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AAVAnc80-antiVEGF via Akouos Delivery Device

Phase 1

Vestibular Schwannoma | Gene therapy | Oncology |Eli Lilly and Company|Last Updated: Apr 6, 2026

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment27

FDA Designations

No designations recorded

Clinical trial landscape

AAVAnc80-antiVEGF via Akouos Delivery Device · 1 trial · 1 indication

Phase 1 1
NCT06517888Anti-VEGF Gene Therapy Trial for Vestibular SchwannomaVestibular Schwannoma
RECRUITING27 Analytics
PHASE1RECRUITING
Anti-VEGF Gene Therapy Trial for Vestibular Schwannoma
Vestibular SchwannomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Frequency of Adverse Events (AEs)
through trial completion, approximately one year

AEs with relationship to the investigational medicinal product and/or to the administration procedure (including the delivery device)

Secondary Endpoints

Tumor Volume
through trial completion, approximately one year
Performance of Akouos Delivery Device
through trial completion, approximately one year
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Cohort 1EXPERIMENTALAdult participants to receive a single unilateral intracochlear administration of AAVAnc80-antiVEGF (dose level 1) in the study ear using a sterile, one-time use investigational medical device.
Cohort 2EXPERIMENTALAdult participants to receive a single unilateral intracochlear administration of AAVAnc80-antiVEGF (dose level 2) in the study ear using a sterile, one-time use investigational medical device.
Cohort 3EXPERIMENTALAdult participants to receive a single unilateral intracochlear administration of AAVAnc80-antiVEGF (dose level 3) in the study ear using a sterile, one-time use investigational medical device

Interventions

NameTypeDescription
AAVAnc80-antiVEGF via Akouos Delivery DeviceCOMBINATION_PRODUCTAAVAnc80-antiVEGF is a sterile suspension intended to be administered via intracochlear administration as a single dose using the Akouos Delivery Device
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites4

Criteria for Inclusion: 1. Presence of unilateral, progressive vestibular schwannoma. 2. Vestibular schwannoma larger than 2 mm. 3. Profound hearing loss, defined by pure-tone audiometry thresholds or word recognition score, in the affected ear. 4. Able and willing to comply with all trial requirem...

Countries:United States
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Frequently asked questions about AAVAnc80-antiVEGF via Akouos Delivery Device

What is AAVAnc80-antiVEGF via Akouos Delivery Device used for?

AAVAnc80-antiVEGF via Akouos Delivery Device is an investigational gene therapy being developed for the treatment of vestibular schwannoma, a type of non-cancerous brain tumor. It is currently in Phase 1 clinical development and is not yet approved by regulatory authorities.

How does AAVAnc80-antiVEGF via Akouos Delivery Device work?

AAVAnc80-antiVEGF via Akouos Delivery Device is a gene therapy designed to deliver an anti-VEGF agent to target vestibular schwannoma. The therapy uses an Anc80 adeno-associated viral vector to deliver the anti-VEGF gene, which is intended to inhibit vascular endothelial growth factor and potentially reduce tumor growth.

Who is developing AAVAnc80-antiVEGF via Akouos Delivery Device?

AAVAnc80-antiVEGF via Akouos Delivery Device is being developed by Eli Lilly and Company, a biopharmaceutical company listed on the New York Stock Exchange under the ticker symbol LLY. The therapy is in Phase 1 clinical development for vestibular schwannoma.

What phase is AAVAnc80-antiVEGF via Akouos Delivery Device in?

AAVAnc80-antiVEGF via Akouos Delivery Device is currently in Phase 1 clinical development. It is an investigational gene therapy and has not been approved by the FDA or any other regulatory agency. The therapy is being studied in a Phase 1 clinical trial for vestibular schwannoma.

What clinical trials is AAVAnc80-antiVEGF via Akouos Delivery Device in?

AAVAnc80-antiVEGF via Akouos Delivery Device is being evaluated in one active Phase 1 clinical trial, identified as NCT06517888. This trial is titled 'Anti-VEGF Gene Therapy Trial for Vestibular Schwannoma' and is currently recruiting participants in the United States. The trial is a controlled study with an estimated enrollment of 27 participants.