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Omitted Doxorubicin

Phase 3

Leukemia, Acute Lymphoblastic | Small molecule | Oncology |Amgen Inc.|Last Updated: May 5, 2026

Success Probability

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Market & Valuation

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Trial Design

RandomizedNO_TREATMENT_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment6,430

FDA Designations

No designations recorded

Clinical trial landscape

Omitted Doxorubicin · 1 trial · 1 indication

Phase 3 1
NCT04307576A Treatment Study Protocol for Participants 0-45 Years With Acute Lymphoblastic LeukaemiaLeukemia, Acute Lymphoblastic
RECRUITING6,430 Analytics
PHASE3RECRUITING
A Treatment Study Protocol for Participants 0-45 Years With Acute Lymphoblastic Leukaemia
Leukemia, Acute LymphoblasticUnlock trial analytics

Study Endpoints

Primary Endpoints

Event-free survival (EFS) for the whole protocol
5 year estimates from the time of diagnosis will be measured but adequate follow-up for these estimates will be ensured: at least 5 years follow-up.

The primary endpoint for the whole protocol (compared with the legacy protocols of the participating study-groups forming the consortium) is event-free survival (EFS) - as defined in the protocol.

Event-free survival (EFS) for the TKI intervention
From the start of TKI (day 15 or day 30), 5 year estimates will be measured but adequate follow-up for these estimates will be ensured: at least 5 years follow-up for all interventions except Inotuzumab-randomisation (minimum 2-year follow-up).

The primary endpoint for the TKI intervention is event-free survival (EFS) - as defined in the protocol, from the start of TKI until event or end of follow-up

Disease-free survival (DFS) R1 + R2
5 and 8 year estimates from the time of randomisation will be measured but adequate follow-up for these estimates will be ensured: at least 5 years follow-up.

The primary endpoint for Randomisation 1 and 2 is disease-free survival (DFS) - as defined in the protocol counting from the time of randomisation

Disease-free survival (DFS) R3
5 year estimates from the time of randomisation will be measured but adequate follow-up for these estimates will be ensured: at least 2-year follow-up

The primary endpoint for Randomisation 3 and the ABL-class fusion intervention is disease-free survival (DFS) - as defined in the protocol counting from the time of randomisation (R3) and the start of TKI-therapy (ABL-class fusion intervention).

MRD response after 1 cycle of Blinatumomab
End of first Blinatumomab infusion +/- 1 week

Fraction of patients with undetectable MRD ("Complete MRD response") at the end of one cycle of Blinatumomab (+/- 1 week)

Secondary Endpoints

Overall survival (OS) for the whole protocol
5 year estimates will be measured but adequate follow-up for these estimates will be ensured: at least 5 years follow-up.
Overall survival (OS) for R1 + R2
5 and 8 year estimates will be measured but adequate follow-up for these estimates will be ensured: at least 5 years follow-up.
Overall survival (OS) for R3
5 year estimates will be measured but adequate follow-up for these estimates will be ensured: at least 2 years follow-up
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
R1 - SR standard armNO_INTERVENTIONStandard risk arm receiving standard treatment (Delayed Intensification including Doxorubicin).
R1 - SR experimental armEXPERIMENTALStandard risk arm, receiving Delayed Intensification without Doxorubicin IV 3 x 30 mg/m2/dose.
R2 - IR-low standard armNO_INTERVENTIONStandard treatment with Delayed Intensification including Doxorubicin and Maintenance including Vincristine+Dexamethasone pulses.
R2 - IR-low experimental arm AEXPERIMENTALStandard treatment with omission of Doxorubicin IV 3 x 30 mg/m2/dose in the Delayed Intensification phase.
R3 - IR-high standard armNO_INTERVENTIONIntermediate risk high arm receiving Standard Maintenance Therapy.
R3-InO - IR-high experimental armEXPERIMENTALInotuzumab IV 0,5 mg/m2, given on days 253, 260, 267 and on days 274, 281, 288 before start of Standard Maintenance Therapy.
ABL-class fusions interventionEXPERIMENTALImatinib p.o. 340 mg/m2 given daily from day 15 or 30 (depending on age) to the end of therapy (week 106) in addition to Standard IR-high chemotherapy.
R3-TEAM - IR-high experimental armEXPERIMENTAL6-tioguanine p.o, 2,5-12,5 mg/m2, given daily in addition to Standard Maintenance Therapy.
ALLTogether1 DS Blinatumomab interventionEXPERIMENTALBlinatumomab IV, 5 mcg/m2/day up to 28 mcg/day (detailed dosing in protocol) continous infusion. Two 28 day courses with a two week treatment free interval in between. Blinatumomab courses replace Consolidation 1 and Consolidation 2 in the standard protocol adapted for Down syndrome patients.
R2 - IR-low experimental arm BEXPERIMENTALStandard treatment with omission of monthly pulses of Vincristine IV 1,5 mg/m2/dose and 5 days of Dexamethasone p.o. 6 mg/m2/day in the Maintenance Phase.

