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Trastuzumab

Phase 2

Brain Metastases | Small molecule | Oncology |Pfizer, Inc.|Last Updated: Jul 20, 2026

Target and mechanism

Molecular targetERBB2
Target classInhibitor
ModalitySmall molecule

Also known as Herceptin®, Herceptin

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment48

FDA Designations

No designations recorded

Clinical trial landscape

Trastuzumab · 5 trials · 6 indications

Phase 2 4Phase 1 1
NCT05323955Secondary BRain Metastases Prevention After Isolated Intracranial Progression on Trastuzumab/Pertuzumab or T-DM1 in Patients With aDvanced Human Epidermal Growth Factor Receptor 2+ brEast Cancer With the Addition of TucatinibBrain Metastases
ACTIVE NOT_RECRUITING48 Analytics
NCT03414658The AVIATOR Study: Trastuzumab and Vinorelbine With Avelumab OR Avelumab & Utomilumab in Advanced HER2+ Breast CancerBreast Cancer
ACTIVE NOT_RECRUITING100 Analytics
NCT03043313Tucatinib Plus Trastuzumab in Patients With HER2+ Colorectal CancerMetastatic Colorectal Adenocarcinoma
COMPLETED117 Analytics
NCT00043394CPG 7909 Plus Herceptin® In Patients With Metastatic Breast CancerCarcinoma, Breast
COMPLETED16 Analytics
PHASE2ACTIVE NOT_RECRUITING
Secondary BRain Metastases Prevention After Isolated Intracranial Progression on Trastuzumab/Pertuzumab or T-DM1 in Patients With aDvanced Human Epidermal Growth Factor Receptor 2+ brEast Cancer With the Addition of Tucatinib
Brain MetastasesUnlock trial analytics
PHASE2ACTIVE NOT_RECRUITING
The AVIATOR Study: Trastuzumab and Vinorelbine With Avelumab OR Avelumab & Utomilumab in Advanced HER2+ Breast Cancer
Breast CancerUnlock trial analytics
PHASE2COMPLETED
Tucatinib Plus Trastuzumab in Patients With HER2+ Colorectal Cancer
Metastatic Colorectal AdenocarcinomaUnlock trial analytics
PHASE2COMPLETED
CPG 7909 Plus Herceptin® In Patients With Metastatic Breast Cancer
Carcinoma, BreastUnlock trial analytics

Study Endpoints

Primary Endpoints

Progression Free Survival (PFS)
3 years

Evaluate the ability of tucatinib in combination with trastuzumab/pertuzumab or TDM-1 to prolong intracranial progression free survival (PFS) in patients compared to historical controls. PFS is defined as the time from the day of study treatment initiation until evidence of intracranial disease progression per RANO-BM or death from any cause.

Progression Free Survival
2 years

Progression Free Survival is defined from the time from randomization to the first occurrence of disease progression as determined by the investigator using RECIST 1.1 or death from any cause, whichever occurs first.

Confirmed Objective Response Rate (cORR) Per RECIST v1.1 Per Blinded Independent Central Review (BICR) in Pooled Cohorts A+B
Up to 46.6 months

cORR was defined as the percentage of participants with confirmed CR or PR according to RECIST v1.1. CR was defined as the disappearance of all target lesions and each target lymph node must have reduction in short axis to less than (\<)1.0 centimeter (cm). PR was defined as at least a 30 percentage (%) decrease in post-baseline sum of the diameters (sum of the longest diameter for all target lesions plus the sum of the short axis of all the target lymph nodes at current evaluation) taking as reference the baseline sum of diameters.

