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BEAM-103

Phase 1

Healthy Subjects | Small molecule | Other |Beam Therapeutics Inc.|Last Updated: Dec 26, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment30
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07304791This is a Phase 1, Randomized, Single-blind, Placebo-controlled Study to Assess the Safety, Pharmacokinetics (PK), and Pharmacodynamics (PD) of BEAM-103 in Healthy SubjectsPHASE1 RECRUITING 30Oct 27, 2025May 29, 2026Dec 26, 20251 United Kingdom
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Study Endpoints
Primary Endpoints
To determine the safety and tolerability of single ascending doses of BEAM-103
from enrollment to the end of study at 5 months

Incidence of treatment-emergent AEs, serious AEs, severe AEs, AEs related to BEAM-103

Secondary Endpoints
Change in Free Stem Cell Factor (SCF) in Peripheral Blood Over Time
from the start of treatment to the end of study at 5 months
Change in Tryptase Level in Peripheral Blood Over Time
from the start of treatment to the end of study at 5 months
Change in Reticulocyte Count in Peripheral Blood Over Time
From enrollment to end of study at 5 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingSINGLE
ModelSEQUENTIAL
PurposeBASIC_SCIENCE
Treatment Arms
ArmTypeDescription
BEAM-103 Drug ProductEXPERIMENTALBEAM-103 is a monoclonal antibody that will be administered in single dose ascending dose cohorts as an intravenous infusion through the arm.
PlaceboPLACEBO_COMPARATORNormal Saline Solution will be administered as a matching place in single dose ascending dose cohorts as an intravenous infusion through the arm.
Interventions
NameTypeDescription
BEAM-103DRUG• BEAM-103 is a monoclonal antibody administered as a single intravenous dose
Placebo ComparatorDRUG• The matching placebo comparator is administered as a single intravenous dose
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Eligibility Criteria
Age Range18 Years — 55 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion Criteria: * Ages 18 to ≤55 years * Body mass index (BMI) of 18.5 to 25 kg/m2 * Morning neutrophil count ≥2.6 × 109 cells/L for Black/African American subjects or ≥3.5 ×109 cells/L for Caucasian/Other subjects * Baseline hemoglobin value of ≥14 g/dL for males and ≥12 g/dL for females * Bas...

Countries:United Kingdom
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT07304791primaryCompletionDate: changed
LOWMay 24, 2026NCT07304791studyFirstPostDate: changed