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empasiprubart

Phase 3

Chronic Inflammatory Demyelinating Polyneuropathy | Monoclonal antibody | Neurology |argenx SE|Last Updated: Aug 13, 2026

Target and mechanism

ModalityMonoclonal antibody

Also known as Empasiprubart IV, empasiprubart IV

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLEDDMC
Total Trials2
Total Enrollment378

FDA Designations

No designations recorded

Clinical trial landscape

empasiprubart · 7 trials · 14 indications

Phase 3 3Phase 2 3Phase 1 1
NCT07091630A Study to Assess the Efficacy and Safety of Empasiprubart in Adults With CIDPChronic Inflammatory Demyelinating Polyneuropathy
RECRUITING160 Analytics
NCT06920004A Study to Assess Efficacy and Safety of Empasiprubart Versus IVIg in Adults With CIDPChronic Inflammatory Demyelinating Polyneuropathy
RECRUITING218 Analytics
NCT06742190A Study to Assess the Efficacy and Safety of Empasiprubart Versus IVIg in Adults With Multifocal Motor NeuropathyMultifocal Motor Neuropathy (MMN)
ACTIVE NOT_RECRUITING154 Analytics
PHASE3RECRUITING
A Study to Assess the Efficacy and Safety of Empasiprubart in Adults With CIDP
Chronic Inflammatory Demyelinating PolyneuropathyUnlock trial analytics
PHASE3RECRUITING
A Study to Assess Efficacy and Safety of Empasiprubart Versus IVIg in Adults With CIDP
Chronic Inflammatory Demyelinating PolyneuropathyUnlock trial analytics
PHASE3ACTIVE NOT_RECRUITING
A Study to Assess the Efficacy and Safety of Empasiprubart Versus IVIg in Adults With Multifocal Motor Neuropathy
Multifocal Motor Neuropathy (MMN)Unlock trial analytics

Study Endpoints

Primary Endpoints

Reduction of ≥1 point compared with baseline in aINCAT score at week 24
Up to 24 weeks

The Adjusted Inflammatory Neuropathy Cause and Treatment Disability Score (aINCAT) score is a 10-point scale that covers the functionality of legs and arms. The score varies between 0 and 10 (higher score, worse outcome).

Change from baseline in grip strength (4-week average) in the most affected hand at week 24
Up to 24 weeks
Empasiprubart serum concentrations as input for a population PK-driven analysis to determine the effect of age and body size on CL and Vd
Up to 8 weeks

CL = Clearance; Vd = apparent volume of distribution.

Free and total C2 levels as input for PK/PD modeling analysis
Up to 8 weeks

C2 = complement component 2.

Incidence of adverse events and serious adverse events in the DBTP
Up to 12 weeks
Incidence of adverse events (AEs)
Up to 90 weeks
Percentage of participants discontinuing investigational medicinal product (IMP) due to an adverse event (AE)
Up to 25 weeks
Change from baseline in nerve CSA at week 24 as measured by ultrasound imaging of the median nerve and brachial plexus (individual nerves and average sum score)
Up to 48 weeks

CSA : cross-sectional area

Secondary Endpoints

Change from baseline in I-RODS centile points score
Up to 24 weeks (part A) + 96 weeks (Part B)
Change from baseline in MRC-SS at week 24
Up to 24 weeks
Change from baseline in grip strength (3-day moving average) in the dominant hand at week 24
Up to 24 weeks
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Part A - EmpasiprubartEXPERIMENTALParticipants receive empasiprubart during part A
Part A - PlaceboPLACEBO_COMPARATORParticipants receive placebo during part A
Part B - EmpasiprubartEXPERIMENTALParticipants receive empasiprubart during part B. Participants from the empasiprubart arm in part A will receive placebo once to maintain the blind of part A.
Part A - empasiprubart + IVIg-placeboEXPERIMENTALDuring Part A, participants receive empasiprubart and a placebo resembling the IVIg treatment in this arm.
Part A - IVIg + empasiprubart-placeboACTIVE_COMPARATORDuring Part A, participants receive IVIg and a placebo resembling the empasiprubart treatment in this arm.
Empasiprubart IVEXPERIMENTALParticipants will receive empasiprubart IV
Placebo IVPLACEBO_COMPARATORParticipants receive placebo IV in the DBTP
Efgartigimod PH20 SC PFSOTHERParticipants receive open-label efgartigimod PH20 SC PFS in the safety follow-up period
EmpasiprubartEXPERIMENTALPatients receiving Empasiprubart IV
PlaceboPLACEBO_COMPARATORPatients receiving Placebo IV

