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HMPL-523

Phase 3

Primary Immune Thrombocytopenia (ITP) | Small molecule | Hematology |HUTCHMED (China) Limited|Last Updated: May 4, 2026

Target and mechanism

Molecular targetSyk
Target classKinase
ModalitySmall molecule

Also known as HMPL-523(300mg PO QD)

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment272

FDA Designations

No designations recorded

Clinical trial landscape

HMPL-523 · 11 trials · 9 indications

Phase 3 1Phase 2 1Phase 1 8Early Phase 1 1
NCT05029635Phase III Study on HMPL-523 for Treatment of ITPPrimary Immune Thrombocytopenia (ITP)
COMPLETED272 Analytics
PHASE3COMPLETED
Phase III Study on HMPL-523 for Treatment of ITP
Primary Immune Thrombocytopenia (ITP)Unlock trial analytics

Study Endpoints

Primary Endpoints

the durable response rate in the primary study
treatment period Week14-Week24

Platelet count ≥50×10\^9 /L on at least 4 of 6 scheduled visits of Week14-Week24 in the primary study

Phase II: overall Hb response rate
24Weeks

Phase II: Overall Hb response rate: the proportion of patients with overall Hb response by Week 24

Number of Participants with any Adverse Event
From first dose to within 28 days after the last dose

Adverse Events evaluated by the National Cancer Institute Common Terminology Criteria for Adverse Events (NCI CTCAE) v5.0

Dose limited toxicities evaluated with NCI CTCAE v4.03
within 28 days after the first dose

Incidence of dose limited toxicities and associated dose of HMPL-523

To assess number of participants with adverse events as a measure of safety and tolerability during dose escalating
6 months
maximum plasma concentration (Cmax)
through study completion, an average of 2 months

To evaluate the pharmacokinetics and bioequivalence of HMPL- 523 Tablets 300 mg (100 mg/tablet×3) (produced by two different manufacturers) taken orally in a single dose after a standard meal in healthy Chinese subjects

time to maximum plasma concentration (Tmax)
Time Frame: through study completion, an average of 2 months

To evaluate the pharmacokinetics and bioequivalence of HMPL- 523 Tablets 300 mg (100 mg/tablet×3) (produced by two different manufacturers) taken orally in a single dose after a standard meal in healthy Chinese subjects

terminal elimination half-life (t1/2)
through study completion, an average of 2 months

To evaluate the pharmacokinetics and bioequivalence of HMPL- 523 Tablets 300 mg (100 mg/tablet×3) (produced by two different manufacturers) taken orally in a single dose after a standard meal in healthy Chinese subjects

Area under plasma drug concentration-time curve (AUC0-t, AUC0-∞)
through study completion, an average of 2 months

To evaluate the pharmacokinetics and bioequivalence of HMPL- 523 Tablets 300 mg (100 mg/tablet×3) (produced by two different manufacturers) taken orally in a single dose after a standard meal in healthy Chinese subjects

Secondary Endpoints

the overall response rate in the primary study
treatment period Week1-Week24 in the primary study
Incidence of treatment emergent adverse events
treatment period Week1-Week24 in the primary study
Plasma concentration at steady state 2 hours post dose (C2h,ss)
treatment period Week1-Week24 in the primary study
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Drug: HMPL-523ACTIVE_COMPARATORPrimacy study (Randomized, Double-Blind Phase): Eligible subjects receive 300 mg HMPL-523 treatment once daily for 24 weeks. Sub study (Open-label Phase): Eligible subjects receive 300 mg HMPL-523 treatment once daily for 76 weeks after the enrollment of the last patient enrolled in open-label phase.
Drug: placeboPLACEBO_COMPARATORPrimacy study (Randomized, Double-Blind Phase): Eligible subjects will receive 300 mg HMPL-523 matched placebo treatment once daily for 24 weeks.
HMPL-523EXPERIMENTALPhase II: Eligible subjects will receive 300 mg HMPL-523 treatment once daily for 8 weeks and at least 16 weeks open-label treatment. Phase III: Eligible subjects will receive 300 mg HMPL-523 treatment once daily for 24 weeks and enter open-label phase in the opinion of the Investigator.
PlaceboPLACEBO_COMPARATORPhase II: Eligible subjects will receive 300 mg HMPL-523 treatment once daily for 8 weeks and at least 16 weeks open-label treatment. Phase III: Eligible subjects will receive 300 mg HMPL-523 treatment once daily for 24 weeks and enter open-label phase in the opinion of the Investigator.
treatment armACTIVE_COMPARATOREligible subjects will be treated with planned dose of 100 mg, 200 mg and 300 mg HMPL-523 once daily for 8 weeks and 16 weeks open-label treatment.
placebo armPLACEBO_COMPARATOREligible subjects will be treated with HMPL-523 matching placebo once daily for 8 weeks and 16 weeks open-label treatment.
HMPL-523-TRREXPERIMENTALThree cycle dose: TRR Test product: HMPL-523 Tablets manufactured by Hutchison MediPharma (Suzhou) Co., Ltd.; Reference product: HMPL-523 Tablets manufactured by WuXi STA
HMPL-523-RTREXPERIMENTALThree cycle dose:RTR Test product: HMPL-523 Tablets manufactured by Hutchison MediPharma (Suzhou) Co., Ltd.; Reference product: HMPL-523 Tablets manufactured by WuXi STA
HMPL-523-RRTEXPERIMENTALThree cycle dose:RRT Test product: HMPL-523 Tablets manufactured by Hutchison MediPharma (Suzhou) Co., Ltd.; Reference product: HMPL-523 Tablets manufactured by WuXi STA

