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Ascendis Pharma Reports Second Quarter 2024 Financial Results YORVIPATH approved by U.S. Food & Drug Administration (FDA) as the first and only treatment of hypoparathyroidism in adults TransCon CNP (navepe

Key Takeaway: Ascendis Pharma has reported its financial results for Q2 2024, revealing a total revenue of 36 million, down from 47.4 million in Q2 2023. The FDA has approved YORVIPATH, the first treatment for hypoparathyroidism in adults, showcasing the company's commitment to addressing unmet needs in rare diseases. Nevertheless, the company faced adjustments to previous sales estimates that negatively impacted revenue. Ascendis also reported a net loss of 109.4 million but indicated a positive outlook for SKYTROFA with expectations of reaching blockbuster status.

Market Sentiment Analysis

POSITIVE FACTORS

  • YORVIPATH has received FDA approval as the first treatment for hypoparathyroidism in adults.
  • SKYTROFA has achieved significant revenue growth and is well positioned for blockbuster status.
  • Ascendis Pharma has two FDA-approved products and is preparing for additional product launches.

CONCERNS & RISKS

  • Total revenue declined significantly, primarily due to negative adjustments related to sales deductions.
  • The company reported a net loss, although it was less than the loss in the same period the previous year.
  • R&D costs were still high despite having decreased from the previous year.

