Full Press Release Details
| Investor Contact | JSB-Partners Contact |
| Matthew P. Duffy | Wolfgang Stoiber |
| Managing Director | Managing Director |
| LifeSci Advisors LLC | JSB-Partners |
| Matthew@LifeSciAdvisors.com | wstoiber@jsb-partners.com |
| Phone: 212-915-0685 | Phone: 978-697-9753 |
Bioblast Pharma Reports Second Quarter
2017 Financial Results
Tel Aviv, Israel, - August
4, 2017 - Bioblast Pharma Ltd. (NasdaqCM: ORPN), a clinical-stage, orphan disease-focused biotechnology company,
today announced financial results for the second quarter ended June 30, 2017.
Second Quarter 2017 Financial
Results and Cash Position
Post Second Quarter 2017
Bioblast Pharma is a clinical-stage biotechnology company committed
to developing clinically meaningful therapies for patients with rare and ultra-rare genetic diseases. Bioblast is traded on the
NASDAQ under the symbol "ORPN." For more information, please visit our website: www.BioblastPharma.com, the content
of which is not incorporated herein by reference.
Forward Looking Statements
This press release contains forward-looking statements within
the meaning of the "safe harbor" provisions of the Private Securities Litigation Reform Act of 1995 and other Federal
securities laws. For example, we are using forward-looking statements when we discuss exploring partnership or merger opportunities,
and when we imply that our product candidate may successfully treat certain medical conditions. In addition, historic results of
scientific research and clinical and preclinical studies do not guarantee that the conclusions of future research or studies will
suggest identical or even similar conclusions or that historic results referred to in this press release would not be interpreted
differently, in light of additional research and clinical and preclinical study results. Because such statements deal with future
events and are based on Bioblast Pharma Ltd.'s current expectations, they are subject to various risks and uncertainties and actual
results, performance or achievements of Bioblast Pharma could differ materially from those described in or implied by the statements
in this press release, including those discussed under the heading "Risk Factors" in Bioblast Pharma's annual report
on Form 20-F filed with the Securities and Exchange Commission ("SEC") on February 24, 2017, and in any subsequent filings
with the SEC. Except as otherwise required by law, Bioblast Pharma disclaims any intention or obligation to update or revise any
forward-looking statements, which speak only as of the date hereof, whether as a result of new information, future events or circumstances
CONSOLIDATED STATEMENTS OF OPERATIONS
U.S. dollars in thousands, except share and per share amounts
| Three Months Ended | Six Months Ended | |||||||||||||||
| June 30 | June 30 | |||||||||||||||
| 2017 | 2016 | 2017 | 2016 | |||||||||||||
| (Unaudited) | (Unaudited) | (Unaudited) | (Unaudited) | |||||||||||||
| Research and development | $ | 883 | $ | 1,935 | $ | 1,982 | $ | 3,793 | ||||||||
| Pre-commercialization | 65 | 64 | 471 | 836 | ||||||||||||
| General and administrative | 703 | 1,723 | 1,838 | 3,585 | ||||||||||||
| Total operating expenses | 1,651 | 3,722 | 4,291 | 8,214 | ||||||||||||
| Loss from operations | (1,651 | ) | (3,722 | ) | (4,291 | ) | (8,214 | ) | ||||||||
| Financial income, net | 21 | 14 | 29 | 41 | ||||||||||||
| Loss before taxes on income | (1,630 | ) | (3,708 | ) | (4,262 | ) | (8,173 | ) | ||||||||
| Taxes on income | 3 | (23 | ) | 43 | 106 | |||||||||||
