Recent Updates
Recently added Catalysts

cinacalcet

Phase 3

Hyperparathyroidism, Primary | Small molecule | Endocrine |Amgen Inc.|Last Updated: Oct 17, 2018

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials3
Total Enrollment190
FDA Designations
No designations recorded
Clinical Trials (3)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00975221Efficacy and Safety Study of Cinacalcet for the Treatment of Hypercalcemia in Patients With Primary Hyperparathyroidism Unable to Undergo ParathyroidectomyPHASE3 COMPLETED 67Mar 10, 2010Dec 21, 2012Oct 17, 201847 United States, Australia +5
NCT00936988A Multicenter, Open-label Extension Study to Assess the Long-term Safety and Efficacy of an Oral Calcimimetic Agent AMG 073 (Cinacalcet) in Primary HyperparathyroidismPHASE2 COMPLETED 45Nov 1, 2000Dec 1, 2005May 8, 2013 -
NCT00936650A Study to Assess the Efficacy and Safety of Twice-Daily Dose Regimens of an Oral Calcimimetic Agent AMG 073 (Cinacalcet) in Primary Hyperparathyroidism (PHPT)PHASE2 COMPLETED 78Nov 1, 1999Jun 1, 2001May 8, 2013 -
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Percentage of Participants With Mean Corrected Total Serum Calcium Concentration ≤ 10.3 mg/dL (2.57 mmol/L) During the EAP
Efficacy assessment phase (study visits at Weeks 16, 20, 24, and 28)
Nature, frequency, severity, and relationship to treatment of adverse events
234 weeks
Proportion of subjects with the mean of the maintenance phase serum calcium measurements ≤ 10.3 mg/dL and with a mean decrease of at least 0.5 mg/dL
24 weeks
Secondary Endpoints
Percentage of Participants With a ≥ 1 mg/dL (0.25 mmol/L) Decrease From Baseline in Mean Corrected Total Serum Calcium Concentration During the EAP
Baseline and the EAP (mean of Weeks 16, 20, 24, and 28)
Percent Change From Baseline in Corrected Total Serum Calcium Concentration During the EAP
Baseline and the EAP (mean of Weeks 16, 20, 24, and 28)
Percent Change From Baseline in Plasma Parathyroid Hormone Level During the EAP
Baseline and the EAP (mean of Weeks 16, 20, 24, and 28)
Unlock Study Endpoints
Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
CinacalcetEXPERIMENTALParticipants received cinacalcet at a starting dose of 30 mg orally BID and were eligible for a dose titration once every 3 weeks during the 12-week dose-titration phase based on corrected total serum calcium concentration and safety assessments. Participants continued to receive cinacalcet for another 16 weeks during the efficacy assessment phase and then continued into the open-label extension phase and received cinacalcet at a starting dose of 30 mg BID for 24 weeks. The dose of cinacalcet could have been increased or decreased as needed to maintain a corrected total serum calcium concentration within the normal range through Week 52.
PlaceboPLACEBO_COMPARATORParticipants received placebo orally twice a day (BID) for 12 weeks during the dose titration phase and for another 16 weeks during the efficacy assessment phase. Participants then continued into the open-label extension phase and received cinacalcet at a starting dose of 30 mg BID for 24 weeks. The dose of cinacalcet could have been increased or decreased as needed to maintain a corrected total serum calcium concentration within the normal range through Week 52.
Interventions
NameTypeDescription
CinacalcetDRUGAdministered orally at a starting dose of 30 mg twice a day (BID). Participants will be eligible for a dose titration once every 3 weeks during the placebo-controlled dose titration phase based on corrected total serum calcium concentration and safety assessments obtained the previous week. Doses may be sequentially increased to 60 mg BID, 90 mg BID, and 90 mg 3 times a day (TID).
PlaceboDRUGAdministered orally following the same tiitration regimen as the experimental arm.
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites47

Inclusion Criteria: * age ≥ 18 years * diagnosis of primary hyperparathyroidism (HPT) * subjects must have the following laboratory values: 1. local/historical laboratory result showing a corrected total serum calcium \> 1 mg/dL (0.25 mmol/L) above the upper limit of normal and ≤ 12.5 mg/d...

Countries:United StatesAustraliaCanadaHungaryPolandPortugalRussia
Unlock Eligibility Criteria