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Mibefradil with Radiation

Phase 1

Glioblastoma Multiforme (GBM) | Small molecule | Oncology |Jazz Pharmaceuticals plc|Last Updated: Jul 24, 2019

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMC
Total Trials1
Total Enrollment18

FDA Designations

No designations recorded

Clinical trial landscape

Mibefradil with Radiation · 1 trial · 1 indication

Phase 1 1
NCT02202993TAU-2014-1: Mibefradil and Hypofractionated Re-Irradiation Therapy in Recurrent GBMGlioblastoma Multiforme (GBM)
COMPLETED18 Analytics
PHASE1COMPLETED
TAU-2014-1: Mibefradil and Hypofractionated Re-Irradiation Therapy in Recurrent GBM
Glioblastoma Multiforme (GBM)Unlock trial analytics

Study Endpoints

Primary Endpoints

Dose limiting toxicities
Monitored continuously, 27 months
Maximum tolerated dose
Monitored continuously, 27 months

Secondary Endpoints

Adverse events
27 months
Mibefradil dihydrochloride steady state plasma concentrations
27 months
Progression-free survival of treated patients
27 months
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Mibefradil with RadiationEXPERIMENTALPatients will receive mibefradil dihydrochloride, which will be dose escalated from 150mg/day until the maximum tolerated dose (MTD) is determined, or until a dose of 350 mg/day is reached using a standard 3 + 3 design. Mibefradil dihydrochloride will be dosed orally in 4 divided doses per day for 17 consecutive days to the MTD. This will be given concurrently with hypofractionated radiation therapy.

Interventions

NameTypeDescription
Mibefradil with RadiationDRUGPatients will receive mibefradil dihydrochloride, which will be dose escalated from 150mg/day until the maximum tolerated dose (MTD) is determined, or until a dose of 350 mg/day is reached using a standard 3 + 3 design. Mibefradil dihydrochloride will be dosed orally in 4 divided doses per day for 17 consecutive days to the MTD. This will be given concurrently with hypofractionated radiation therapy.
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Eligibility Criteria

Age Range18 Years to 80 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Sign written informed consent. * Histologically proven glioblastoma multiforme (GBM) that is progressive or recurrent following standard radiation therapy (RT) and temozolomide (i.e., at least "biopsy-proven" recurrent disease). Previous salvage therapies after first recurrenc...

Countries:United States
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Frequently asked questions about Mibefradil with Radiation

What is Mibefradil with Radiation used for?

Mibefradil with Radiation is an investigational small molecule being studied for use in Glioblastoma Multiforme (GBM), a type of brain cancer. It is being developed by Jazz Pharmaceuticals plc (JAZZ) and is currently in Phase 1 clinical development. The drug has also been studied in healthy volunteers.

Who makes Mibefradil with Radiation?

Mibefradil with Radiation is being developed by Jazz Pharmaceuticals plc, which trades under the ticker symbol JAZZ. The company is conducting clinical trials to evaluate the drug's safety and potential use in treating Glioblastoma Multiforme (GBM).

What phase is Mibefradil with Radiation in?

Mibefradil with Radiation is in Phase 1 clinical development. It is an investigational drug and has not been approved by regulatory authorities. Clinical trials have been completed to assess its safety in healthy volunteers and in patients with Glioblastoma Multiforme (GBM).

What clinical trials is Mibefradil with Radiation in?

Mibefradil with Radiation has been studied in two completed Phase 1 trials. NCT01550458 evaluated the drug given four times a day in 30 healthy volunteers in the United States. NCT02202993 studied mibefradil combined with hypofractionated re-irradiation therapy in 18 patients with recurrent Glioblastoma Multiforme (GBM).

Is Mibefradil with Radiation FDA approved?

Mibefradil with Radiation is not FDA approved. It is an investigational drug currently in Phase 1 clinical development. The completed trials have focused on safety and dosing, and the drug has not yet progressed to later-stage trials or regulatory submission.