Full Press Release Details
PRINCETON, N.J., Sept. 03, 2024 (GLOBE NEWSWIRE) -- Amicus Therapeutics (Nasdaq: FOLD), today announced that five posters across its development programs will be included at the Society for the Study of Inborn Errors of Metabolism (SSIEM) 2024 Annual Symposium, being held September 3-6, 2024 in Porto, Portugal.
Abstract Title: FollowME Fabry Pathfinders registry: patient-reported outcomes in a cohort of patients on migalastat treatment for at least two years (Poster #21180)
Presenter: Aleš Linhart, D.Sc., Charles University and General University Hospital in Prague, Prague, Czech Republic
Poster Session: Wednesday, September 4, 6:15 – 8:15 p.m. WET
Location: Poster Room, Rosa Mota Pavilion
Abstract Title: Quality of life of migalastat-treated adolescents with Fabry disease: results from the ASPIRE study and open-label extension (Poster #21202)
Presenter: Amarilis Sanchez-Valle, MD, University of South Florida Health, Tampa, U.S.A.
Poster Session: Wednesday, September 4, 6:15 – 8:15 p.m. WET
Location: Poster Room, Rosa Mota Pavilion
Abstract Title: Exploring the journey of patients living with Fabry disease in Poland (Poster #20789)
Presenter: Anna Moskal, The Association of Families with Fabry Disease, Wroclaw, Poland
Poster Session: Wednesday, September 4, 6:15 – 8:15 p.m. WET
Location: Poster Room, Rosa Mota Pavilion
Abstract Title: Post-baseline outcomes of the UK Early Access to Medicines Scheme registry for cipaglucosidase alfa plus miglustat in late-onset Pompe disease (Poster #20863)
Presenter: Elaine Murphy, MD, University College London Hospitals, London, U.K.
Poster Session: Wednesday, September 4, 6:15 – 8:15 p.m. WET
Guided Poster Walk: Thursday, September 5, 12:10 – 1:40 p.m. WET
Location: Poster Room, Rosa Mota Pavilion
Abstract Title: Miglustat: a first-in-class enzyme stabilizer for late-onset Pompe disease (Poster #20873)
Presenter: Mark Roberts, MD, Salford Royal NHS Foundation Trust, Greater Manchester Neurosciences Centre, Manchester, U.K.
Poster Session: Wednesday, September 4, 6:15 – 8:15 p.m. WET
Location: Poster Room, Rosa Mota Pavilion
For more information on the SSIEM 2024 Annual Symposium, please visit ssiem2024.org.
About Amicus Therapeutics
Amicus Therapeutics (Nasdaq: FOLD) is a global, patient-dedicated biotechnology company focused on discovering, developing and delivering novel high-quality medicines for people living with rare diseases. With extraordinary patient focus, Amicus Therapeutics is committed to advancing and expanding a pipeline of cutting-edge, first- or best-in-class medicines for rare diseases. For more information please visit the company’s website at www.amicusrx.com, and follow on X and LinkedIn.
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