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Coagulation Factor IX variant

Phase 2

Hemophilia B | Monoclonal antibody | Hematology |Gyre Therapeutics, Inc.|Last Updated: Aug 8, 2021

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLED
Total Trials1
Total Enrollment6
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03995784Study of Next-Generation Recombinant Factor IX Variant in Adult Subjects With Hemophilia BPHASE2 COMPLETED 6Jun 1, 2019Apr 1, 2020Aug 8, 2021 -
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Study Design & Arms
Interventions
NameTypeDescription
Coagulation Factor IX variantBIOLOGICALSingle intravenous injection of CB2679d/Dalcinonacog alfa
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