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BRTX-100

Phase 2

Lumbar Disc Disease | Monoclonal antibody | Musculoskeletal |BioRestorative Therapies, Inc.|Last Updated: Aug 26, 2025

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindSHAM_CONTROLLEDDMC
Total Trials1
Total Enrollment99

FDA Designations

FAST_TRACK

Clinical trial landscape

BRTX-100 · 1 trial · 1 indication

Phase 2 1
NCT04042844A Single Dose of BRTX 100 for Patients With Chronic Lumbar Disc Disease (cLDD)Lumbar Disc Disease
RECRUITING99 Analytics
PHASE2RECRUITING
A Single Dose of BRTX 100 for Patients With Chronic Lumbar Disc Disease (cLDD)
Lumbar Disc DiseaseUnlock trial analytics

Study Endpoints

Primary Endpoints

Primary Safety Measures
Baseline through Week 104 / Early Termination

Report of adverse events (AEs), clinical review and questionnaires for pain, disability and quality of life at Baseline through Week 104/ Early Termination * Vital Signs * Physical Examination * Laboratory Evaluation (hematology and chemistry) * Clinical review of MRI changes from Baseline to Week 104 (MRI density measurements in T2 weighted images performed at Baseline, Week 52 and Week 104 with predetermined MRI rating scores)

Primary Efficacy Measures
Baseline through Week 52

* VAS for Pain Assessment * ODI for Functional Assessment Primary Efficacy Endpoint: Clinical response, defined as at least a 30% decrease in pain as measured on the VAS scale and at least a 30% increase in function based on the ODI at Week 52 as compared to baseline.

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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Active Treatment- BRTX-100EXPERIMENTALBRTX-100 consists of a population of hypoxic-cultured bone marrow mononuclear cells highly enriched in mesenchymal stem cells from autologous bone marrow with autologous platelet lysate.
ShamSHAM_COMPARATORIsotonic saline will be used as a control (sham) in this study. Drug: saline (0.9% sodium chloride). Please note this will be a sham procedure. This isotonic saline will not be injected intradiscally.

Interventions

NameTypeDescription
BRTX-100BIOLOGICALHypoxic cultured mesenchymal stem cells (MSCs) from autologous bone marrow with autologous platelet lysate.
SalineDRUGSodium Chloride (0.9%) intravenous infusion preparation is a sterile and non-pyrogenic solution
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites19

Subject Inclusion Criteria: A subject is eligible for inclusion if all the following criteria are met: 1. A high index of suspicion for discogenic pain, (i.e., painful degenerative disc(s) with or without protrusions less than or equal to 5 mm) 1. Chronic Lower Back Pain for at least 6 months ...

Countries:United States
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Frequently asked questions about BRTX-100

What is BRTX-100 used for?

BRTX-100 is an investigational monoclonal antibody being developed for the treatment of Lumbar Disc Disease, a musculoskeletal condition. It is currently in Phase 2 clinical development and has been granted Fast Track designation by the FDA. The drug is administered as a single dose to patients with chronic lumbar disc disease.

What does BRTX-100 target?

BRTX-100 is a monoclonal antibody, but its specific molecular target has not been disclosed. The drug is being studied for its potential to treat Lumbar Disc Disease, a condition affecting the intervertebral discs of the lower spine. Its mechanism of action is not publicly detailed.

Who makes BRTX-100?

BRTX-100 is being developed by BioRestorative Therapies, Inc., a biopharmaceutical company traded on the stock exchange under the ticker symbol BRTX. The company is conducting clinical trials to evaluate the safety and efficacy of BRTX-100 for the treatment of Lumbar Disc Disease.

What phase is BRTX-100 in?

BRTX-100 is currently in Phase 2 clinical development. It is an investigational drug and has not yet been approved by the FDA. The drug has received Fast Track designation, which is intended to facilitate its development and expedite its review process for the treatment of Lumbar Disc Disease.

What clinical trials is BRTX-100 in?

BRTX-100 is being evaluated in a Phase 2 clinical trial identified as NCT04042844. This randomized, double-blind, sham-controlled study is recruiting 99 participants in the United States to assess the effects of a single dose of BRTX-100 in patients with chronic lumbar disc disease. The trial is currently recruiting participants aged 18 years and older.

Is BRTX-100 the same as BRTX 100?

Yes, BRTX-100 and BRTX 100 refer to the same investigational drug. The clinical trial NCT04042844 uses the title 'A Single Dose of BRTX 100 for Patients With Chronic Lumbar Disc Disease (cLDD)', confirming that BRTX-100 and BRTX 100 are alternative names for the same drug being developed by BioRestorative Therapies.