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Fostamatinib

Phase 1

Chronic Graft Versus Host Disease | Small molecule | Immunology |Incyte Corporation|Last Updated: Jan 22, 2026

Target and mechanism

Molecular targetSYK
Target classInhibitor
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment30

FDA Designations

No designations recorded

Clinical trial landscape

Fostamatinib · 1 trial · 1 indication

Phase 1 1
NCT06233110Ruxolitinib Plus Fostamatinib for Steroid Refractory cGvHDChronic Graft Versus Host Disease
RECRUITING30 Analytics
PHASE1RECRUITING
Ruxolitinib Plus Fostamatinib for Steroid Refractory cGvHD
Chronic Graft Versus Host DiseaseUnlock trial analytics

Study Endpoints

Primary Endpoints

Minimum safe and biologically effective dose
6 months

Minimum safe and biologically effective dose will be determined by dose limiting toxicities and overall response rate of the combination regimen, as well as pharmacokinetic and pharmacodynamic markers of fostamatinib (if available)

Secondary Endpoints

Overall response rate
6 months
Duration of Response
1 year
1-year cGvHD-free survival
1 year
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingSINGLE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Dose escalation phase: Dose level 0EXPERIMENTALFostamatinib at dose level 0 (dose of 50mg QAM) in combination with standard of care ruxolitinib 10mg BID
Dose escalation phase: Dose level 1EXPERIMENTALFostamatinib at dose level 1 (dose of 100mg QAM) in combination with standard of care ruxolitinib 10mg BID
Dose escalation phase: Dose level 2EXPERIMENTALFostamatinib at dose level 2 (dose of 150mg QAM) in combination with standard of care ruxolitinib 10mg BID
Dose escalation phase: Dose level 3EXPERIMENTALFostamatinib at dose level 3 (dose of 100mg BID) in combination with standard of care ruxolitinib 10mg BID
Candidate Dose #1EXPERIMENTALIn the safety expansion cohort, subjects will be randomized to one of two candidate doses of fostamatinib (identified from the dose escalation phase) in combination with ruxolitinib 10mg BID.
Candidate Dose #2EXPERIMENTALIn the safety expansion cohort, subjects will be randomized to one of two candidate doses of fostamatinib (identified from the dose escalation phase) in combination with ruxolitinib 10mg BID.

Interventions

NameTypeDescription
FostamatinibDRUGFostamatinib will be administered as part of the initial dose escalation cohort and then two candidate doses will be identified to be administered for the safety expansion cohort.
RuxolitinibDRUGRuxolitinib 10mg BID will be administered in combination with Fostamatinib in each of the study arms.
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Eligibility Criteria

Age Range18 Years to 80 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria 1. Patient is able and willing to provide written informed consent prior to any study related screening procedures are performed. 2. Age ≥ 18 years old at the time of informed consent 3. Have undergone allogeneic hematopoietic cell transplantation (HCT) from any donor source (mat...

Countries:United States
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Frequently asked questions about Fostamatinib

What is Fostamatinib used for in Chronic Graft Versus Host Disease?

Fostamatinib is being studied for the treatment of Chronic Graft Versus Host Disease (cGvHD). It is currently in Phase 1 clinical development as an investigational therapy for this condition. The drug is being evaluated in combination with ruxolitinib for patients with steroid refractory cGvHD.

What does Fostamatinib target?

Fostamatinib is a small molecule kinase inhibitor, belonging to the -tinib class of drugs. It works by inhibiting kinase enzymes, which play a role in cellular signaling pathways. This mechanism is being explored for its potential to treat Chronic Graft Versus Host Disease.

Who makes Fostamatinib?

Fostamatinib is being developed by Incyte Corporation, a biopharmaceutical company traded on the NASDAQ under the ticker symbol INCY. The company is conducting clinical trials to evaluate the drug for the treatment of Chronic Graft Versus Host Disease.

What phase is Fostamatinib in?

Fostamatinib is in Phase 1 clinical development for Chronic Graft Versus Host Disease. It is an investigational drug and has not been approved by the FDA for this indication. The ongoing Phase 1 trial is currently recruiting participants in the United States.

What clinical trials is Fostamatinib in?

Fostamatinib is being studied in a Phase 1 clinical trial with the identifier NCT06233110. The trial is titled 'Ruxolitinib Plus Fostamatinib for Steroid Refractory cGvHD' and is recruiting 30 participants aged 18 years and older in the United States. The study is controlled but not randomized or double-blind.