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anvumetostat

Phase 2

MTAP-deleted NSCLC | Small molecule | Oncology |Amgen Inc.|Last Updated: Jun 1, 2026

Success Probability

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Market & Valuation

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Trial Design

RandomizedCONTROLLED
Total Trials1
Total Enrollment61

FDA Designations

No designations recorded

Clinical trial landscape

anvumetostat · 5 trials · 7 indications

Phase 2 1Phase 1 4
NCT06593522A Phase 2 Study of Anvumetostat in Participants With MTAP-deleted Advanced NSCLC (MTAPESTRY 201)MTAP-deleted NSCLC
ACTIVE NOT_RECRUITING61 Analytics
PHASE2ACTIVE NOT_RECRUITING
A Phase 2 Study of Anvumetostat in Participants With MTAP-deleted Advanced NSCLC (MTAPESTRY 201)
MTAP-deleted NSCLCUnlock trial analytics

Study Endpoints

Primary Endpoints

Objective Response (OR) per RECIST 1.1
Up to 35 months
Objective response (OR) Measured by Computed Tomography (CT) or Magnetic Resonance Imaging (MRI) and Assessed per Response Evaluation Criteria in Solid Tumors v1.1 (RECIST 1.1)
Up to 35 months
Number of Participants Experiencing Treatment-emergent Adverse Events (TEAEs)
Up to 35 months
Number of Participants Experiencing Events of Interest (EOIs)
Up to 35 months
Maximum Concentration (Cmax) of anvumetostat
Cycle 1: Day 1 and Day 15 pre-dose, 0.5 hours, 1 hour, 2 hours, 4 hours, and 6 hours post-dose; Cycle 2: Day 1 and Day 15 pre-dose; Cycles 3-5: Day 1 pre-dose
Time to Cmax (Tmax) of anvumetostat
Cycle 1: Day 1 and Day 15 pre-dose, 0.5 hours, 1 hour, 2 hours, 4 hours, and 6 hours post-dose; Cycle 2: Day 1 and Day 15 pre-dose; Cycles 3-5: Day 1 pre-dose
Area Under The Concentration-time Curve (AUC) of anvumetostat
Cycle 1: Day 1 and Day 15 pre-dose, 0.5 hours, 1 hour, 2 hours, 4 hours, and 6 hours post-dose; Cycle 2: Day 1 and Day 15 pre-dose; Cycles 3-5: Day 1 pre-dose
Number of Participants Experiencing Dose Limiting Toxicities (DLT)
Up to approximately 21 days
Number of Participants Experiencing Treatment Emergent Adverse Events (TEAE)
Up to approximately 3 years

TEAEs are any event that occurred after the participant received study treatment. Any clinically significant changes in vital signs, electrocardiograms, and clinical laboratory tests that occurred after study treatment administration were recorded as TEAEs. A serious TEAE is any untoward medical occurrence in a clinical study participant after first dose irrespective of a causal relationship with the study treatment(s) that resulted in death, was immediately life threatening, required in-patient hospitalization or prolongation of existing hospitalization, resulted in persistent or significant disability/incapacity, a congenital anomaly/birth defect, or another medically important serious event.

Number of Participants Experiencing Serious Adverse Events (SAE)
Up to approximately 3 years

An SAE is defined as any AE that results in death, is life threatening, requires in-patient hospitalization or prolongation of existing hospitalization, results in persistent or significant disability/incapacity, is a congenital abnormality/birth defect or important medical events that do not meet the preceding criteria but based on appropriate medical judgment may jeopardize the participant or may require medical or surgical intervention to prevent any of the outcomes listed above.

Part 1: Number of Participants Experiencing Dose Limiting Toxicities (DLTs)
Day 1 up to Day 21
Part 1: Number of Participants Experiencing Treatment-emergent Adverse Events (TEAEs)
Day 1 up to approximately 2.5 years

Any clinically significant changes in vital signs, electrocardiogram (ECG), or clinical laboratory test results will be recorded as adverse events

Part 1: Number of Participants Experiencing Serious Adverse Events (SAEs)
Day 1 up to approximately 2.5 years
Part 2: Objective Response (OR) per modified Response Evaluation Criteria in Solid Tumors (RECIST) 1.1
Day 1 up to approximately 2.5 years
Parts 1 and 2: Number of Participants Who Experience a Dose-Limiting Toxicity (DLT)
28 days
Parts 1 and 2: Number of Participants Who Experience a Treatment-emergent Adverse Event (TEAE)
Up to approximately 3 years

Adverse events (AEs) are defined as any untoward medical occurrence in clinical study participant irrespective of a causal relationship with the study treatment. TEAEs are any event that occurs after the participant has received study treatment. Any clinically significant changes in vital signs, electrocardiograms (ECGs) and clinical laboratory tests will be recorded as TEAEs. Serious AEs (SAEs) are defined as any event that meets at least 1 of the following serious criteria: * Results in death (fatal) * Requires in-patient hospitalization or prolongation of existing hospitalization * Results in persistent or significant disability/incapacity * Is a congenital anomaly/birth defect * Other medically important serious event