Full Press Release Details

Ascendis Pharma Reports Second Quarter 2024 Financial Results
YORVIPATH approved by U.S. Food & Drug Administration (FDA) as the first and only treatment of
hypoparathyroidism in adults
TransCon CNP (navepegritide) pivotal ApproaCH Trial topline results expected in the coming
SKYTROFA Q2 revenue of 26 million 134%
year-over-year volume growth offset by negative adjustment of 27 million, resetting market access for continued growth
Revising full year 2024 SKYTROFA revenue outlook to 220 - 240 million
Conference call today at 4:30 pm ET
COPENHAGEN, Denmark, September 3, 2024 (GLOBE NEWSWIRE) Ascendis Pharma A/S (Nasdaq: ASND) today announced financial results
for the second quarter ended June 30, 2024, and provided a business update.
The recent FDA approval of YORVIPATH demonstrates why our
unrelenting focus on helping patients suffering from hypoparathyroidism and other serious diseases with considerable unmet need is so important for Ascendis, said Jan Mikkelsen, Ascendis Pharma s President and Chief Executive Officer.
Already, two out of our three Endocrine Rare Disease TransCon product candidates have been approved by the FDA and European Commission. Our first, SKYTROFA, has achieved U.S. market value leadership, and, we believe, now with broader market
access, remains well positioned to reach blockbuster status in the U.S. alone. Looking forward, we are preparing for our second U.S. launch with YORVIPATH and are on track to report pivotal data in the coming weeks for our third TransCon product
candidate, TransCon CNP.
Select Highlights & Anticipated 2024 Milestones
(lonapegsomatropin, marketed as SKYTROFA)
(palopegteriparatide, marketed as YORVIPATH)
Second Quarter 2024 Financial Results
Total revenue for the second quarter of 2024 was 36.0 million, compared to 47.4 million during the same period for 2023. Results in the
quarter were primarily impacted by a negative adjustment to prior periods estimates and assumptions for sales deductions of 27.1 million, where 19.5 million and 7.6 million were attributable to the three months
ended March 31, 2024, and periods prior to January 1, 2024, respectively. This was partially offset by increased demand for SKYTROFA in the U.S. and revenue contribution from YORVIPATH. In addition,
non-product revenue was 4.6 million in the second quarter of 2024, compared to 11.5 million during the same period for 2023.
Total Revenue (In EUR 000s) Three Months Ended June 30, Six Months Ended June 30,
2024 2023 2024 2023
Revenue from external customers
Commercial sale of products 31,389 35,895 97,888 67,446
Licenses 869 589 25,639 1,203
Other 3,740 10,909 8,365 12,333
Total revenue from external customers 35,998 47,393 131,892 80,982
Research and development (R&D) costs for the second quarter of 2024 were 83.5 million, compared to
105.0 million during the same period in 2023. The decline was largely tied to lower external development costs for TransCon TLR 7/8 Agonist and lower costs for TransCon PTH, as well as lower employee costs as a result of the Eyconis spin-off.
Selling, general, and administrative (SG&A) expenses for the second quarter of 2024 were
74.3 million, compared to 70.3 million during the same period in 2023. The increase was primarily due to higher employee costs, including the impact from commercial expansion.
Total operating expenses for the second quarter of 2024 were 157.8 million compared to
175.3 million during the same period in 2023.
Net finance income for the second quarter of 2024 was 29.4 million compared to
a net finance income of 26.4 million during the same period in 2023.
For the second quarter of 2024, Ascendis Pharma reported a net loss of
109.4 million, or 1.91 per share (basic and diluted) compared to a net loss of 121.4 million, or 2.16 per share (basic and diluted) for the same period in 2023.
As of June 30, 2024, Ascendis Pharma had cash, cash equivalents, and marketable securities totaling 258.7 million compared to
399.4 million as of December 31, 2023. As of June 30, 2024, Ascendis Pharma had 58,231,484 ordinary shares outstanding, including 881,730 ordinary shares represented by ADSs held by the company.
Conference Call and Webcast Information
will host a conference call and webcast today at 4:30 pm Eastern Time (ET) to discuss its second quarter 2024 financial results.
Those who would like to
participate may access the live webcast here, or register in advance for the teleconference here. The link to the live webcast will also be available on the Investors & News section of the Ascendis Pharma website at
https://investors.ascendispharma.com. A replay of the webcast will be available on this section of the Ascendis Pharma website shortly after conclusion of the event for 30 days.
About Ascendis Pharma A/S
Ascendis Pharma is applying
its innovative TransCon technology platform to build a leading, fully integrated biopharma company focused on making a meaningful difference in patients lives. Guided by its core values of Patients, Science, and Passion, Ascendis uses its
TransCon technologies to create new and potentially best-in-class therapies. Ascendis is headquartered in Copenhagen, Denmark and has additional facilities in Europe and
the United States. Please visit ascendispharma.com to learn more.
Forward-Looking Statements
This press release contains forward-looking statements that involve substantial risks and uncertainties. All statements, other than statements of historical
facts, included in this press release regarding Ascendis future operations, plans and objectives of management are forward-looking statements. Examples of such statements include, but are not limited to, statements relating to (i) the
timing of topline results from the ApproaCH Trial, (ii) Ascendis expectations regarding full year 2024 SKYTROFA revenue, (iii) Ascendis expectations regarding SKYTROFA s potential to reach blockbuster status,
(iv) Ascendis plan to submit a supplemental Biologics License Application for SKYTROFA for adult growth hormone deficiency in the third quarter of 2024, (v) the timing of topline results from the Phase 2 trial of TransCon hGH in Turner
syndrome, (vi) Ascendis plan to submit a New Drug Application for TransCon CNP for children with achondroplasia, (vii) Ascendis expectations regarding completing manufacturing of YORVIPATH commercial product for the U.S. market
and the timing of initial supply, (viii) dialogue with FDA regarding commercialization of existing YORVIPATH manufactured product and, if agreed,
the potential timing of introduction, (ix) Ascendis expectations regarding initial revenue in France from YORVIPATH, (x) Ascendis plan to complete enrollment in the COACH
