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AK-antiVEGF

Phase 1

Vestibular Schwannoma | Gene therapy | Oncology |Eli Lilly and Company|Last Updated: Apr 6, 2026

Target and mechanism

ModalityGene therapy

Also known as AAVAnc80-antiVEGF via Akouos Delivery Device

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment27

FDA Designations

No designations recorded

Clinical trial landscape

AK-antiVEGF · 1 trial · 1 indication

Phase 1 1
NCT06517888Anti-VEGF Gene Therapy Trial for Vestibular SchwannomaVestibular Schwannoma
RECRUITING27 Analytics
PHASE1RECRUITING
Anti-VEGF Gene Therapy Trial for Vestibular Schwannoma
Vestibular SchwannomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Frequency of Adverse Events (AEs)
through trial completion, approximately one year

AEs with relationship to the investigational medicinal product and/or to the administration procedure (including the delivery device)

Secondary Endpoints

Tumor Volume
through trial completion, approximately one year
Performance of Akouos Delivery Device
through trial completion, approximately one year
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Cohort 1EXPERIMENTALAdult participants to receive a single unilateral intracochlear administration of AAVAnc80-antiVEGF (dose level 1) in the study ear using a sterile, one-time use investigational medical device.
Cohort 2EXPERIMENTALAdult participants to receive a single unilateral intracochlear administration of AAVAnc80-antiVEGF (dose level 2) in the study ear using a sterile, one-time use investigational medical device.
Cohort 3EXPERIMENTALAdult participants to receive a single unilateral intracochlear administration of AAVAnc80-antiVEGF (dose level 3) in the study ear using a sterile, one-time use investigational medical device

Interventions

NameTypeDescription
AAVAnc80-antiVEGF via Akouos Delivery DeviceCOMBINATION_PRODUCTAAVAnc80-antiVEGF is a sterile suspension intended to be administered via intracochlear administration as a single dose using the Akouos Delivery Device
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites4

Criteria for Inclusion: 1. Presence of unilateral, progressive vestibular schwannoma. 2. Vestibular schwannoma larger than 2 mm. 3. Profound hearing loss, defined by pure-tone audiometry thresholds or word recognition score, in the affected ear. 4. Able and willing to comply with all trial requirem...

Countries:United States
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