Part 3: Objective Response Rate (ORR)
Up to approximately 3 years

Secondary Endpoints

Disease Control (DC) by BICR
Up to 35 months
Duration of Response (DOR) by BICR
Up to 35 months
Time to Response (TTR) by BICR
Up to 35 months
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Part 1: Dose EvaluationEXPERIMENTALParticipants will be randomized to receive one of 2 active dose levels of anvumetostat orally (PO) daily (QD) in 28 days cycles. Part 1 of the study will determine the recommended phase 2 dose (RP2D).
Part 2: Dose ExpansionEXPERIMENTALParticipants will receive anvumetostat PO QD in 28-day cycles at the RP2D.
Subprotocol A: Non-Small Cell Lung Cancer (NSCLC) Arm AEXPERIMENTALParticipants with MTAP-deleted NSCLC will receive a regimen of Anvumetostat orally (PO) and carboplatin, paclitaxel, and pembrolizumab intravenously (IV)
Subprotocol A: NSCLC Arm BEXPERIMENTALParticipants with MTAP-deleted NSCLC will receive a regimen of Anvumetostat PO and carboplatin, pemetrexed, and pembrolizumab IV
Subprotocol A: NSCLC Arm CEXPERIMENTALParticipants with MTAP-deleted NSCLC will receive a combination of Anvumetostat PO and pembrolizumab IV
Subprotocol B: NSCLC With KRasG12C MutationEXPERIMENTALParticipants with MTAP-deleted NSCLC and KRasG12C mutation will receive a combination of Anvumetostat and sotorasib PO
Subprotocol C: NSCLC With Brain MetastasesEXPERIMENTALParticipants with MTAP-deleted NSCLC with brain metastases will receive Anvumetostat PO
Subprotocol B: Pancreatic Ductal Adenocarcinoma (PDAC) Arm AEXPERIMENTALPart 1: Participants with MTAP-deleted PDAC will receive doses of Anvumetostat orally in combination with gemcitabine and nab-paclitaxel IV. Part 2: Participants with MTAP-deleted PDAC will receive the recommended dose of Anvumetostat in combination with gemcitabine and nab-paclitaxel.
Subprotocol B: PDAC Arm BEXPERIMENTALPart 1: Participants with MTAP-deleted PDAC will receive doses of Anvumetostat orally in combination with mFOLFIRINOX (irinotecan, fluorouracil, leucovorin calcium, oxaliplatin) IV. Part 2: Participants with MTAP-deleted PDAC will receive the recommended dose of Anvumetostat in combination with mFOLFIRINOX.
Subprotocol C: Dose ExplorationEXPERIMENTALPart 1: Participants with MTAP-deleted PDAC will receive oral doses of Anvumetostat and RMC-6236.
Subprotocol C: Dose ExpansionEXPERIMENTALPart 2: Participants with MTAP-deleted PDAC will receive oral doses of Anvumetostat andRMC-6236.
Part 1: Dose Exploration of Anvumetostat Combined With IDE397EXPERIMENTALParticipants will receive escalating doses of Anvumetostat and IDE397 administered orally (PO) in cycles of 21 days.
Part 2: Dose Expansion of Anvumetostat Combined With IDE397EXPERIMENTALAnvumetostat and IDE397 will be administered PO in cycles of 21 days.
Part 1a, Phase 1: Anvumetostat Monotherapy Dose ExplorationEXPERIMENTALParticipants with MTAP-null solid tumors will receive escalating doses of Anvumetostat to estimate the MTD and/or the RP2D.
Part 1c, Phase 1: Anvumetostat Monotherapy Dose ExpansionEXPERIMENTALParticipants will receive the identified MTD/RP2D of Anvumetostat in the following cohort: MTAP-null NSCLC.
Part 2a, Phase 1: Anvumetostat Dose Exploration + DocetaxelEXPERIMENTALParticipants with MTAP-null NSCLC will receive escalating doses of Anvumetostat + a fixed dose of docetaxel to estimate the MTD/RP2D of the combination.
Part 2b, Phase 1: Anvumetostat + Docetaxel Dose ExpansionEXPERIMENTALParticipants with MTAP-null NSCLC will receive the identified MTD/RP2D of Anvumetostat + docetaxel.
Part 3: Anvumetostat Phase 2EXPERIMENTALParticipants with MTAP-null solid tumors will receive Anvumetostat.
Part 1e, Phase 1: Anvumetostat Monotherapy Dose ExpansionEXPERIMENTALParticipants will receive the identified selected dose/MTD of Anvumetostat in the following cohort: MTAP-null BTC.
Part 1f, Phase 1: Anvumetostat Monotherapy Dose ExpansionEXPERIMENTALParticipants will receive the identified selected dose/MTD of Anvumetostat in the following cohort: MTAP-null head and neck squamous cell carcinoma (HNSCC).
Part 1g, Phase 1: Anvumetostat Monotherapy Dose ExpansionEXPERIMENTALParticipants will receive the identified selected dose/MTD of Anvumetostat in the following cohort: MTAP-null pancreatic adenocarcinoma.
Part 1h, Phase 1: Anvumetostat Monotherapy Dose ExpansionEXPERIMENTALParticipants will receive the identified selected dose/MTD of Anvumetostat in the following cohort: MTAP-null or lost MTAP expression solid tumors (other than lymphoma or primary brain tumor).
Part 1i, Phase 1: Anvumetostat Dose OptimizationEXPERIMENTALParticipants will receive a randomized dose optimization evaluation of Anvumetostat.
Part 1j, Phase 1: Anvumetostat DSPS Substudy (US Sites Only)EXPERIMENTALParticipants will receive doses of Anvumetostat and comparator Anvumetostat test tables at different times in a fasted state.
Part 1k, Phase 1: Anvumetostat Food Effect Substudy (US Sites Only)EXPERIMENTALParticipants will receive Anvumetostat once on a fasted state and once after eating a standardized high-fat, high calorie meal.
Part 1l, Phase 1: Anvumetostat Monotherapy Dose ExpansionEXPERIMENTALParticipants will receive the identified selected dose/MTD of Anvumetostat in the following cohort: MTAP-null esophageal/gastric cancer.
Part 1m, Phase 1: Anvumetostat Monotherapy Dose ExpansionEXPERIMENTALParticipants will receive the identified selected dose/MTD of Anvumetostat in the following cohort: MTAP-null glioma.

