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Fostamatinib

Phase 1

Chronic Graft Versus Host Disease | Small molecule | Immunology |Incyte Corporation|Last Updated: Jan 22, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDBiomarker
Total Trials1
Total Enrollment30
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT06233110Ruxolitinib Plus Fostamatinib for Steroid Refractory cGvHDPHASE1 RECRUITING 30Oct 29, 2025Jul 1, 2029Jan 22, 20261 United States
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Study Endpoints
Primary Endpoints
Minimum safe and biologically effective dose
6 months

Minimum safe and biologically effective dose will be determined by dose limiting toxicities and overall response rate of the combination regimen, as well as pharmacokinetic and pharmacodynamic markers of fostamatinib (if available)

Secondary Endpoints
Overall response rate
6 months
Duration of Response
1 year
1-year cGvHD-free survival
1 year
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingSINGLE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Dose escalation phase: Dose level 0EXPERIMENTALFostamatinib at dose level 0 (dose of 50mg QAM) in combination with standard of care ruxolitinib 10mg BID
Dose escalation phase: Dose level 1EXPERIMENTALFostamatinib at dose level 1 (dose of 100mg QAM) in combination with standard of care ruxolitinib 10mg BID
Dose escalation phase: Dose level 2EXPERIMENTALFostamatinib at dose level 2 (dose of 150mg QAM) in combination with standard of care ruxolitinib 10mg BID
Dose escalation phase: Dose level 3EXPERIMENTALFostamatinib at dose level 3 (dose of 100mg BID) in combination with standard of care ruxolitinib 10mg BID
Candidate Dose #1EXPERIMENTALIn the safety expansion cohort, subjects will be randomized to one of two candidate doses of fostamatinib (identified from the dose escalation phase) in combination with ruxolitinib 10mg BID.
Candidate Dose #2EXPERIMENTALIn the safety expansion cohort, subjects will be randomized to one of two candidate doses of fostamatinib (identified from the dose escalation phase) in combination with ruxolitinib 10mg BID.
Interventions
NameTypeDescription
FostamatinibDRUGFostamatinib will be administered as part of the initial dose escalation cohort and then two candidate doses will be identified to be administered for the safety expansion cohort.
RuxolitinibDRUGRuxolitinib 10mg BID will be administered in combination with Fostamatinib in each of the study arms.
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Eligibility Criteria
Age Range18 Years — 80 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria 1. Patient is able and willing to provide written informed consent prior to any study related screening procedures are performed. 2. Age ≥ 18 years old at the time of informed consent 3. Have undergone allogeneic hematopoietic cell transplantation (HCT) from any donor source (mat...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT06233110primaryCompletionDate: changed
LOWMay 24, 2026NCT06233110studyFirstPostDate: changed