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Alendronate

Phase 3

Postmenopausal Osteoporosis | Small molecule | Endocrine |Amgen Inc.|Last Updated: Jul 25, 2014

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials2
Total Enrollment751
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00377819Study of Transitioning From Alendronate to DenosumabPHASE3 COMPLETED 504Sep 1, 2006Jul 1, 2008Jul 11, 2011 -
NCT00293813A Multicenter, Randomized Placebo Controlled Pilot MicroCT Study to Estimate the Effect of Treatment With Denosumab (AMG 162) and Alendronate Sodium in Postmenopausal Women With Low Bone Mineral DensityPHASE2 COMPLETED 247May 1, 2006Aug 1, 2008Jul 25, 2014 -
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Study Endpoints
Primary Endpoints
Percent Change From Baseline in Total Hip Bone Mineral Density
Baseline, 12 months

Bone Mineral Density Assessed by Dual Energy X-Ray Absorptiometry. Percent change calculated using \[(12 month value - baseline value) / baseline value\]\*100.

Cortical Thickness of Radius by XtremeCT Percent Change From Baseline at Month 12
12 months

Cortical Thickness measured by XtremeCT.

Secondary Endpoints
Percent Change From Baseline in Lumbar Spine Bone Mineral Density
Baseline, 12 months
Percent Change From Baseline in Serum C-Telopeptide-I (CTX-I)
Baseline, 3 months
Cortical Thickness of Tibia by XtremeCT Percent Change From Baseline at Month 12
12 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
denosumabEXPERIMENTAL -
alendronateACTIVE_COMPARATOR -
3PLACEBO_COMPARATORPlacebo for denosumab and placebo for alendronate
1EXPERIMENTALdenosumab and placebo for alendronate
2ACTIVE_COMPARATORPlacebo for denosumab and alendronate
Interventions
NameTypeDescription
alendronateDRUG70 mg oral QW
Denosumab (AMG 162)DRUG60 mg SC q 6 mos
DenosumabDRUGdenosumab 60 mg SC q 6 mos
PlaceboDRUGPlacebo for alendronate and placebo for denosumab
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Eligibility Criteria
Age Range55 Years — N/A
SexFEMALE
Healthy VolunteersNo

Inclusion Criteria: * Postmenopausal females 55 yrs or older * Received alendronate therapy for osteoporosis for at least 6 months prior to entry into study * Lumbar spine or total hip Bone Mineral Density (BMD) corresponding to T-score ≤ -2 and ≥ -4 Exclusion Criteria: * Vitamin D deficiency * A...

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