Interventions

NameTypeDescription
anvumetostatDRUGFilm-coated tablet
CarboplatinDRUGAdministered IV
PaclitaxelDRUGAdministered IV
PembrolizumabDRUGAdministered IV
PemetrexedDRUGAdministered IV
SotorasibDRUGAdministered PO
GemcitabineDRUGAdministered IV
Nab-paclitaxelDRUGAdministered IV
Modified FOLFIRINOXDRUGModified FOLFIRINOX consists of irinotecan, 5-FU, LV, and oxaliplatin administered IV
RMC-6236DRUGAdministered orally
IDE397DRUGAdministered PO
DocetaxelDRUGDocetaxel: Intravenous infusion
Comparator Anvumetostat Test TabletDRUGComparator Anvumetostat test tablet: Orally via tablet. Only participants in the DSPS group of the Part 1a, Phase 1: Anvumetostat Monotherapy Dose Exploration, and Part 1j, Phase 1 arms will receive comparator Anvumetostat test tablet.
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Eligibility Criteria

Age Range18 Years to 99 Years
SexALL
Healthy VolunteersNo
Study Sites91

Inclusion Criteria: * Histologically or cytologically confirmed metastatic or unresectable locally advanced MTAP-deleted (Homozygous deletion of MTAP) NSCLC * Participants will have received and progressed or experienced disease recurrence on or after receiving at least 1 prior systemic therapy for...

Countries:United StatesAustraliaBrazilCanadaChinaCzechiaHong KongJapanLatviaNetherlandsPortugalSingaporeSouth KoreaSwitzerlandTaiwanTurkey (Türkiye)ArgentinaAustriaBelgiumFranceGermanyGreeceItalyPolandSpainDenmarkUnited Kingdom
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Frequently asked questions about anvumetostat

What is Anvumetostat used for?

Anvumetostat is an investigational small molecule being studied for the treatment of MTAP-null solid tumors, including non-small-cell lung cancer, thoracic tumors, and advanced gastrointestinal, biliary tract, and pancreatic cancers. It is in Phase 1 clinical development and is not yet approved by the FDA.

What does Anvumetostat target?

Anvumetostat is a small molecule enzyme inhibitor, classified under the '-stat' target class. It is being studied in tumors with homozygous MTAP deletion or MTAP-null status, which are genetic alterations that may make cancer cells susceptible to this type of enzyme inhibition.

Who makes Anvumetostat?

Anvumetostat is being developed by Amgen Inc., a biopharmaceutical company traded on NASDAQ under the ticker AMGN. The company is conducting multiple Phase 1 clinical trials to evaluate the drug in various MTAP-null advanced solid tumor indications.

What phase is Anvumetostat in?

Anvumetostat is in Phase 1 clinical development. It is an investigational drug and has not received FDA approval. All four registered clinical trials for Anvumetostat are Phase 1 studies, with three currently active and one completed.

What clinical trials is Anvumetostat in?

Anvumetostat is being studied in four Phase 1 trials. NCT05094336 (MTAPESTRY 101) evaluates it alone in advanced MTAP-null solid tumors. NCT05975073 tests it with IDE397 in MTAP-null NSCLC and solid tumors. NCT06333951 (MTAPESTRY 104) studies it alone or combined in thoracic tumors. NCT06360354 (MTAPESTRY 103) evaluates it in gastrointestinal, biliary, and pancreatic cancers.

Is Anvumetostat the same as IDE397?

No, Anvumetostat is not the same as IDE397. Anvumetostat is an investigational small molecule enzyme inhibitor developed by Amgen. IDE397 is a separate drug being studied in combination with Anvumetostat in a Phase 1 clinical trial for MTAP-null solid tumors.