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CMX001

Phase 1

Hepatic Impairment | Small molecule | Gastrointestinal |Jazz Pharmaceuticals plc|Last Updated: May 26, 2022

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment25
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05391724Safety and Pharmacokinetics of CMX001 in Impaired Hepatic Function and Healthy SubjectsPHASE1 COMPLETED 25Feb 1, 2011Sep 1, 2011May 26, 20223 United States
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Study Endpoints
Primary Endpoints
Number of participants with treatment-related adverse events as assessed by Common Terminology Criteria for Adverse Events (CTCAE) v4.0
6 months

An objective of this study was to determine the safety following administration of a single dose of CMX001 in subjects with moderate and severe hepatic impairment compared to match subjects with normal hepatic function.

Secondary Endpoints
Maximum concentration (Cmax) of moderate and severe hepatic impairment after a single dose of CMX001
6 months
Time to maximum concentration (Tmax) of moderate and severe hepatic impairment after a single dose of CMX001
6 months
Area under the concentration-time curve from time zero extrapolated to infinity (AUCinf) of moderate and severe hepatic impairment after a single dose of CMX001
6 months
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeOTHER
Treatment Arms
ArmTypeDescription
CMX001EXPERIMENTALsingle dose of CMX001 administered at 2 mg/kg of ideal body weight rounded to the closest 20 mg
Interventions
NameTypeDescription
CMX001DRUGsingle dose of CMX001 administered at 2 mg/kg of ideal body weight rounded to the closest 20 mg
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Eligibility Criteria
Age Range18 Years — 65 Years
SexALL
Healthy VolunteersYes
Study Sites3

Inclusion Criteria: 1. Able to comprehend and willing to sign an informed consent form (ICF); 2. Male or female subjects, between 18 and 65 years of age, inclusive; 3. Within body mass index (BMI) range 18 to 40 kg/m2, inclusive; 4. Negative test for selected drugs of abuse at Screening (does not i...

Countries:United States
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