * Concomita...

Countries:United StatesCanadaItalyPolandSerbiaSpainTurkey (Türkiye)United Kingdom
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT06799247primaryCompletionDate: changed
LOWMay 24, 2026NCT06799247studyFirstPostDate: changed