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Recombinant Coagulation Factor IX

Phase 3

Hemophilia B | Small molecule | Hematology |Pfizer, Inc.|Last Updated: Oct 4, 2011

Success Probability

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Market & Valuation

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Trial Design

RandomizedCONTROLLED
Total Trials1
Total Enrollment50

FDA Designations

No designations recorded

Clinical trial landscape

Recombinant Coagulation Factor IX · 1 trial · 1 indication

Phase 3 1
NCT00364182Study Comparing On-Demand Treatment With Two Prophylaxis Regimens Of BeneFIX In Patients With Severe Hemophilia BHemophilia B
COMPLETED50 Analytics
PHASE3COMPLETED
Study Comparing On-Demand Treatment With Two Prophylaxis Regimens Of BeneFIX In Patients With Severe Hemophilia B
Hemophilia BUnlock trial analytics

Study Endpoints

Primary Endpoints

Annualized Number of Bleeding Episodes
Baseline up to Week 56

Annualized bleed rate (ABR) or number of bleeds per year derived for each participant for each treatment regimen by using the following formula: ABR = number of bleeds / (days on treatment regimen / 365.25)

Secondary Endpoints

Amount of Sleep Measured by Sleep Diary After Hemarthrosis
24 and 48 hours post-bleed
Quality of Sleep Measured by Sleep Diary After Hemarthrosis
24 and 48 hours post-bleed
Acute Pain After Hemarthrosis
24 and 48 hours post-bleed
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelCROSSOVER
PurposePREVENTION

Treatment Arms

ArmTypeDescription
AEXPERIMENTAL -
BEXPERIMENTAL -

Interventions

NameTypeDescription
Recombinant Coagulation Factor IX (BeneFIX)DRUG100 IU/kg once weekly then crossover to 50 IU/kg twice weekly
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Eligibility Criteria

Age Range6 Years to 65 Years
SexMALE
Healthy VolunteersNo
Study Sites19

Inclusion Criteria: * Documented history of moderately severe or severe hemophilia B (FIX:C less than or equal to 2%) * Male subjects, aged 6 years to 65 years. * Subjects with a minimum of 12 bleeding episodes, 6 of which must be joint bleeds, in the 12 months before screening. Exclusion Criteria...

Countries:United StatesCanadaCroatiaHungaryItalyRomaniaRussiaSerbiaSpain
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Frequently asked questions about Recombinant Coagulation Factor IX

What is Recombinant Coagulation Factor IX used for in Hemophilia B?

Recombinant Coagulation Factor IX is used for the treatment of Hemophilia B, a bleeding disorder. It is being studied in patients with severe Hemophilia B to compare on-demand treatment with two prophylaxis regimens. The drug is currently in Phase 3 clinical development and is being developed by Pfizer, Inc.

What does Recombinant Coagulation Factor IX target?

Recombinant Coagulation Factor IX targets and replaces the missing or deficient clotting factor IX in patients with Hemophilia B. By providing the functional factor IX protein, it helps restore the blood's ability to clot properly, reducing the risk of bleeding episodes in affected individuals.

Who makes Recombinant Coagulation Factor IX?

Recombinant Coagulation Factor IX is being developed by Pfizer, Inc., a biopharmaceutical company listed on the New York Stock Exchange under the ticker symbol PFE. The drug is currently in Phase 3 clinical trials for the treatment of Hemophilia B.

What phase is Recombinant Coagulation Factor IX in?

Recombinant Coagulation Factor IX is in Phase 3 clinical development. It is an investigational drug, meaning it has not yet been approved by regulatory authorities. The ongoing Phase 3 trial is studying its use in patients with severe Hemophilia B, comparing on-demand treatment with two prophylaxis regimens.

What clinical trials is Recombinant Coagulation Factor IX in?

Recombinant Coagulation Factor IX is being studied in a Phase 3 clinical trial with the identifier NCT00364182. This completed trial enrolled 50 male patients with severe Hemophilia B and compared on-demand treatment with two prophylaxis regimens. The study was conducted in multiple countries, including the United States, Canada, and several European nations.