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macitentan/tadalafil

Phase 3

Pulmonary Arterial Hypertension (PAH) (WHO Group 1 PH) | Small molecule | Cardiovascular |Johnson & Johnson|Last Updated: Dec 19, 2025

Target and mechanism

Molecular targetEDNRB, EDNRA
Target classAntagonist
ModalitySmall molecule

Also known as Macitentan

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLEDDMC
Total Trials1
Total Enrollment187

FDA Designations

No designations recorded

Clinical trial landscape

macitentan/tadalafil · 1 trial · 1 indication

Phase 3 1
NCT03904693Clinical Study to Compare the Efficacy and Safety of Macitentan and Tadalafil Monotherapies With the Corresponding Fixed-dose Combination Therapy in Subjects With Pulmonary Arterial Hypertension (PAH)Pulmonary Arterial Hypertension (PAH) (WHO Group 1 PH)
COMPLETED187 Analytics
PHASE3COMPLETED
Clinical Study to Compare the Efficacy and Safety of Macitentan and Tadalafil Monotherapies With the Corresponding Fixed-dose Combination Therapy in Subjects With Pulmonary Arterial Hypertension (PAH)
Pulmonary Arterial Hypertension (PAH) (WHO Group 1 PH)Unlock trial analytics

Study Endpoints

Primary Endpoints

Change in Pulmonary Vascular Resistance (PVR) Expressed as the Ratio of Geometric Means of End of Double-blind Treatment (EDBT) to Baseline
Baseline, EDBT (up to 16 weeks)

Change in PVR expressed as the ratio of geometric means of EDBT to baseline were reported.

Secondary Endpoints

Change From Baseline to EDBT in 6-minutes Walking Distance (6MWD)
Baseline, EDBT (Week 16)
Change From Baseline in Pulmonary Arterial Hypertension Symptoms and Impact (PAH-SYMPACT) in Cardiopulmonary Symptom Domain Scores to EDBT
Baseline, EDBT (Week 16)
Change From Baseline in Pulmonary Arterial Hypertension Symptoms and Impact (PAH-SYMPACT) in Cardiovascular Symptom Domain Scores to EDBT
Baseline, EDBT (Week 16)
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
FDC therapy + Placebo macitentan + Placebo tadalafilEXPERIMENTALSubjects to receive FDC macitentan/tadalafil (macitentan 10 mg and tadalafil 40 mg) plus matching placebos for the two other study treatments.
Macitentan mono-therapy + Placebo tadalafil + Placebo FDCACTIVE_COMPARATORSubjects to receive macitentan 10 mg plus matching placebos for the two other study treatments.
Tadalafil mono-therapy + Placebo macitentan + Placebo FDCACTIVE_COMPARATORSubjects to receive tadalafil 40 mg (2 x 20 mg) plus matching placebos for the two other study treatments.

Interventions

NameTypeDescription
FDC macitentan/tadalafilDRUGFilm-coated tablet with 10 mg macitentan and 40 mg tadalafil, to be administered orally once daily.
Macitentan 10 mgDRUGFilm-coated tablet with 10 mg macitentan, to be administered orally once daily.
Tadalafil 40 mgDRUGFilm-coated tablet with 40 mg tadalafil (2 x 20 mg tablets), to be administered orally once daily.
Placebo FDCDRUGMatching placebo not containing any active substance but otherwise identical in appearance to the respective active drug tablet, to be administered orally once daily.
Placebo macitentanDRUGMatching placebo not containing any active substance but otherwise identical in appearance to the respective active drug tablet, to be administered orally once daily.
Placebo tadalafilDRUGMatching placebo not containing any active substance but otherwise identical in appearance to the respective active drug tablet, to be administered orally once daily.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites148

Inclusion Criteria: * Signed and dated informed consent form (ICF) * Confirmed diagnosis of symptomatic PAH in WHO FC II or III * Symptomatic PAH belonging to one of the following subgroups of WHO Group 1 pulmonary hypertension: * Idiopathic * Heritable * Drug- or toxin-induced * Associate...

Countries:United StatesAustraliaBrazilBulgariaCanadaChinaCzechiaGermanyHungaryItalyJapanMalaysiaMexicoPolandRussiaSouth AfricaSpainTaiwanTurkey (Türkiye)
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Frequently asked questions about macitentan/tadalafil

What is Macitentan used for?

Macitentan is an investigational small molecule being studied for systemic sclerosis, pulmonary arterial hypertension (PAH, WHO Group 1 PH), congenital heart disease, and heart failure with preserved ejection fraction. It is also used in clinical trials involving healthy subjects. The drug is in Phase 2 development for these indications.

What does Macitentan target?

Macitentan is a small molecule being developed for cardiovascular conditions. It is being studied in patients with pulmonary arterial hypertension and heart failure with preserved ejection fraction. The drug's specific molecular target is not disclosed in the available information.

Who makes Macitentan?

Macitentan is developed by Johnson & Johnson, a company traded on the New York Stock Exchange under the ticker JNJ. The drug is currently in Phase 2 clinical development for cardiovascular indications.

What phase is Macitentan in?

Macitentan is in Phase 2 clinical development. It is an investigational drug and has not been approved by regulatory authorities. The drug is being studied for systemic sclerosis, pulmonary arterial hypertension, congenital heart disease, and heart failure with preserved ejection fraction.

What clinical trials is Macitentan in?

Macitentan has been studied in 10 clinical trials with a total enrollment of 3,395 participants. One trial is active, and nine are completed. Notable trials include NCT04273945, a Phase 3 study of a 75 mg dose in pulmonary arterial hypertension, and NCT03153111, a Phase 2 study in heart failure with preserved ejection fraction.

Is Macitentan the same as Macitentan 10 mg?

Yes, Macitentan is also known as Macitentan 10 mg. This alternative name refers to the 10 mg dosage form of the drug. The drug is being developed by Johnson & Johnson under the ticker JNJ.