| Net loss | $ | (1,633 | ) | $ | (3,685 | ) | $ | (4,305 | ) | $ | (8,279 | ) | ||||
| Net loss attributable to Ordinary shareholders | $ | (1,633 | ) | $ | (3,685 | ) | $ | (4,305 | ) | $ | (8,279 | ) | ||||
| Net loss per share attributable to Ordinary shareholders - basic and diluted | $ | (0.10 | ) | $ | (0.22 | ) | $ | (0.26 | ) | $ | (0.54 | ) | ||||
| Weighted average number of Ordinary shares outstanding - basic and diluted | 16,452,126 | 16,391,770 | 16,421,948 | 15,429,877 |
CONSOLIDATED BALANCE SHEETS
U.S. dollars in thousands, except share amounts
| June 30, 2017 | December 31, 2016 | |||||||
| (Unaudited) | (Audited) | |||||||
| ASSETS | ||||||||
| CURRENT ASSETS: | ||||||||
| Cash and cash equivalents | $ | 5,163 | $ | 6,871 | ||||
| Short-term bank deposits | - | 3,007 | ||||||
| Receivables and prepaid expenses | 342 | 663 | ||||||
| Property and equipment, net | 9 | - | ||||||
| Total current assets | 5,514 | 10,541 | ||||||
| LONG-TERM ASSETS: | ||||||||
| Long-term assets | - | 18 | ||||||
| Property and equipment, net | - | 71 | ||||||
| Total long-term assets | - | 89 | ||||||
| TOTAL ASSETS | $ | 5,514 | $ | 10,630 | ||||
| LIABILITIES AND SHAREHOLDERS' EQUITY | ||||||||
| CURRENT LIABILITIES: | ||||||||
| Trade payables | $ | 89 | $ | 700 | ||||
| Other accounts payable | 703 | 1,231 | ||||||
| Total current liabilities | 792 | 1,931 | ||||||
| LONG-TERM LIABILITIES | - | - | ||||||
| SHAREHOLDERS' EQUITY: | ||||||||
| Ordinary shares of NIS 0.01 par value - 50,000,000 shares authorized at June 30, 2017 and December 31, 2016; Issued and outstanding shares 16,711,301 at June 30, 2017 and 16,391,770 at December 31, 2016 | 46 | 45 | ||||||
| Additional paid-in capital | 48,790 | 48,463 | ||||||
| Accumulated deficit | (44,114 | ) | (39,809 | ) | ||||
| Total stockholders' equity | 4,722 | 8,699 | ||||||
| TOTAL LIABILITIES AND SHAREHOLDERS' EQUITY | $ | 5,514 | $ | 10,630 |
CONSOLIDATED STATEMENTS OF CASH FLOWS
U.S. dollars in thousands
| Six Months Ended | ||||||||
| June 30 | ||||||||
| 2017 | 2016 | |||||||
| (Unaudited) | (Unaudited) | |||||||
| Cash flows from operating activities | ||||||||
| Net loss | $ | (4,305 | ) | $ | (8,279 | ) | ||
| Adjustments to reconcile net loss to net cash used in operating activities: | ||||||||
| Depreciation and disposal of property and equipment | 64 | 13 | ||||||
| Share based compensation | 328 | (256 | ) | |||||
| Interest on short-term deposit | 7 | 42 | ||||||
| Changes in operating assets and liabilities: | ||||||||
| Decrease (increase) in receivables and prepaid expenses | 321 | (33 | ) | |||||
| Decrease (increase) in long-term assets | 18 | (23 | ) | |||||
| Decrease in trade payables | (611 | ) | (793 | ) | ||||
| Increase (decrease) in other accounts payable | (528 | ) | (253 | ) | ||||
| Increase in long-term liabilities | - | (70 | ) | |||||
| Net cash used in operating activities | (4,706 | ) | (9,652 | ) | ||||
| Cash flow from investing activities | ||||||||
| Withdraw of short term deposits | 3,000 | 5,000 | ||||||
| Purchase of property and equipment | (2 | ) | (10 | ) | ||||
| Net cash used in investing activities | 2,998 | 4,990 | ||||||
| Cash flow from financing activities | ||||||||
| Proceeds from exercise of options | * | - | ||||||
| Issuance of shares and warrants, net | - | 6,090 | ||||||
| Net cash provided by financing activities | - | 6,090 | ||||||
| Increase (decrease) in cash and cash equivalents | (1,708 | ) | 1,428 | |||||
| Cash and cash equivalents, beginning of the year | 6,871 | 7,286 | ||||||
| Cash and cash equivalents, end of the year | $ | 5,163 | $ | 8,714 |