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CC-11050

Phase 2

Cutaneous Lupus Erythematosus | Small molecule | Immunology |Amgen Inc.|Last Updated: Jun 23, 2020

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment48
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01300208To Evaluate the Preliminary Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of CC-11050 in Subjects With Discoid Lupus Erythematosus and Subacute Cutaneous Lupus ErythematosusPHASE2 COMPLETED 48Oct 1, 2010Mar 1, 2013Jun 23, 202019 United States
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Study Endpoints
Primary Endpoints
Laboratory values from chemistry, hematology, urinalysis, inflammation/immunology panel that reveal clinically significant abnormalities and that may constitute a safety concern
Up to 21 weeks
Secondary Endpoints
Pharmacokinetics (PK)
Up to 21 weeks
To assess the clinical response rate of CC-11050 in subjects with discoid lupus erythematosus or sub acute lupus erythematosus using the Cutaneous Lupus Area and Severity Index Activity Score following 12-weeks of treatment
12 weeks
Pharmacokinetics
Up to 21 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Cohort 1EXPERIMENTALCC-11050 (50 milligrams twice per day and Placebo)
Cohort 2EXPERIMENTALCC-11050 (100 milligrams twice per day and Placebo)
Cohort 3EXPERIMENTALCC-11050 (200 milligrams twice per day and Placebo)
Interventions
NameTypeDescription
CC-11050DRUGCohort 1: 50 milligrams twice per day for 4 weeks Cohort 2: 100 milligrams twice per day for 8 weeks Cohort 3: 200 milligrams twice per day for 12 week
PlaceboOTHER -
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites19

Key Inclusion Criteria: * Subjects with a clinical diagnosis of discoid lupus erythematosus or sub acute lupus erythematosus for \> 16 weeks prior to screening and consistent histological findings on skin biopsy based on Gilliam classification who are candidates for systemic therapies (as determine...

Countries:United States
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