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MarzAA

Phase 1

Hemophilia A | Monoclonal antibody | Hematology |Gyre Therapeutics, Inc.|Last Updated: Sep 12, 2021

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLED
Total Trials1
Total Enrollment11
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04072237Study of Coagulation Faction VIIa Variant Marzeptacog Alfa (Activated) in Adult Subjects With HemophiliaPHASE1 COMPLETED 11Sep 1, 2019Jun 1, 2020Sep 12, 2021 -
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Study Design & Arms
Interventions
NameTypeDescription
MarzAA (marzeptacog alfa [activated])BIOLOGICALSingle intravenous dose and ascending doses of subcutaneous injection of MarzAA (Coagulation Faction VIIa Variant)
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