Success Probability
Approval Probability
TA Base Rate
Adjusted LOA
ML Risk
Market & Valuation
rNPV
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Trial Design
UNCONTROLLED
Total Trials1
Total Enrollment6
FDA Designations
No designations recordedClinical trial landscape
Coagulation Factor IX variant · 1 trial · 1 indication
NCT03995784Study of Next-Generation Recombinant Factor IX Variant in Adult Subjects With Hemophilia BHemophilia B PHASE2COMPLETED
Study of Next-Generation Recombinant Factor IX Variant in Adult Subjects With Hemophilia B
Hemophilia BUnlock trial analytics Study Design & Arms
Competitive Landscape -Hemophilia 38 trials (matched to "Hemophilia B")