Recent Updates
Recently added Catalysts

Ibrutinib

Phase 2

Waldenstrom Macroglobulinemia | Small molecule | Hematology |Amgen Inc.|Last Updated: Apr 4, 2025

Target and mechanism

Molecular targetBTK
Target classInhibitor
ModalitySmall molecule

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedACTIVE_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment99

FDA Designations

No designations recorded

Clinical trial landscape

Ibrutinib · 1 trial · 1 indication

Phase 2 1
NCT04263480Efficacy and Safety of Carfilzomib in Combination With Ibrutinib vs Ibrutinib in Waldenström's MacroglobulinemiaWaldenstrom Macroglobulinemia
ACTIVE NOT_RECRUITING99 Analytics
PHASE2ACTIVE NOT_RECRUITING
Efficacy and Safety of Carfilzomib in Combination With Ibrutinib vs Ibrutinib in Waldenström's Macroglobulinemia
Waldenstrom MacroglobulinemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

CR/VGPR
12 months

Primary endpoint is the rate of CR or VGPR 12 months after the start of treatment using the response criteria updated at the Sixth IWWM (CR/VGPR).

Secondary Endpoints

Response rate
12/ 24 months
Best response
12 months
Time to best response
12 months
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Arm A: Carfilzomib + IbrutinibEXPERIMENTALPatients will be treated with Ibrutinib until evidence of progressive disease or no longer tolerated. Patients will receive in addition Carfilzomib for two years.
Arm B: IbrutinibACTIVE_COMPARATORPatients will be treated with Ibrutinib until evidence of progressive disease or no longer tolerated.

Interventions

NameTypeDescription
Carfilzomib + IbrutinibDRUGCarfilzomib: Cycle 1, day 1: 20 mg/m² i.v. Cycle 1, day 8, day 15: 70 mg/m² i.v. Cycle 2 - 12, day 1, day 8, day 15: 70 mg/m² i.v. Cycle 13 - 24, day 1, day 15: 70 mg/m² i.v. Ibrutinib: 420 mg p.o daily until disease progression or non-tolerable toxicities
IbrutinibDRUGIbrutinib: 420 mg p.o daily until disease progression or non-tolerable toxicities
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites20

Inclusion Criteria: Each patient must meet all of the following inclusion criteria to be enrolled in this study: * Proven clinicopathological diagnosis of WM as defined by consensus panel one of the Second International Workshop on WM. Histopathology has to occur before randomization within the la...

Countries:AustriaGermanyGreece
Unlock Eligibility Criteria

Recent Changes (Last 90 Days)

LOWMay 24, 2026NCT04263480studyFirstPostDate: changed

Frequently asked questions about Ibrutinib

What is Ibrutinib used for in Waldenstrom Macroglobulinemia?

Ibrutinib is a small molecule being studied for the treatment of Waldenstrom Macroglobulinemia, a rare type of B-cell lymphoma. It is currently in Phase 2 clinical development as an investigational therapy for this condition.

What does Ibrutinib target?

Ibrutinib targets BTK, which stands for Bruton's tyrosine kinase. It is a BTK inhibitor, meaning it works by blocking the activity of this enzyme, which is involved in the growth and survival of malignant B cells in Waldenstrom Macroglobulinemia.

Who makes Ibrutinib?

Ibrutinib is being developed by Amgen Inc., a biopharmaceutical company. Amgen's stock is traded under the ticker symbol AMGN on the NASDAQ stock exchange.

What phase is Ibrutinib in?

Ibrutinib is currently in Phase 2 clinical trials for Waldenstrom Macroglobulinemia. It is an investigational drug, meaning it has not yet been approved by regulatory authorities and is still undergoing clinical evaluation.

What clinical trials is Ibrutinib in?

Ibrutinib is being studied in a Phase 2 clinical trial with the identifier NCT04263480. This trial is comparing the efficacy and safety of carfilzomib in combination with ibrutinib versus ibrutinib alone in patients with Waldenstrom's Macroglobulinemia. The trial is active but not recruiting participants.

Is Ibrutinib the same as any other drug?

Ibrutinib is a distinct drug and is not known by any other names. It is being studied as a monotherapy and in combination with carfilzomib in the ongoing clinical trial for Waldenstrom Macroglobulinemia.