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NNC126-0083

Phase 2

Growth Hormone Disorder | Small molecule | Endocrine |Novo Nordisk A/S|Last Updated: Feb 9, 2017

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindCONTROLLEDBiomarker
Total Trials4
Total Enrollment160
FDA Designations
No designations recorded
Clinical Trials (4)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00936403A Single Dose Trial in Growth Hormone Deficient Children Investigating Safety, Pharmacokinetics and Pharmacodynamics of Long Acting Growth HormonePHASE2 COMPLETED 31Aug 1, 2009Jul 1, 2010Feb 8, 201721 Belgium, Czechia +8
NCT00715689Dose Study in Growth Hormone Deficient Adults Investigating Safety, Pharmacokinetics and Pharmacodynamics of NNC126-0083PHASE2 COMPLETED 33Jul 1, 2008Mar 1, 2009Feb 8, 20173 Denmark
NCT00722540Dose Study in Healthy Japanese Males Investigating Safety, Pharmacokinetics and Pharmacodynamics of NNC126-0083PHASE1 COMPLETED 40Jul 1, 2008Apr 1, 2009Feb 8, 20171 Germany
NCT01034202Dose Study in Healthy Males Investigating Safety, Pharmacokinetics and Pharmacodynamics of NNC126-0083 Compared to Norditropin® SimpleXx®PHASE1 COMPLETED 56Aug 1, 2007Jan 1, 2008Feb 9, 20171 Denmark
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Study Endpoints
Primary Endpoints
Frequency of Adverse events (AEs)
0-10 days after dosing
Safety and tolerability (adverse events, local tolerability, physical examination)
0 to 10 days after third dosing, (day 15-25 after first dose)
Number of adverse events
after administration of a single dose of NNC126-0083
Secondary Endpoints
AUC (0-168h), the area under the plasma NNC126-0083 profile in the interval 0-168 hours after trial product administration
Measured 10 days after dosing
IGF-I AUC (0-168h) the area under IGF-I profile in the interval 0-168 hours after trial product administration
Measured 10 days after dosing
Cmax, maximum concentration of IGF-I
after trial product administration
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
NNC126-0083EXPERIMENTAL -
Norditropin NordiFlex®ACTIVE_COMPARATOR -
AEXPERIMENTAL -
BEXPERIMENTAL -
CEXPERIMENTAL -
DEXPERIMENTAL -
EEXPERIMENTAL -
Norditropin® SimpleXx® 0.02 mg/kg + NNC126-0083EXPERIMENTAL -
Norditropin® SimpleXx® 0.04 mg/kg + NNC126-0083EXPERIMENTAL -
Norditropin® SimpleXx® 0.02 mg/kg + placeboPLACEBO_COMPARATOR -
Norditropin® SimpleXx® 0.04 mg/kg + placeboPLACEBO_COMPARATOR -
PlaceboPLACEBO_COMPARATOR -
Interventions
NameTypeDescription
NNC126-0083DRUGOne single dose administered in four dose levels in an escalating order
somatropinDRUGA daily dose of Norditropin NordiFlex® for seven days. Dose will remain constant
placeboDRUGDose level 1; NNC126-0083 placebo for s.c. injection once weekly for 3 weeks
Norditropin® SimpleXx®DRUGOne of two dose levels, followed by NNC126-0083, administered subcutaneously (under the skin)
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Eligibility Criteria
Age Range6 Years — 12 Years
SexALL
Healthy VolunteersNo
Study Sites21

Inclusion Criteria: * Confirmed diagnosis of growth hormone insufficiency as defined by two different GH provocation tests, defined as a peak of GH level less than 7ng/ml * Pre-pubertal children * Growth hormone replacement treatment for at least three months Exclusion Criteria: * Evidence of tum...

Countries:BelgiumCzechiaDenmarkFranceIsraelNorth MacedoniaSloveniaSpainTurkey (Türkiye)United KingdomGermany
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