Recent Updates
Recently added Catalysts
RARE

Ultragenyx Receives Breakthrough Therapy Designation for GTX-102 in Angelman Syndrome

Key Takeaway: Ultragenyx Receives Breakthrough Therapy Designation for GTX-102 in Angelman Syndrome

Full Press Release Details

Ultragenyx Receives Breakthrough Therapy Designation for GTX-102 in Angelman Syndrome.
Last updated: Jun 27, 2025