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ALXN2060

Phase 3

Symptomatic Transthyretin Amyloid Cardiomyopathy | Small molecule | Cardiovascular |AstraZeneca PLC|Last Updated: Jun 10, 2026

Success Probability

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment25

FDA Designations

No designations recorded

Clinical trial landscape

ALXN2060 · 1 trial · 1 indication

Phase 3 1
NCT04622046A Phase 3 Study of ALXN2060 in Japanese Participants With Symptomatic ATTR-CMSymptomatic Transthyretin Amyloid Cardiomyopathy
COMPLETED25 Analytics
PHASE3COMPLETED
A Phase 3 Study of ALXN2060 in Japanese Participants With Symptomatic ATTR-CM
Symptomatic Transthyretin Amyloid CardiomyopathyUnlock trial analytics

Study Endpoints

Primary Endpoints

Part A: Change From Baseline To Month 12 Of Treatment In Distance Walked During The Six-minute Walk Test (6MWT)
Baseline, Month 12

The 6MWT measures how far a participant can walk in 6 minutes. Change from baseline was calculated as the difference between the distance walked during the 6MWT at 12 months and the distance walked during the 6MWT at baseline. To determine the baseline, at least 2 6MWTs were conducted \> 24 hours to ≤ 3 weeks apart prior to the first dose of ALXN2060. The baseline 6MWT is the average of the total distance walked by participants for the 2 qualifying 6MWTs that met all the protocol-defined criteria. Least squares mean change from baseline data were adjusted for baseline measures and visits.

Parts A and B: Number of Cardiovascular (CV)-Related Hospitalizations Over A 30-month Period
30 months

CV-related hospitalization was defined as the mean number of CV-related hospitalizations per participant per year over a 30-month period. CV-related hospitalizations were also reported as adverse events and were reviewed and adjudicated by an independent Clinical Events Committee (CEC).

All-cause Mortality (ACM) Over A 30-month Period
30 months

ACM was assessed as time from the date of first initiation of study treatment to the date of death during a 30-month period, and was analyzed using Kaplan-Meier analysis. Data are reported for the number of participants with ACM over the 30-month period.

Secondary Endpoints

Parts A and B: Change From Baseline In Distance Walked During The 6MWT
Baseline, Months 6, 9, 18, 24 and 30
Parts A and B: Change From Baseline In The Kansas City Cardiomyopathy Questionnaire Overall Score (KCCQ-OS)
Baseline, Months 6, 9, 12, 18, 24 and 30
Parts A and B: Number of Participants With Treatment-emergent Adverse Events (AEs), Serious Adverse Events (SAEs) and AEs Leading to Treatment Discontinuation
Up to Month 30
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
ALXN2060EXPERIMENTALParticipants will receive ALXN2060.

Interventions

NameTypeDescription
ALXN2060DRUGALXN2060 tablets will be administered twice daily at a dose of 800 milligrams.
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Eligibility Criteria

SexALL
Healthy VolunteersNo
Study Sites11

Inclusion Criteria: 1. Established diagnosis of ATTR-CM with either wild-type TTR or a variant TTR genotype. 2. History of heart failure evidenced by at least 1 prior hospitalization for heart failure or clinical evidence of heart failure without prior heart failure hospitalization manifested by si...

Countries:Japan
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Recent Changes (Last 90 Days)

MEDIUMJul 11, 2026NCT04622046TRIAL_REMOVED: changed
MEDIUMJul 11, 2026NCT04622046TRIAL_REMOVED: changed
MEDIUMJul 11, 2026NCT04622046TRIAL_REMOVED: changed

Frequently asked questions about ALXN2060

What is ALXN2060 used for?

ALXN2060 is an investigational small molecule being developed for the treatment of symptomatic transthyretin amyloid cardiomyopathy (ATTR-CM), a condition in which abnormal protein deposits accumulate in the heart muscle and impair its function. It is currently in Phase 3 clinical development.

Who is developing ALXN2060?

ALXN2060 is being developed by AstraZeneca PLC, a biopharmaceutical company traded on the NASDAQ under the ticker symbol AZN. The drug is currently in Phase 3 clinical development for symptomatic transthyretin amyloid cardiomyopathy.

What phase is ALXN2060 in?

ALXN2060 is in Phase 3 clinical development. It is an investigational drug and has not been approved by regulatory authorities. A Phase 3 study of ALXN2060 in Japanese participants with symptomatic transthyretin amyloid cardiomyopathy has been completed.

What clinical trials is ALXN2060 in?

ALXN2060 has been studied in a Phase 3 clinical trial registered as NCT04622046, titled "A Phase 3 Study of ALXN2060 in Japanese Participants With Symptomatic ATTR-CM." This trial enrolled 25 participants in Japan and has been completed.

Is ALXN2060 the same as any other drug?

ALXN2060 is the drug name used in clinical development. No alternative names have been reported for this investigational compound. It is being studied for symptomatic transthyretin amyloid cardiomyopathy and is not yet approved for any use.