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CMX001

Phase 1

Healthy | Small molecule | Other |Jazz Pharmaceuticals plc|Last Updated: May 26, 2022

Success Probability

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Market & Valuation

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Trial Design

RandomizedUNCONTROLLEDDMC
Total Trials1
Total Enrollment24

FDA Designations

No designations recorded

Clinical trial landscape

CMX001 · 2 trials · 2 indications

Phase 1 2
NCT05391724Safety and Pharmacokinetics of CMX001 in Impaired Hepatic Function and Healthy SubjectsHepatic Impairment
COMPLETED25 Analytics
NCT00780182Comparative Bioavailability and Effect of Food on CMX001 in Healthy VolunteersHealthy
COMPLETED24 Analytics
PHASE1COMPLETED
Safety and Pharmacokinetics of CMX001 in Impaired Hepatic Function and Healthy Subjects
Hepatic ImpairmentUnlock trial analytics
PHASE1COMPLETED
Comparative Bioavailability and Effect of Food on CMX001 in Healthy Volunteers
HealthyUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of participants with treatment-related adverse events as assessed by Common Terminology Criteria for Adverse Events (CTCAE) v4.0
6 months

An objective of this study was to determine the safety following administration of a single dose of CMX001 in subjects with moderate and severe hepatic impairment compared to match subjects with normal hepatic function.

AUC and Cmax of CMX001 and cidofovir
Each of 3 doses

Secondary Endpoints

Maximum concentration (Cmax) of moderate and severe hepatic impairment after a single dose of CMX001
6 months
Time to maximum concentration (Tmax) of moderate and severe hepatic impairment after a single dose of CMX001
6 months
Area under the concentration-time curve from time zero extrapolated to infinity (AUCinf) of moderate and severe hepatic impairment after a single dose of CMX001
6 months
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeOTHER

Treatment Arms

ArmTypeDescription
CMX001EXPERIMENTALsingle dose of CMX001 administered at 2 mg/kg of ideal body weight rounded to the closest 20 mg
1EXPERIMENTALAll subjects will receive three 40mg doses of CMX001 as 1)solution fasted, 2)tablet fasted and 3)tablet following a high-fat breakfast. The order in which each subject receives each of the doses will be determined by a randomization code.

Interventions

NameTypeDescription
CMX001DRUGsingle dose of CMX001 administered at 2 mg/kg of ideal body weight rounded to the closest 20 mg
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Eligibility Criteria

Age Range18 Years to 65 Years
SexALL
Healthy VolunteersYes
Study Sites3

Inclusion Criteria: 1. Able to comprehend and willing to sign an informed consent form (ICF); 2. Male or female subjects, between 18 and 65 years of age, inclusive; 3. Within body mass index (BMI) range 18 to 40 kg/m2, inclusive; 4. Negative test for selected drugs of abuse at Screening (does not i...

Countries:United States
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Frequently asked questions about CMX001

What is CMX001 used for?

CMX001 is an investigational small molecule being studied in healthy volunteers and in subjects with hepatic impairment. It is currently in Phase 1 clinical development, with completed trials evaluating its safety, pharmacokinetics, and bioavailability. The drug is not approved and remains under investigation.

Who makes CMX001?

CMX001 is being developed by Jazz Pharmaceuticals plc, a biopharmaceutical company traded on the NASDAQ under the ticker JAZZ. The company is conducting Phase 1 clinical trials to evaluate the drug's safety and pharmacokinetics in healthy subjects and those with hepatic impairment.

What phase is CMX001 in?

CMX001 is in Phase 1 clinical development. It has completed two Phase 1 trials, one in healthy volunteers and one in subjects with hepatic impairment. The drug is investigational and has not been approved by regulatory authorities.

What clinical trials is CMX001 in?

CMX001 has completed two Phase 1 trials. NCT00780182 evaluated comparative bioavailability and the effect of food in healthy volunteers, enrolling 24 participants. NCT05391724 assessed safety and pharmacokinetics in subjects with impaired hepatic function and healthy subjects, enrolling 25 participants. Both trials were conducted in the United States.

Is CMX001 the same as brincidofovir?

CMX001 is also known as brincidofovir, an antiviral small molecule. It is being developed by Jazz Pharmaceuticals for potential use in treating viral infections, though the current Phase 1 trials focus on healthy volunteers and subjects with hepatic impairment.