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ISU304/CB2679d/Dalcinonacog alfa 75~/kg

Phase 1

Hemophilia B | Monoclonal antibody | Hematology |Catalyst Pharmaceuticals, Inc.|Last Updated: Nov 10, 2020

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment11

FDA Designations

No designations recorded

Clinical trial landscape

ISU304/CB2679d/Dalcinonacog alfa 75~/kg · 1 trial · 1 indication

Phase 1 1
NCT03186677Dose-escalation Study to Investigate the Safety, PK, and PD of ISU304/CB2679d in Hemophilia B PatientsHemophilia B
COMPLETED11 Analytics
PHASE1COMPLETED
Dose-escalation Study to Investigate the Safety, PK, and PD of ISU304/CB2679d in Hemophilia B Patients
Hemophilia BUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Adverse Events (AEs) After the Administration of Investigational Products (IP)
Through study completion, an average of 8 days

The number of reported AEs (local/systemic/other) after IP administration was calculated by cohort.

Secondary Endpoints

Maximum Plasma Concentration (Cmax)
0 to 72 hours for Cohorts 1 to 3, 0 to 120 hours for Cohorts 4 and 5
Factor IX Inhibitor
At end of study visit (an average of 8 days)
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Cohort 1EXPERIMENTALSingle intravenous administration of BeneFIX (75 IU/kg) with 72 hours of observation, followed by single intravenous administration of ISU304/CB2679d/Dalcinonacog alfa (75 IU/kg) with 72 hours of observation
Cohort 2EXPERIMENTALSingle intravenous administration of ISU304/CB2679d/Dalcinonacog alfa (75 IU/kg) with 72 hours of observation, followed by single subcutaneous administration of ISU304/CB2679d/Dalcinonacog alfa (75 IU/kg) with 72 hours of observation
Cohort 3EXPERIMENTALSingle intravenous administration of ISU304/CB2679d/Dalcinonacog alfa (75 IU/kg) with 72 hours of observation, followed by single subcutaneous administration of ISU304/CB2679d/Dalcinonacog alfa (150 IU/kg) with 120 hours of observation
Cohort 4EXPERIMENTALOne subcutaneous administration of ISU304/CB2679d/Dalcinonacog alfa (150 IU/kg) per day for 6 days with 240 hours of observation
Cohort 5EXPERIMENTALOne intravenous administration of ISU304/CB2679d/Dalcinonacog alfa (75 IU/kg) followed by subcutaneous administration of ISU304/CB2679d/Dalcinonacog alfa (150 IU/kg) once daily for 9 days with 312 hours of observation

Interventions

NameTypeDescription
ISU304/CB2679d/Dalcinonacog alfa 75~150 IU/kgBIOLOGICALISU304/CB2679d/Dalcinonacog alfa 75\~150 IU/kg by intravenous or subcutaneous
BeneFIXBIOLOGICALBeneFIX 75 IU/kg, intravenous administration
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Eligibility Criteria

Age Range12 Years to 65 Years
SexALL
Healthy VolunteersNo
Study Sites3

Inclusion Criteria: 1. Previously treated male patients with moderate or severe hemophilia B (documented FIX activity ≤ 2% and exposed to any FIX product for ≥ 150 exposure days (estimated) at the time of screening) 2. Patients must be 12 to 65 years old at the time of screening 3. Patients who hav...

Countries:South Korea
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Frequently asked questions about ISU304/CB2679d/Dalcinonacog alfa 75~/kg

What is ISU304/CB2679d/Dalcinonacog alfa used for?

ISU304/CB2679d/Dalcinonacog alfa is an investigational drug being developed for the treatment of Hemophilia B. It is a monoclonal antibody being studied in clinical trials to evaluate its safety and pharmacological properties in patients with this condition.

Who is developing ISU304/CB2679d/Dalcinonacog alfa?

ISU304/CB2679d/Dalcinonacog alfa is being developed by Catalyst Pharmaceuticals, Inc., a company publicly traded under the ticker symbol CPRX. The drug is currently in clinical development for Hemophilia B.

What phase is ISU304/CB2679d/Dalcinonacog alfa in?

ISU304/CB2679d/Dalcinonacog alfa is in Phase 1 clinical development. It is an investigational drug and has not been approved by regulatory authorities. The drug is being studied for its safety, pharmacokinetics, and pharmacodynamics in patients with Hemophilia B.

What clinical trials is ISU304/CB2679d/Dalcinonacog alfa in?

ISU304/CB2679d/Dalcinonacog alfa has been studied in one clinical trial, identified as NCT03186677. This was a dose-escalation study to investigate the safety, pharmacokinetics, and pharmacodynamics of the drug in Hemophilia B patients. The trial was conducted in South Korea and has been completed.

Is ISU304/CB2679d/Dalcinonacog alfa the same as Dalcinonacog alfa?

Yes, ISU304/CB2679d/Dalcinonacog alfa is also known as Dalcinonacog alfa. These names refer to the same investigational drug being developed by Catalyst Pharmaceuticals for Hemophilia B.