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CLS-AX

Phase 2

Neovascular Age-related Macular Degeneration | Small molecule | Ophthalmology |Clearside Biomedical, Inc.|Last Updated: Jul 25, 2025

Success Probability

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Trial Design

RandomizedDouble-BlindCONTROLLEDDMC
Total Trials2
Total Enrollment87

FDA Designations

No designations recorded

Clinical trial landscape

CLS-AX · 2 trials · 1 indication

Phase 2 1Phase 1 1
NCT05891548Study to Evaluate Suprachoroidally Administered CLS-AX in the Treatment of Neovascular Age-Related Macular DegenerationNeovascular Age-related Macular Degeneration
COMPLETED60 Analytics
PHASE2COMPLETED
Study to Evaluate Suprachoroidally Administered CLS-AX in the Treatment of Neovascular Age-Related Macular Degeneration
Neovascular Age-related Macular DegenerationUnlock trial analytics

Study Endpoints

Primary Endpoints

Evaluations of Outcomes Related to ETDRS BCVA in the Study Eye Over Time
Baseline, Weeks 4, 12, 16, 20, 24, 28, 32 and 36

Best Corrected Visual Acuity (BCVA) letter score measured on the Early Treatment Diabetic Retinopathy Study (ETDRS) chart at a starting test distance of 4 meters. The BCVA letter score ranges from 0 to 100 (best score attainable). An increase in BCVA letter score from baseline indicates an improvement in visual acuity.

Number of Participants With Treatment-emergent Adverse Events (TEAEs)
Day 1 to Week 12

Number of participants with treatment-emergent adverse events (TEAEs) reported between the administration of CLS-AX and study exit.

Number of Participants With Serious Adverse Events
Day 1 to Week 12

Number of participants with serious adverse events (SAEs) reported between the administration of CLS-AX and study exit.

Secondary Endpoints

Evaluations of Outcomes Related to Fluid Detected on Optical Coherence Tomography in the Study Eye Over Time
Baseline, Weeks 4, 12, 16, 20, 24, 28, 32 and 36
Evaluations of Outcomes Related to Lesion Size on Fundus Fluorescein Angiography in the Study Eye Over Time
Baseline, Week 36
Evaluation of the Number of Study Drug Injections and Supplemental Therapy Injections in the Study Eye Over Time
From Baseline Through Week 36
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
1.0 mg CLS-AXEXPERIMENTALSuprachoroidal injection of 10 mg/mL (1.0 mg in 0.1 mL) of CLS-AX
AfliberceptACTIVE_COMPARATORIntravitreal injection of aflibercept (2 mg in 0.05 mL)
Cohort 1 (Low Dose)EXPERIMENTALSubjects will receive a low dose of 0.03 mg CLS-AX
Cohort 2 (Low-mid Dose)EXPERIMENTALSubjects will receive a low-mid dose of 0.10 mg CLS-AX
Cohort 3 (High-mid Dose)EXPERIMENTALSubjects will receive a high-mid dose of 0.50 mg CLS-AX
Cohort 4 (High Dose)EXPERIMENTALSubjects will receive a high-mid dose of 1.0 mg CLS-AX

Interventions

NameTypeDescription
CLS-AXDRUGCLS-AX will be administered by suprachoroidal injection into the study eye on Day 1 and then every 12 to 24 weeks as determined by protocol-defined disease activity criteria.
AfliberceptDRUGAflibercept will be administered by intravitreal injection into the study eye once every 8 weeks (Q8W).
Anti-VEGFDRUGStandard of care therapy used to block vascular endothelial growth factor
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Eligibility Criteria

Age Range50 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites32

Key Inclusion Criteria: * Diagnosis of neovascular age-related macular degeneration (nAMD) in the study eye within 36 months of Visit 1. * Subfoveal choroidal neovascularization (CNV) secondary to nAMD of any lesion type in the study eye that shows total lesion area ≤30 mm2, CNV component area of ≥...

Countries:United States
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Frequently asked questions about CLS-AX

What is CLS-AX used for in neovascular age-related macular degeneration?

CLS-AX is an investigational small molecule being developed for the treatment of neovascular age-related macular degeneration (nAMD), a condition characterized by abnormal blood vessel growth in the eye. It is administered via suprachoroidal injection and is currently in Phase 2 clinical development.

What does CLS-AX target?

The specific molecular target of CLS-AX has not been disclosed in available information. It is a small molecule designed for suprachoroidal administration in the eye, intended to treat neovascular age-related macular degeneration, but its precise mechanism of action is not publicly detailed.

Who makes CLS-AX?

CLS-AX is being developed by Clearside Biomedical, Inc., a biopharmaceutical company traded on the Nasdaq under the ticker symbol CLSD. The company is focused on ophthalmology and is advancing CLS-AX through clinical trials for neovascular age-related macular degeneration.

What phase is CLS-AX in?

CLS-AX is currently in Phase 2 clinical development. It has completed a Phase 1 safety and tolerability study and a Phase 2 efficacy study, both in patients with neovascular age-related macular degeneration. It is not yet approved by regulatory authorities.

What clinical trials is CLS-AX in?

CLS-AX has been studied in two completed clinical trials. NCT04626128 was a Phase 1 safety and tolerability study of suprachoroidal injection of CLS-AX following anti-VEGF therapy, enrolling 27 participants. NCT05891548 was a Phase 2 study evaluating suprachoroidally administered CLS-AX in neovascular AMD, enrolling 60 participants.

Is CLS-AX the same as any other drug?

No alternative names for CLS-AX have been identified in available information. It is referred to solely as CLS-AX in clinical trial records and company communications, and no other drug names have been associated with this investigational agent.