Recent Updates
Recently added Catalysts
RARE

Ultragenyx Announces Top-Line Results from Phase 3 Study of Ace-ER in GNE Myopathy

Key Takeaway: Ultragenyx Announces Top-Line Results from Phase 3 Study of Ace-ER in GNE Myopathy

BiopharmaWatch Analysis

From our catalyst data and publicly available data · not financial advice
Best trade, last catalyst
+43%
120-day peak, hindsight
Typical move
2.9%
average across 6 past catalysts
Cash runway
~13 mo
Low dilution risk
Lead asset
BPS804
Phase 2 · Hypophosphatasia

Full Press Release Details

Ultragenyx Announces Top-Line Results from Phase 3 Study of Ace-ER in GNE Myopathy.
Last updated: Aug 22, 2017