Interventions

NameTypeDescription
HMPL-523DRUGHMPL-523(300mg PO QD)
PlaceboDRUGPlacebo(300mg PO QD)
HMPL-523(300mg PO QD)DRUGHMPL-523(300mg PO QD)
HMPL-523 Acetate Tablets (Test Formulation)DRUGThe trial participants were administered the drug on the first day of each cycle. dose 300mg
HMPL-523 Acetate Tablets (Reference Formulation)DRUGThe trial participants were administered the drug on the first day of each cycle. dose 300mg
150 µCi [14C]HMPL-523DRUGD8: \[14C\] HMPL-523 Suspension 300 mg/150 μCi Single dose
ItraconazoleDRUGItraconazole is an FDA approved synthetic triazole antifungal agent
RifampinDRUGRifampin is an FDA approved semisynthetic antiobiotic derivative indicated in the treatment of both tuberculosis and meningococcal carrier state
RabeprazoleDRUG40 mg of rabeprazole will be administered by mouth once daily in the morning from Day 20 to Day 26
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Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites37

Inclusion Criteria for double-blind phase: 1. Voluntary signature of written informed consent form; 2. Male or female aged 18\~75 years; 3. Performance Status score \[Eastern Cooperative Oncology Group (ECOG) score\] 0\~1; 4. Having been diagnosed as ITP prior to randomization, and duration of dise...

Countries:ChinaAustralia
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Frequently asked questions about HMPL-523

What is HMPL-523 used for?

HMPL-523 is an investigational small molecule being studied for several conditions, including Primary Immune Thrombocytopenia (ITP), Rheumatoid Arthritis (RA), Mature B-cell Neoplasms, and Warm Antibody Autoimmune Hemolytic Anemia. It is also used in healthy volunteer studies for pharmacokinetic and bioequivalence assessments. The drug is not approved and remains in clinical development.

What does HMPL-523 target?

HMPL-523 targets Syk, a kinase enzyme involved in immune signaling. By inhibiting Syk, the drug may modulate immune responses relevant to autoimmune and hematologic conditions. This mechanism is being explored in clinical trials for indications such as immune thrombocytopenia and rheumatoid arthritis.

Who makes HMPL-523?

HMPL-523 is developed by HUTCHMED (China) Limited, a biopharmaceutical company listed on the stock exchange under the ticker HCM. The company is conducting clinical trials for this investigational drug across multiple indications, primarily in China.

What phase is HMPL-523 in?

HMPL-523 is in Phase 1 and Phase 2 clinical development. Completed trials include Phase 1 studies in Mature B-cell Neoplasms and healthy subjects, while an active Phase 2 trial is evaluating the drug for Warm Antibody Autoimmune Hemolytic Anemia. The drug is investigational and not yet approved.

What clinical trials is HMPL-523 in?

HMPL-523 has been studied in several clinical trials. NCT02857998 was a completed Phase 1 study in relapsed or refractory Mature B-cell Neoplasms. NCT05318820 was a completed early Phase 1 bioequivalence study in healthy subjects. NCT05535933 is an active Phase 2 trial for Warm Antibody Autoimmune Hemolytic Anemia. NCT05781906 was a completed human mass balance study.

Is HMPL-523 the same as Sovleplenib?

Yes, HMPL-523 is also known as Sovleplenib. In clinical trial NCT05535933, the drug is referred to as HMPL-523 (Sovleplenib) in the treatment of Warm Antibody Autoimmune Hemolytic Anemia. This alternative name may appear in research publications and trial registries.