Recent Updates
Recently added Catalysts

HMPL-523

Phase 3

Primary Immune Thrombocytopenia (ITP) | Small molecule | Hematology |HUTCHMED (China) Limited|Last Updated: May 4, 2026

Success Probability
Subscribe to view
Market & Valuation
Subscribe to view
Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment272
FDA Designations
No designations recorded
Clinical trial landscape

HMPL-523 · 11 trials · 9 indications

Phase 3 1Phase 2 1Phase 1 8Early Phase 1 1
NCT05029635Phase III Study on HMPL-523 for Treatment of ITPPrimary Immune Thrombocytopenia (ITP)
COMPLETED272 Analytics
PHASE3COMPLETED
Phase III Study on HMPL-523 for Treatment of ITP
Primary Immune Thrombocytopenia (ITP)Unlock trial analytics
Study Endpoints
Primary Endpoints
the durable response rate in the primary study
treatment period Week14-Week24

Platelet count ≥50×10\^9 /L on at least 4 of 6 scheduled visits of Week14-Week24 in the primary study

Phase II: overall Hb response rate
24Weeks

Phase II: Overall Hb response rate: the proportion of patients with overall Hb response by Week 24

Number of Participants with any Adverse Event
From first dose to within 28 days after the last dose

Adverse Events evaluated by the National Cancer Institute Common Terminology Criteria for Adverse Events (NCI CTCAE) v5.0

Dose limited toxicities evaluated with NCI CTCAE v4.03
within 28 days after the first dose

Incidence of dose limited toxicities and associated dose of HMPL-523

To assess number of participants with adverse events as a measure of safety and tolerability during dose escalating
6 months
maximum plasma concentration (Cmax)
through study completion, an average of 2 months

To evaluate the pharmacokinetics and bioequivalence of HMPL- 523 Tablets 300 mg (100 mg/tablet×3) (produced by two different manufacturers) taken orally in a single dose after a standard meal in healthy Chinese subjects

time to maximum plasma concentration (Tmax)
Time Frame: through study completion, an average of 2 months

To evaluate the pharmacokinetics and bioequivalence of HMPL- 523 Tablets 300 mg (100 mg/tablet×3) (produced by two different manufacturers) taken orally in a single dose after a standard meal in healthy Chinese subjects

terminal elimination half-life (t1/2)
through study completion, an average of 2 months

To evaluate the pharmacokinetics and bioequivalence of HMPL- 523 Tablets 300 mg (100 mg/tablet×3) (produced by two different manufacturers) taken orally in a single dose after a standard meal in healthy Chinese subjects

Area under plasma drug concentration-time curve (AUC0-t, AUC0-∞)
through study completion, an average of 2 months

To evaluate the pharmacokinetics and bioequivalence of HMPL- 523 Tablets 300 mg (100 mg/tablet×3) (produced by two different manufacturers) taken orally in a single dose after a standard meal in healthy Chinese subjects

Secondary Endpoints
the overall response rate in the primary study
treatment period Week1-Week24 in the primary study
Incidence of treatment emergent adverse events
treatment period Week1-Week24 in the primary study
Plasma concentration at steady state 2 hours post dose (C2h,ss)
treatment period Week1-Week24 in the primary study
Unlock Study Endpoints
Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Drug: HMPL-523ACTIVE_COMPARATORPrimacy study (Randomized, Double-Blind Phase): Eligible subjects receive 300 mg HMPL-523 treatment once daily for 24 weeks. Sub study (Open-label Phase): Eligible subjects receive 300 mg HMPL-523 treatment once daily for 76 weeks after the enrollment of the last patient enrolled in open-label phase.
Drug: placeboPLACEBO_COMPARATORPrimacy study (Randomized, Double-Blind Phase): Eligible subjects will receive 300 mg HMPL-523 matched placebo treatment once daily for 24 weeks.
HMPL-523EXPERIMENTALPhase II: Eligible subjects will receive 300 mg HMPL-523 treatment once daily for 8 weeks and at least 16 weeks open-label treatment. Phase III: Eligible subjects will receive 300 mg HMPL-523 treatment once daily for 24 weeks and enter open-label phase in the opinion of the Investigator.
PlaceboPLACEBO_COMPARATORPhase II: Eligible subjects will receive 300 mg HMPL-523 treatment once daily for 8 weeks and at least 16 weeks open-label treatment. Phase III: Eligible subjects will receive 300 mg HMPL-523 treatment once daily for 24 weeks and enter open-label phase in the opinion of the Investigator.
treatment armACTIVE_COMPARATOREligible subjects will be treated with planned dose of 100 mg, 200 mg and 300 mg HMPL-523 once daily for 8 weeks and 16 weeks open-label treatment.
placebo armPLACEBO_COMPARATOREligible subjects will be treated with HMPL-523 matching placebo once daily for 8 weeks and 16 weeks open-label treatment.
HMPL-523-TRREXPERIMENTALThree cycle dose: TRR Test product: HMPL-523 Tablets manufactured by Hutchison MediPharma (Suzhou) Co., Ltd.; Reference product: HMPL-523 Tablets manufactured by WuXi STA
HMPL-523-RTREXPERIMENTALThree cycle dose:RTR Test product: HMPL-523 Tablets manufactured by Hutchison MediPharma (Suzhou) Co., Ltd.; Reference product: HMPL-523 Tablets manufactured by WuXi STA
HMPL-523-RRTEXPERIMENTALThree cycle dose:RRT Test product: HMPL-523 Tablets manufactured by Hutchison MediPharma (Suzhou) Co., Ltd.; Reference product: HMPL-523 Tablets manufactured by WuXi STA
Interventions
NameTypeDescription
HMPL-523DRUGHMPL-523(300mg PO QD)
PlaceboDRUGPlacebo(300mg PO QD)
HMPL-523(300mg PO QD)DRUGHMPL-523(300mg PO QD)
HMPL-523 Acetate Tablets (Test Formulation)DRUGThe trial participants were administered the drug on the first day of each cycle. dose 300mg
HMPL-523 Acetate Tablets (Reference Formulation)DRUGThe trial participants were administered the drug on the first day of each cycle. dose 300mg
150 µCi [14C]HMPL-523DRUGD8: \[14C\] HMPL-523 Suspension 300 mg/150 μCi Single dose
ItraconazoleDRUGItraconazole is an FDA approved synthetic triazole antifungal agent
RifampinDRUGRifampin is an FDA approved semisynthetic antiobiotic derivative indicated in the treatment of both tuberculosis and meningococcal carrier state
RabeprazoleDRUG40 mg of rabeprazole will be administered by mouth once daily in the morning from Day 20 to Day 26
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites37

Inclusion Criteria for double-blind phase: 1. Voluntary signature of written informed consent form; 2. Male or female aged 18\~75 years; 3. Performance Status score \[Eastern Cooperative Oncology Group (ECOG) score\] 0\~1; 4. Having been diagnosed as ITP prior to randomization, and duration of dise...

Countries:ChinaAustralia
Unlock Eligibility Criteria
Recent Changes (Last 90 Days)
LOWMay 24, 2026NCT05535933studyFirstPostDate: changed