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AZD7503 Intervention

Phase 1

Non-alcoholic Fatty Liver Disease | Small molecule | Metabolic |AstraZeneca PLC|Last Updated: Jul 20, 2025

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment19

FDA Designations

No designations recorded

Clinical trial landscape

AZD7503 Intervention · 1 trial · 6 indications

Phase 1 1
NCT05560607Knockdown of HSD17B13 mRNA, Pharmacokinetics, Safety, and Tolerability, of AZD7503 in Non-Alcoholic Fatty Liver DiseaseNon-alcoholic Fatty Liver Disease
COMPLETED19 Analytics
PHASE1COMPLETED
Knockdown of HSD17B13 mRNA, Pharmacokinetics, Safety, and Tolerability, of AZD7503 in Non-Alcoholic Fatty Liver Disease
Non-alcoholic Fatty Liver DiseaseUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of participants with Adverse Events (AEs).
99 days

To assess adverse events as a variable of safety and tolerability of AZD7503.

Secondary Endpoints

Change in HSD17B13 mRNA Expression
31 days
Number of participants with positive anti-drug antibodies to AZD7503
99 days
Area under plasma concentration time-curve from zero to infinity (AUCinf) of AZD7503
99 days
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeOTHER

Treatment Arms

ArmTypeDescription
Intervention/ DrugEXPERIMENTALInvestigation of the knockdown of hepatic HSD17B13 mRNA expression, PK, safety, and tolerability following multiple dose administration of AZD7503 in male participants and female participants of non-childbearing potential with NAFLD or NASH

Interventions

NameTypeDescription
AZD7503 InterventionDRUGPart A: Participants will be screened for histologic evidence of NAFLD or NASH and all eligibility criteria in part A prior to enrollment in part B. Part B: Participants consented to part B will be administered the study drug over the course of 31 days. At the end of the study a liver biopsy will be collected to measure for endpoints.
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Eligibility Criteria

Age Range18 Years to 70 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria # Part A 1. Participant must be ≥ 18 to ≤ 70 years of age at the time of signing the informed consent. 2. Participants with suspected or confirmed NAFLD or NASH including laboratory values with any of the following deviations at screening 1. ALT \> ULN, 2. Imaging demonstr...

Countries:United States
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Frequently asked questions about AZD7503 Intervention

What is AZD7503 used for?

AZD7503 is an investigational small molecule being developed for non-alcoholic fatty liver disease (NAFLD). It is designed to target the liver condition, which is also associated with nonalcoholic steatohepatitis (NASH). The drug is currently in Phase 1 clinical development and has not been approved by regulatory authorities.

What does AZD7503 target?

AZD7503 is designed to knock down HSD17B13 mRNA, according to its clinical trial title. This mechanism targets the HSD17B13 gene, which is linked to liver fat metabolism and the progression of non-alcoholic fatty liver disease. The drug is being studied for its effects on this molecular target in patients with NAFLD.

Who makes AZD7503?

AZD7503 is being developed by AstraZeneca PLC, a multinational pharmaceutical company listed on the stock exchange under the ticker AZN. The company is conducting clinical research on this investigational drug for the treatment of non-alcoholic fatty liver disease.

What phase is AZD7503 in?

AZD7503 is in Phase 1 clinical development. It is an investigational drug, meaning it has not been approved by the FDA or any other regulatory agency. The drug is still in early-stage clinical trials to evaluate its safety, tolerability, and pharmacokinetics in patients with non-alcoholic fatty liver disease.

What clinical trials is AZD7503 in?

AZD7503 has been studied in one clinical trial, identified as NCT05560607. This Phase 1 study, titled 'Knockdown of HSD17B13 mRNA, Pharmacokinetics, Safety, and Tolerability, of AZD7503 in Non-Alcoholic Fatty Liver Disease,' has been completed. The trial enrolled 19 participants in the United States and was not randomized or double-blinded.

Is AZD7503 the same as any other drug?

AZD7503 is the primary name for this investigational drug, and no alternative names have been reported. It is a distinct small molecule being developed by AstraZeneca for non-alcoholic fatty liver disease. Patients and healthcare providers should refer to it by its official name, AZD7503, in clinical and research contexts.