Phase I: To evaluate the safety and tolerability of several dose levels of CPG 7909 (up to a maximum of 0.16 mg/kg) and to determine the maximum tolerated dose (MTD)* of CPG 7909 in combination with Herceptin®
24 weeks
Phase II: To evaluate tumor response and safety of CPG 7909 (at the MTD as determined in Phase I) in combination with Herceptin® in patients with metastatic breast cancer.
24 weeks
Number of Participants With Treatment-Emergent Adverse Events (AEs) or Serious Adverse Events (SAEs)
From screening until 28 days post last dose of study drug

An AE was any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship. A SAE was an AE resulting in any of following outcomes or deemed significant for any other reason: death; initial or prolonged inpatient hospitalization; life-threatening experience (immediate risk of dying); persistent or significant disability/incapacity; congenital anomaly. Treatment-emergent are events between first dose of study drug and up to 28 days after last dose that were absent before treatment or that worsened relative to pretreatment state.

Secondary Endpoints

Progression Free Survival by RECIST 1.1
3 years
Progression Free Survival of Extracranial Disease
3 years
Distant Versus Local Intracranial Progression Free Survival
3 years
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Experimental GroupEXPERIMENTALTrastuzumab/pertuzumab + tucatinib or T-DM1 + tucatinib 300mg of tucatinib taken orally twice a day. Taken on Days 1-21 of a 21 Day cycle (3 Weeks). Trastuzumab/Biosimilar administered per current package insert based on site standard of care guidelines Pertuzumab or Biosimilar administered per current package insert based on site standard of care guidelines Trastuzumab Emtansine (T-DM1) administered per current package insert based on site standard of care guidelines
NH: Trastuzumab + VinorelbineEXPERIMENTAL* Trastuzumab is administered intravenously twice per cycle * Vinorelbine is administered intravenously 3 times per cycle
NHA: Trastuzumab + Vinorelbine + AvelumabEXPERIMENTAL* Trastuzumab is administered intravenously twice per cycle * Vinorelbine is administered intravenously 3 times per cycle * Avelumab is administered intravenously twice per cycle * Antihistamine and with acetaminophen is mandatory 30 to 60 minutes prior to each dose of avelumab
NHAU: Trastuzumab + Vinorelbine + Avelumab + UtomilumabEXPERIMENTAL* Trastuzumab is administered intravenously twice per cycle * Vinorelbine is administered intravenously 3 times per cycle * Avelumab is administered intravenously twice per cycle * Antihistamine and with acetaminophen is mandatory 30 to 60 minutes prior to each dose of avelumab * Utomilumab is administered intravenously once per cycle
Cohort A: Tucatinib + TrastuzumabEXPERIMENTALNon-randomized cohort. Participants take tucatinib twice per day orally on Days 1-21 and trastuzumab intravenously (into the vein; IV) on Day 1. Cycles repeat every 21 days.
Cohort B: Tucatinib + TrastuzumabEXPERIMENTALRandomized cohort. Participants take tucatinib twice per day orally on Days 1-21 and trastuzumab intravenously (into the vein; IV) on Day 1. Cycles repeat every 21 days.
Cohort C: Tucatinib MonotherapyEXPERIMENTALRandomized cohort. Participants take tucatinib twice per orally every day. Participants who do not respond to therapy may have the option to receive tucatinib and trastuzumab.
Cohort 1EXPERIMENTAL0.04 mg/kg CpG 7909
Cohort 2EXPERIMENTAL0.08 mg/kg CpG 7909
Cohort 3EXPERIMENTAL0.12 mg/kg CpG 7909 Injection once weekly
Cohort 4EXPERIMENTAL0.16 mg/kg CpG 7909
1EXPERIMENTALCombination of SU011248 (37.5 mg once daily \[Schedule 2/1\]) with docetaxel (75 mg/m2 every 3 weeks) and trastuzumab (therapeutic dose)

