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OZ1 transduced cells

Phase 2

HIV-1 | Gene therapy | Infectious Disease |Johnson & Johnson|Last Updated: Dec 12, 2018

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment68

FDA Designations

No designations recorded

Clinical trial landscape

OZ1 transduced cells · 1 trial · 1 indication

Phase 2 1
NCT01177059Long Term Follow-Up Study of Human Immunodeficiency Virus Type 1 (HIV-1) Positive Patients Who Have Received OZ1 Gene Therapy as Part of a Clinical TrialHIV-1
COMPLETED68 Analytics
PHASE2COMPLETED
Long Term Follow-Up Study of Human Immunodeficiency Virus Type 1 (HIV-1) Positive Patients Who Have Received OZ1 Gene Therapy as Part of a Clinical Trial
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Study Endpoints

Primary Endpoints

Percentage of Participants With Clonal Expansion of Cells With a Predominant OZ1 Insertion Site
Approximately up to 15 years

Percentage of participants with clonal expansion of cells with a predominant OZ1 insertion site was reported. A predominant integration site was defined as an integration site which has a density of at least 50 percent (%) of the total signal detected by polymerase chain reaction (PCR), when the percentage of cells marked by vector was greater than (\>)1% of the test cell population.

Percentage of Participants With Insertional Oncogenesis
Approximately up to 15 years

Percentage of participants with insertional oncogenesis by clonal expansion of cells modified with OZ1/LNL6 were reported.

Number of Participants With Quantitative Marking of Gene Transfer Product in Peripheral Blood Mononuclear Cells (PBMC) Over Time
Up to end of study (Approximately up to 15 years)

OZ1 and LNL6 marking analysis were performed by quantitative deoxyribonucleic acid-polymerase chain reaction (DNA-PCR). Number of participants in each of 3 categories for gene detection: Not Detected, Detected (1, 2 and 3 of the 3 triplicates of the sample were detected respectively \[1/3 Detected, 2/3 Detected, 3/3 Detected\]) and Detected (Quantifiable) were reported for marking of gene transfer product in PBMC.

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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeOTHER

Treatment Arms

ArmTypeDescription
Anti-HIV-1 Ribozyme (OZ1) transduced cellsOTHEROZ1 transduced cells Long term follow up of previously infused OZ1 transduced cells

Interventions

NameTypeDescription
OZ1 transduced cellsGENETICLong term follow up of previously infused OZ1 transduced cells
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Eligibility Criteria

SexALL
Healthy VolunteersNo
Study Sites6

Inclusion Criteria: * All patients who were enrolled (between 18 and 45 years of age) in the base study "OTH/OZ1-INT-1" (NCT00074997) will be invited to participate in this long term follow-up study * Patients must have received the Final Cell Product infusion in base study "OTH/OZ1-INT-1" * Have s...

Countries:United StatesAustralia
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Frequently asked questions about OZ1 transduced cells

What is OZ1 transduced cells used for?

OZ1 transduced cells is an investigational gene therapy being studied for the treatment of HIV-1 infection. It is intended for patients who are HIV-1 positive. The therapy is currently in clinical development and has not been approved for commercial use.

Who is developing OZ1 transduced cells?

OZ1 transduced cells is being developed by Johnson & Johnson, a company publicly traded under the ticker symbol JNJ. The therapy is in Phase 2 clinical development for the treatment of HIV-1 infection.

What phase is OZ1 transduced cells in?

OZ1 transduced cells is in Phase 2 clinical development. It is an investigational gene therapy for HIV-1 infection and has not been approved by regulatory authorities. A Phase 2 clinical trial has been completed to evaluate its safety and efficacy.

What clinical trials is OZ1 transduced cells in?

OZ1 transduced cells has been studied in one clinical trial with the identifier NCT01177059. This was a Phase 2, long-term follow-up study in HIV-1 positive patients who had received the gene therapy. The trial was completed and enrolled 68 participants in the United States and Australia.

Is OZ1 transduced cells the same as OZ1?

OZ1 transduced cells is a gene therapy product that involves cells transduced with the OZ1 construct. The clinical trial NCT01177059 refers to the therapy as OZ1 gene therapy. The product is being developed by Johnson & Johnson for HIV-1 infection.