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NeoVax

Phase 1

Lymphocytic Leukemia | Small molecule | Oncology |BioNTech SE|Last Updated: May 28, 2026

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment15

FDA Designations

No designations recorded

Clinical trial landscape

NeoVax · 1 trial · 1 indication

Phase 1 1
NCT03219450A Personalized Neoantigen Cancer Vaccine in Treatment Naïve, Asymptomatic Patients With IGHV Unmutated CLL.Lymphocytic Leukemia
RECRUITING15 Analytics
PHASE1RECRUITING
A Personalized Neoantigen Cancer Vaccine in Treatment Naïve, Asymptomatic Patients With IGHV Unmutated CLL.
Lymphocytic LeukemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Feasibility of neoantigen identification
6 months

The proportion of all enrolled patients for whom sequencing and analysis leads to identification of at least 7 actionable peptides to initiate vaccine production

Feasibility of vaccine generation
6 months

Of the patients who generate at least 7 actionable peptides, the proportion for whom the time from sample collection to vaccine availability is less than 12 weeks

Safety of NeoVax
1 year

The number of patients with treatment-limiting toxicities based on NCI CTCAE v5.0

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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
NeoVaxEXPERIMENTAL* NeoVax will be administered in a priming and booster phase. * The priming shots will comprise days 1, 4, 8, 15, and 22. * Booster shots will be given on days 78 and 134.
Neovax + Low-dose cyclophosphamideEXPERIMENTAL* NeoVax will be administered in a priming and booster phase. * The priming shots will comprise days 1, 4, 8, 15, and 22. * Booster shots will be given on days 78 and 134. * Low dose cyclophosphamide is administered twice daily on weeks -2, 1, 3, 5
Neovax + Low-dose cyclophosphamide + PembrolizumabEXPERIMENTAL* NeoVax will be administered in a priming and booster phase. * The priming shots will comprise days 1, 4, 8, 15, and 22. * Booster shots will be given on days 78 and 134. * Low dose cyclophosphamide is administered twice daily on weeks -2, 1, 3, 5 * Pembrolizumab will be administered starting on Week 12 Day 78 and for up to 17 cycles (approximately 1 year).

Interventions

NameTypeDescription
NeoVaxDRUGIt stimulates the immune system to attack cancer cells.
CyclophosphamideDRUGIt is a chemotherapy drug used to treat many cancers. At low doses, it is an investigational drug to help the immune cells to be better at attacking cancer cells while avoiding chemotherapy toxicity.
PembrolizumabDRUGIs a monoclonal antibody that helps the immune cells to be better at attacking cancer cells.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Diagnosis of CLL as per IWCLL 2018 criteria * Patient's CLL must have an unmutated immunoglobulin heavy chain variable (IGHV) region gene, defined as \< 2% mutated compared to germline. * Patient must have had no history of CLL-directed therapy due to meeting IWCLL 2018 criter...

Countries:United States
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Frequently asked questions about NeoVax

What is NeoVax used for in lymphocytic leukemia?

NeoVax is an investigational personalized neoantigen cancer vaccine being studied for the treatment of lymphocytic leukemia, specifically in treatment-naive, asymptomatic patients with IGHV unmutated chronic lymphocytic leukemia. It is currently in Phase 1 clinical development and is not yet approved by regulatory authorities.

Who is developing NeoVax?

NeoVax is being developed by BioNTech SE, a biotechnology company traded on the NASDAQ under the ticker symbol BNTX. The company is conducting a Phase 1 clinical trial to evaluate the safety and efficacy of this personalized cancer vaccine in patients with lymphocytic leukemia.

What phase is NeoVax in?

NeoVax is currently in Phase 1 clinical development. It is an investigational drug, meaning it has not been approved by the FDA or any other regulatory agency. The ongoing Phase 1 trial is actively recruiting participants to assess the vaccine's safety and preliminary efficacy in lymphocytic leukemia.

What clinical trials is NeoVax in?

NeoVax is being evaluated in a single Phase 1 clinical trial registered as NCT03219450. This trial is titled 'A Personalized Neoantigen Cancer Vaccine in Treatment Naïve, Asymptomatic Patients With IGHV Unmutated CLL.' The study is recruiting 15 participants in the United States and is currently active.

Is NeoVax a small molecule drug?

Yes, NeoVax is classified as a small molecule modality. It is a personalized neoantigen cancer vaccine designed to target specific mutations in a patient's tumor. The drug is being studied in an oncology setting for the treatment of lymphocytic leukemia.