Recent Updates
Recently added Catalysts

Ruxolitinib continuous therapy

Phase 2

Bone Marrow Fibrosis | Small molecule | Musculoskeletal |Novartis AG|Last Updated: Mar 30, 2025

Target and mechanism

Molecular targetJAK1, TYK2, JAK2, JAK3
Target classInhibitor
ModalitySmall molecule

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

ACTIVE_CONTROLLEDDMC
Total Trials1
Total Enrollment87

FDA Designations

No designations recorded

Clinical trial landscape

Ruxolitinib continuous therapy · 1 trial · 1 indication

Phase 2 1
NCT03333187Ruxolitinib vs Allogeneic SCT for Patients With Myelofibrosis According to Donor AvailabilityBone Marrow Fibrosis
ACTIVE NOT_RECRUITING87 Analytics
PHASE2ACTIVE NOT_RECRUITING
Ruxolitinib vs Allogeneic SCT for Patients With Myelofibrosis According to Donor Availability
Bone Marrow FibrosisUnlock trial analytics

Study Endpoints

Primary Endpoints

Event free survival
3 years

Compare to event free survival of patients at 3 years after allogeneic SCT and in Ruxolitinib continuous therapy in patients without a suitable donor

Secondary Endpoints

Spleen reduction
3 months
Improvement of constitutional symptoms
3 months
Improvement of bone marrow fibrosis
3 months
Unlock Study Endpoints

Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Arm AEXPERIMENTALTreatment with Allogeneic Stem cell Transplantation after 3 months of Ruxolitinib induction therapy
Arm BACTIVE_COMPARATORTreatment with Ruxolitinib continuous therapy

Interventions

NameTypeDescription
Allogeneic stem cell transplantationPROCEDURE -
Ruxolitinib continuous therapyDRUG -
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to 70 Years
SexALL
Healthy VolunteersNo
Study Sites14

Inclusion Criteria: 1. Symptomatic primary myelofibrosis or myelofibrosis post polycythaemia vera or essential thrombocythemia stage intermediate 2- or high-risk according to IPSS or DIPSS \[46\] or intermediate 1-risk with high risk cytogenetics, other than normal karyotype, sole del 20q, del 13q,...

Countries:Germany
Unlock Eligibility Criteria

Frequently asked questions about Ruxolitinib continuous therapy

What is Ruxolitinib continuous therapy used for?

Ruxolitinib continuous therapy is used for bone marrow fibrosis, a condition also known as myelofibrosis. It is being studied as a treatment option for patients with this disease, with the goal of managing symptoms and potentially improving outcomes.

Who makes Ruxolitinib continuous therapy?

Ruxolitinib continuous therapy is being developed by Novartis AG, a global healthcare company. Novartis is conducting clinical trials to evaluate the safety and efficacy of this treatment for bone marrow fibrosis.

What phase is Ruxolitinib continuous therapy in?

Ruxolitinib continuous therapy is currently in Phase 2 clinical development. It is an investigational drug, meaning it has not yet been approved by regulatory authorities and is still being studied in clinical trials to determine its safety and effectiveness.

What clinical trials is Ruxolitinib continuous therapy in?

Ruxolitinib continuous therapy is being evaluated in a Phase 2 clinical trial with the identifier NCT03333187. This trial is comparing ruxolitinib continuous therapy to allogeneic stem cell transplantation in patients with myelofibrosis, based on donor availability. The study is active but not recruiting participants.

How does Ruxolitinib continuous therapy work?

Ruxolitinib continuous therapy works by targeting kinases, as it belongs to the -tinib class of kinase inhibitors. By inhibiting these enzymes, it aims to reduce the abnormal cell signaling that drives bone marrow fibrosis, potentially slowing disease progression and alleviating symptoms.

Is Ruxolitinib continuous therapy the same as ruxolitinib?

Ruxolitinib continuous therapy is a specific treatment regimen involving ruxolitinib, a JAK inhibitor. While the active ingredient is ruxolitinib, the continuous therapy approach refers to its ongoing administration, as opposed to intermittent dosing. This regimen is being studied specifically for bone marrow fibrosis.