Trial, (xi) the timing of topline Week 26 data from the COACH Trial, (xii) the timing of initiating the teACH Phase 2 trial in adolescents, (xiii) Ascendis plan to present initial results from the Phase 2 dose expansion cohort
of the IL-Believe Trial, (xiv) Ascendis expectations regarding its total operating expenses for 2024, (xv) Ascendis expectation to be operating cash flow breakeven on a quarterly basis in 2024
or 2025, (xvi) Ascendis ability to apply its TransCon technology platform to build a leading, fully integrated biopharma company, and (xvii) Ascendis use of its TransCon technologies to create new and potentially best-in-class therapies. Ascendis may not actually achieve the plans, carry out the intentions or meet the expectations or projections disclosed in the forward-looking
statements and you should not place undue reliance on these forward-looking statements. Actual results or events could differ materially from the plans, intentions, expectations and projections disclosed in the forward-looking statements. Various
important factors could cause actual results or events to differ materially from the forward-looking statements that Ascendis makes, including the following: dependence on third party manufacturers, distributors and service providers for
Ascendis products and product candidates; unforeseen safety or efficacy results in Ascendis development programs or on-market products; unforeseen expenses related to commercialization of any
approved Ascendis products; unforeseen expenses related to Ascendis development programs; unforeseen selling, general and administrative expenses, other research and development expenses and Ascendis business generally; delays in the
development of its programs related to manufacturing, regulatory requirements, speed of patient recruitment or other unforeseen delays; Ascendis ability to obtain additional funding, if needed, to support its business activities; the impact of
international economic, political, legal, compliance, social and business factors. For a further description of the risks and uncertainties that could cause actual results to differ from those expressed in these forward-looking statements, as well
as risks relating to Ascendis business in general, see Ascendis Annual Report on Form 20-F filed with the U.S. Securities and Exchange Commission (SEC) on February 7, 2024 and Ascendis
other future reports filed with, or submitted to, the SEC. Forward-looking statements do not reflect the potential impact of any future licensing, collaborations, acquisitions, mergers, dispositions, joint ventures, or investments that Ascendis may
enter into or make. Ascendis does not assume any obligation to update any forward-looking statements, except as required by law.
Pharma, the Ascendis Pharma logo, the company logo, TransCon, SKYTROFA , and YORVIPATH are trademarks owned by the Ascendis Pharma
group. September 2024 Ascendis Pharma A/S.
Investor Contacts: Media Contact:
Tim Lee Melinda Baker
Ascendis Pharma Ascendis Pharma
+1 (650) 374-6343 +1 (650) 709-8875
tle@ascendispharma.com media@ascendispharma.com
ir@ascendispharma.com
FINANCIAL TABLES FOLLOW
Consolidated Statements of Profit
or Loss and Comprehensive Income / (Loss)
(In EUR 000s, except share and per share data) Three Months Ended June 30, Six Months Ended June 30,
2024 2023 2024 2023
Consolidated Statement of Profit or Loss
Revenue 35,998 47,393 131,892 80,982
Cost of sales 11,465 12,929 19,034 17,551
Gross profit 24,533 34,464 112,858 63,431
Research and development costs 83,478 105,021 154,165 211,134
Selling, general and administrative expenses 74,312 70,281 141,095 136,820
Operating profit/(loss) (133,257 ) (140,838 ) (182,402 ) (284,523 )
Share of profit/(loss) of associate (5,322 ) (7,451 ) (11,118 ) (8,677 )
Finance income 49,052 35,761 14,395 80,374
Finance expenses 19,624 9,334 58,553 18,652
Profit/(loss) before tax (109,151 ) (121,862 ) (237,678 ) (231,478 )
Income taxes/(expenses) (229 ) 429 (2,737 ) (868 )
Net profit/(loss) for the period (109,380 ) (121,433 ) (240,415 ) (232,346 )
Attributable to owners of the Company (109,380 ) (121,433 ) (240,415 ) (232,346 )
Basic and diluted earnings/(loss) per share (1.91 ) (2.16 ) (4.21 ) (4.14 )
Number of shares used for calculation (basic and diluted) 57,345,613 56,218,257 57,114,435 56,155,441
(EUR 000)
Consolidated Statement of Comprehensive Income or (Loss)
Net profit/(loss) for the period (109,380 ) (121,433 ) (240,415 ) (232,346 )
Items that may be reclassified subsequently to profit or loss:
Exchange differences on translating foreign operations 15 (1,016 ) 78 (1,803 )
Other comprehensive income/(loss) for the period, net of tax 15 (1,016 ) 78 (1,803 )
Total comprehensive income/(loss) for the period, net of tax (109,365 ) (122,449 ) (240,337 ) (234,149 )
Attributable to owners of the Company (109,365 ) (122,449 ) (240,337 ) (234,149 )
Consolidated Statements of Financial Position
(In EUR 000s) June 30, 2024 December 31, 2023
Assets
Non-current assets
Intangible assets 4,186 4,419
Property, plant and equipment 104,041 110,634
Investment in associates 20,564 5,686
Other receivables 2,186 2,127
130,977 122,866
Current assets
Inventories 251,199 208,931
Trade receivables 49,163 35,874
Income tax receivables 1,841 802
Other receivables 29,679 19,097
Prepayments 36,743 38,578
Marketable securities 7,275
Cash and cash equivalents 258,696 392,164
627,321 702,721
Total assets 758,298 825,587
Equity and liabilities
Equity
Share capital 7,819 7,749
Distributable equity (328,952 ) (153,446 )
Total equity (321,133 ) (145,697 )
Non-current liabilities
Borrowings 219,052 222,996
Contract liabilities 5,000 5,949
Deferred tax liabilities 7,644 5,830
231,696 234,775
Current liabilities
Convertible notes, matures in April 2028
Borrowings 432,190 407,095
Derivative liabilities 159,059 143,296
591,249 550,391
Other current liabilities
Borrowings 21,397 14,174
Contract liabilities 1,293 1,184
Trade payables and accrued expenses 99,527 94,566
Other liabilities 26,411 41,176
Income tax payables 1,090 2,299
Provisions 106,768 32,719
256,486 186,118
847,735 736,509
Total liabilities 1,079,431 971,284
Total equity and liabilities 758,298 825,587

Frequently Asked Questions

What recent FDA approval did Ascendis Pharma receive?

Ascendis Pharma received FDA approval for YORVIPATH, the first treatment for hypoparathyroidism in adults.

What was SKYTROFA's revenue in Q2 2024?

SKYTROFA generated $26 million in revenue for the second quarter of 2024.

What is Ascendis Pharma's revised SKYTROFA revenue outlook?

The revised revenue outlook for SKYTROFA in 2024 is $220 million to $240 million.

What was Ascendis Pharma's net loss in Q2 2024?

Ascendis Pharma reported a net loss of $109.4 million for the second quarter of 2024.

When will Ascendis hold its conference call?

Ascendis will have its conference call today at 4:30 pm ET.

Last updated: Sep 3, 2024