Recent Updates
Recently added Catalysts

CPX-315

Phase 2

Acute Myeloid Leukemia | Small molecule | Oncology |Jazz Pharmaceuticals plc|Last Updated: Mar 27, 2026

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedACTIVE_CONTROLLEDBiomarker
Total Trials1
Total Enrollment248

FDA Designations

No designations recorded

Clinical trial landscape

CPX-315 · 1 trial · 1 indication

Phase 2 1
NCT05260528CPX-351 vs Intensive Chemotherapy in Patients With de Novo Intermediate or Adverse Risk AML Stratified by GenomicsAcute Myeloid Leukemia
RECRUITING248 Analytics
PHASE2RECRUITING
CPX-351 vs Intensive Chemotherapy in Patients With de Novo Intermediate or Adverse Risk AML Stratified by Genomics
Acute Myeloid LeukemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Improvement in the proportion of patients achieving deep remission (CR)/(CRi) with a standardized flow based MRD in the BM aspirate using the LAIP/Dfn method after the 1st induction
28-56 days

Secondary Endpoints

Rate of CR/CRi with a flow based MRD in the BM aspirate using the LAIP/Dfn method
28-56 days
Analysis of rate of flow-based MRD quantified in the bone marrow according to both the LAIP/DfN method and the LSC method
10-13 weeks
Analysis of flow-based MRD quantified according to both LAIP/DfN method and the LSC methods
10-13 weeks
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Standard armACTIVE_COMPARATORconventional 7+3 chemotherapy
Investigational armEXPERIMENTALCPX-351

Interventions

NameTypeDescription
Cytarabine and IdarubicinDRUGInduction 1: Cytarabine 200 mg/m2 i.v. (continuously) d1-7 + Idarubicin 12mg/m2 d1, 2, 3 i.v (60 min) Induction 2: Cytarabine 1500 mg/m2 i.v. q12h d1-3 Consolidation: Cytarabine 1500 mg/m2 i.v. q12h d1-3
CPX-315DRUGInduction 1:CPX-351 44 mg/m2 daunorubicin / 100 mg/m2 cytarabine i.v. (90 min) d1,3,5 Induction 2: CPX-351 44 mg/m2 daunorubicin / 100 mg/m2 cytarabine i.v. (90 min) d1,3 Consolidation therapy:CPX-351 29 mg/m2 daunorubicin / 65 mg/m2 cytarabine i.v. (90 min) d1,3
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites35

Inclusion Criteria: 1. De novo AML 2. No MRC-defining cytogenetic lesion 3. No t(15;17), t(8;21), inv(16) or t(16;16) 4. No NPM1 gene mutation 5. No FLT3 mutated AML (FLT3 ITD or TKD) 6. Not previously treated except for short course hydroxyurea in patients presenting with high WBC count and/or tum...

Countries:France
Unlock Eligibility Criteria

Frequently asked questions about CPX-315

What is CPX-315 used for?

CPX-315 is an investigational small molecule being developed for the treatment of Acute Myeloid Leukemia (AML). It is currently in Phase 2 clinical development and is being studied in patients with de novo intermediate or adverse risk AML.

Who makes CPX-315?

CPX-315 is being developed by Jazz Pharmaceuticals plc, a biopharmaceutical company listed on the NASDAQ under the ticker symbol JAZZ. The company is conducting a Phase 2 clinical trial of CPX-315 in patients with Acute Myeloid Leukemia.

What phase is CPX-315 in?

CPX-315 is currently in Phase 2 clinical development. It is an investigational drug and has not been approved by regulatory authorities. A Phase 2 trial is actively recruiting participants to evaluate its efficacy and safety in Acute Myeloid Leukemia.

What clinical trials is CPX-315 in?

CPX-315 is being evaluated in a Phase 2 clinical trial with the identifier NCT05260528. This randomized, active-controlled study compares CPX-315 to intensive chemotherapy in patients with de novo intermediate or adverse risk AML, stratified by genomics. The trial is recruiting in France and aims to enroll 248 participants aged 18 years and older.

Is CPX-315 the same as CPX-351?

CPX-315 is not the same as CPX-351. CPX-315 is a distinct investigational drug being developed by Jazz Pharmaceuticals. The Phase 2 trial NCT05260528 compares CPX-315 against intensive chemotherapy, which may include CPX-351 as a comparator, but the two are separate agents.