Interventions

NameTypeDescription
TrastuzumabDRUGAdminister per current package insert based on site standard of care guidelines
Trastuzumab Emtansine (T-DM1)DRUGAdminister per current package insert based on site standard of care guidelines
PertuzumabDRUGAdminister per current package insert based on site standard of care guidelines
TucatinibDRUG300 mg orally twice daily (21 Day Cycle)
VinorelbineDRUGwork by interfering with cell division, which leaves the tumor unable to grow and spread
AvelumabDRUGmonoclonal antibody directed against the human immunosuppressive ligand programmed death-ligand 1 (PD-L1) protein
UtomilumabDRUGUtomilumab is an antibody designed to stimulate the body's immune system to fight cancer cells
0.04 mg/kg CpG 7909DRUG0.04 mg/kg CpG 7909 by subcutaneous Injection once weekly until progression or 24 weeks
Herceptin®DRUGHerceptin® (maintenance dose per the manufacturer's directions) followed by a subcutaneous injection of CpG 7909.
0.08 mg/kg CpG 7909DRUG0.08 mg/kg CpG 7909 by subcutaneous Injection once weekly until progression or 24 weeks
0.12 mg/kg CpG 7909DRUG0.12 mg/kg CpG 7909 by subcutaneous Injection once weekly until progression or 24 weeks
0.16 mg/kg CpG 7909DRUG0.16 mg/kg CpG 7909 by subcutaneous Injection once weekly until progression or 24 weeks
HerceptinDRUGTrastuzumab will be administered intravenously on Day 1 before docetaxel - loading dose of 4 mg/kg over 90-minute on Day 1 followed by weekly maintenance doses of 2 mg/kg on Days 1, 8, 15 given as 30-minute infusions if the initial loading dose was well tolerated. Loading dose of 8 mg/kg over 90-minute on Day 1 followed by 3-weekly maintenance doses of 6 mg/kg given as 90-minute infusions. The administration of 6 mg/kg will be repeated on Day 1 every 3 weeks.
SunitinibDRUGSU011248 will be administered at 37.5 mg once daily for 2 weeks every 3 weeks (Schedule 2/1) starting from Day 2, when in combination with docetaxel. SU011248 will be administered at the starting dose of 37.5 mg daily in a continuous regimen when docetaxel is discontinued.
TaxotereDRUGThe starting dose of docetaxel will be 75 mg/m2 every 3 weeks, administered on Day 1 of each cycle as a 1-hour IV infusion.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites8

Inclusion Criteria: Subject must meet all of the following applicable inclusion criteria to participate in this study: * Written informed consent and HIPAA authorization for release of personal health information prior to registration. NOTE: HIPAA authorization may be included in the informed cons...

Countries:United StatesBelgiumFranceItalySpain
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Frequently asked questions about Trastuzumab

What is Herceptin used for?

Herceptin is used for breast cancer, specifically carcinoma of the breast. It is being studied in patients with metastatic breast cancer and in those with HER-2 positive advanced breast cancer. The drug is in clinical development for these oncology indications.

What does Herceptin target?

Herceptin targets ERBB2, also known as HER2, and acts as an inhibitor of this molecular target. By inhibiting ERBB2, the drug is designed to interfere with signaling pathways that can drive cancer cell growth in breast cancer.

Who makes Herceptin?

Herceptin is developed by Pfizer, Inc., which trades under the ticker symbol PFE on the stock exchange. Pfizer is the company responsible for the clinical development of this drug for breast cancer indications.

What phase is Herceptin in?

Herceptin is in Phase 1 clinical development. It has completed one Phase 1 trial and one Phase 2 trial, but the current development stage is Phase 1. Herceptin is investigational and has not been approved by regulatory authorities.

What clinical trials is Herceptin in?

Herceptin has been studied in two completed clinical trials. NCT00043394 was a Phase 2 study of CPG 7909 plus Herceptin in patients with metastatic breast cancer. NCT00372424 was a Phase 1 study of SU011248 in combination with docetaxel and trastuzumab in patients with HER-2 positive advanced breast cancer.

Is Herceptin the same as Trastuzumab?

Yes, Herceptin is also known as Trastuzumab. The drug is sometimes referred to by its generic name, trastuzumab, and is also studied in combination products such as Trastuzumab plus Pertuzumab. These names refer to the same therapeutic agent.