Recent Updates
Recently added Catalysts

ARGX-113

Phase 2

Primary Immune Thrombocytopenia | Small molecule | Hematology |argenx SE|Last Updated: Jul 25, 2023

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment38
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03102593A Study to Evaluate the Safety, Efficacy, and Pharmacokinetics of ARGX-113 in Patients With ITPPHASE2 COMPLETED 38Mar 13, 2017Apr 9, 2019Jul 25, 202330 Austria, Belgium +8
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Incidence and severity of serious adverse events (SAEs).
After the first administration of Investigational Medicinal Product day 1 to 30 days of a patient's last visit.

Changes from Baseline in vital signs, electrocardiogram parameters (ECGs), physical examination abnormalities and clinical laboratory assessments.

Secondary Endpoints
Frequency and proportion of patients with initial response
Over the study period (up to 13 weeks).
Unlock Study Endpoints
Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
ARGX-113 Dose A + SoCEXPERIMENTALPatients will be randomized in a 1:1:1 ratio to ARGX-113 (Dose A or Dose B) or placebo
ARGX-113 Dose B +SoCEXPERIMENTALPatients will be randomized in a 1:1:1 ratio to ARGX-113 (Dose A or Dose B) or placebo
Placebo + SoCPLACEBO_COMPARATORPatients will be randomized in a 1:1:1 ratio to ARGX-113 (Dose A or Dose B) or placebo
Interventions
NameTypeDescription
ARGX-113DRUGARGX-113 (Dose A or Dose B) or matching placebo will be administered IV weekly
PlaceboOTHERARGX-113 (Dose A or Dose B) or matching placebo will be administered IV weekly
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — 85 Years
SexALL
Healthy VolunteersNo
Study Sites30

Inclusion Criteria: 1. Male or female patients aged ≥ 18 to ≤ 85 years. 2. Must receive SoC treatment for ITP that has been stable in dose and frequency for at least 4 weeks prior to Screening. SoC may include oral corticosteroids and/or permitted oral immunosuppressants and/or TPO-R agonist. 3. Co...

Countries:AustriaBelgiumCzechiaFranceGermanyHungaryPolandSpainUkraineUnited Kingdom
Unlock Eligibility Criteria