Interventions

NameTypeDescription
Omitted DoxorubicinDRUGOmission of IV Doxorubicin
Omitted Vincristine+Dexamethasone pulsesDRUGOmission of Vincristine+Dexamethasone pulses
Inotuzumab Ozogamicin+Standard Maintenance TherapyDRUGAddition of IV Inotuzumab ozogamicin before Maintenance Therapy
ImatinibDRUGp.o. Imatinib
6-tioguanine+Standard Maintenance TherapyDRUGAddition of p.o. 6-tioguanine to Standard Maintenance Therapy
BlinatumomabDRUGIV Blinatumomab
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Eligibility Criteria

Age Range0 Years to 45 Years
SexALL
Healthy VolunteersNo
Study Sites138

Inclusion Criteria: * Patients newly diagnosed with T-lymphoblastic (T-cell) or B-lymphoblastic precursor (BCP) leukaemia (ALL) according to the WHO-classification of Tumours of Haematopoetic and Lymphoid Tissues (Revised 4th edition 2017) and with a diagnosis confirmed by an accredited laboratory ...

Countries:BelgiumDenmarkEstoniaFinlandFranceGermanyIcelandIrelandLithuaniaNetherlandsNorwayPortugalSpainSwedenUnited Kingdom
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Frequently asked questions about Omitted Doxorubicin

What is Omitted Doxorubicin used for?

Omitted Doxorubicin is an investigational small molecule being studied for the treatment of acute lymphoblastic leukemia. It is currently in Phase 3 clinical development. The drug is being evaluated in a large, randomized, biomarker-selected trial enrolling patients aged 0 to 45 years with this condition.

Who makes Omitted Doxorubicin?

Omitted Doxorubicin is being developed by Amgen Inc., a biopharmaceutical company traded on the NASDAQ under the ticker symbol AMGN. The drug is currently in Phase 3 clinical development for acute lymphoblastic leukemia.

What phase is Omitted Doxorubicin in?

Omitted Doxorubicin is in Phase 3 clinical development. It is an investigational drug and has not been approved by regulatory authorities. The ongoing Phase 3 trial is actively recruiting participants with acute lymphoblastic leukemia.

What clinical trials is Omitted Doxorubicin in?

Omitted Doxorubicin is being studied in one active Phase 3 clinical trial, NCT04307576. This trial is a randomized, biomarker-selected study enrolling approximately 6,430 participants aged 0 to 45 years with acute lymphoblastic leukemia. The trial is recruiting in multiple European countries.

What does Omitted Doxorubicin target?

The specific molecular target of Omitted Doxorubicin has not been disclosed in available information. The drug is being studied in a biomarker-selected patient population, indicating that patient selection is based on specific biological markers, though the exact target is not specified.