Interventions

NameTypeDescription
Empasiprubart IVBIOLOGICALIntravenous infusion of empasiprubart
Placebo IVOTHERIntravenous infusion of placebo
empasiprubartBIOLOGICALIntravenous infusion of empasiprubart
IVIgBIOLOGICALIntravenous infusion of IVIg
empasiprubart-placeboOTHERA placebo resembling the empasiprubart treatment
IVIg-placeboOTHERA placebo resembling the IVIg treatment
IVIG (Intravenous Immunoglobulin)BIOLOGICALIntravenous infusion of IVIg
Efgartigimod PH20 SC PFSCOMBINATION_PRODUCTSubcutaneous administration of efgartigimod PH20 via pre-filled syringe (PFS)
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites71

Inclusion Criteria: * Meets criteria for CIDP based on EAN/PNS Task Force CIDP guidelines, second revision (2021) * Has either typical CIDP or 1 of the following CIDP variants: motor CIDP (including motor-predominant CIDP), multifocal CIDP (also known as Lewis-Sumner syndrome), focal CIDP, or dista...

Countries:United StatesArgentinaAustriaBrazilBulgariaChinaCzechiaDenmarkEstoniaFranceGeorgiaGreeceHungaryItalyJapanMoldovaNetherlandsPolandRomaniaSingaporeSlovakiaSouth KoreaUnited KingdomColombiaGermanyIsraelNorwayPortugalSerbiaSloveniaSpainSwedenSwitzerlandTurkey (Türkiye)AustraliaBelgiumCanadaLatviaLithuania
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Recent Changes (Last 90 Days)

LOWAug 14, 2026NCT07610564Status: NOT_YET_RECRUITING → RECRUITING
LOWAug 14, 2026NCT07610564Status: NOT_YET_RECRUITING → RECRUITING
LOWAug 14, 2026NCT07610564Status: NOT_YET_RECRUITING → RECRUITING
LOWJul 24, 2026NCT07673627Status: NOT_YET_RECRUITING → RECRUITING
LOWJul 24, 2026NCT07673627Status: NOT_YET_RECRUITING → RECRUITING
LOWJul 22, 2026NCT07091630lastUpdatePostDate: changed
LOWJul 22, 2026NCT07091630lastUpdatePostDate: changed
LOWJul 21, 2026NCT06920004lastUpdatePostDate: changed
LOWJun 29, 2026NCT07673627NEW_TRIAL: changed
LOWJun 29, 2026NCT07673627NEW_TRIAL: changed
LOWJun 12, 2026NCT07091630lastUpdatePostDate: changed
LOWJun 12, 2026NCT06920004lastUpdatePostDate: changed
LOWJun 12, 2026NCT07091630lastUpdatePostDate: changed
LOWJun 12, 2026NCT06920004lastUpdatePostDate: changed
LOWJun 10, 2026NCT07638566NEW_TRIAL: changed
LOWJun 10, 2026NCT07638566NEW_TRIAL: changed
LOWMay 29, 2026NCT07091630lastUpdatePostDate: changed
LOWMay 29, 2026NCT07610564NEW_TRIAL: changed
LOWMay 29, 2026NCT07091630lastUpdatePostDate: changed
LOWMay 29, 2026NCT07610564NEW_TRIAL: changed

Frequently asked questions about empasiprubart

What is Empasiprubart used for?

Empasiprubart is an investigational monoclonal antibody being developed for neurological conditions including Multifocal Motor Neuropathy (MMN), Chronic Inflammatory Demyelinating Polyneuropathy (CIDP), Chronic Inflammatory Demyelinating Polyradiculoneuropathy, Dermatomyositis, and AChR-Ab Seropositive Generalized Myasthenia Gravis. It is administered intravenously and is currently in Phase 2 clinical development.

Who makes Empasiprubart?

Empasiprubart is being developed by argenx SE, a biopharmaceutical company traded on the NASDAQ under the ticker ARGX. The company is conducting clinical trials for this investigational monoclonal antibody in neurological indications.

What phase is Empasiprubart in?

Empasiprubart is in Phase 2 clinical development. It is an investigational drug and has not been approved by regulatory authorities. Clinical trials are ongoing to assess its efficacy and safety in conditions such as Multifocal Motor Neuropathy and Chronic Inflammatory Demyelinating Polyneuropathy.

What clinical trials is Empasiprubart in?

Empasiprubart is being studied in several clinical trials. NCT06742190 compares it to IVIg in adults with Multifocal Motor Neuropathy. NCT06920004 and NCT07091630 assess it versus IVIg or alone in adults with CIDP. NCT07610564 evaluates its effect on nerve morphology by ultrasound in Multifocal Motor Neuropathy.

Is Empasiprubart the same as empasiprubart IV?

Yes, Empasiprubart and empasiprubart IV refer to the same drug. The intravenous formulation is the route of administration used in clinical trials for this investigational monoclonal antibody being developed by argenx SE.

Is Empasiprubart FDA approved?

Empasiprubart is not FDA approved. It is an investigational drug currently in Phase 2 clinical development. It is being studied in clinical trials for neurological conditions, but it has not received regulatory approval for any use.