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Futibatinib

Phase 3

Biliary Tract Neoplasms | Small molecule | Oncology |Zymeworks Inc.|Last Updated: May 19, 2026

Target and mechanism

Molecular targetFGFR3, FGFR1, FGFR4, FGFR2
Target classInhibitor
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

RandomizedACTIVE_CONTROLLEDDMC
Total Trials1
Total Enrollment800

FDA Designations

No designations recorded

Clinical trial landscape

Futibatinib · 1 trial · 1 indication

Phase 3 1
NCT05615818Personalized Medicine for Advanced Biliary Cancer PatientsBiliary Tract Neoplasms
RECRUITING800 Analytics
PHASE3RECRUITING
Personalized Medicine for Advanced Biliary Cancer Patients
Biliary Tract NeoplasmsUnlock trial analytics

Study Endpoints

Primary Endpoints

Progression-free survival (PFS)
From randomisation to disease progression or death, up to 5 years.

Time from randomisation to the first documented progression of disease (PD) as assessed by the investigator according to RECIST v1.1, or death from any cause, whichever occurs first.

Secondary Endpoints

Overall Survival (OS)
From randomisation to death, up to 5 years.
Objective response rate
From randomisation, up to 5 years.
Time to treatment failure
From randomisation to treatment failure event, up to 5 years.
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
ExperimentalEXPERIMENTALMolecular targeted therapy matched to genetic alteration carried by the tumour
ControlACTIVE_COMPARATORContinued standard of care treatment for first-line biliary tract cancer

Interventions

NameTypeDescription
FutibatinibDRUGDose 20 mg once a day (QD)
IvosidenibDRUGDose 500 mg QD
ZanidatamabDRUGDose: Patients \< 70 kg: 1800 mg every 3 weeks (Q3W), Patients ≥ 70 kg: 2400 mg Q3W
TrastuzumabDRUGLoading dose 8 mg/kg, then 6 mg/kg Q3W (Combination with neratinib)
NeratinibDRUGDose: 240 mg QD (combination with trastuzumab)
EncorafenibDRUGDose: 450 mg QD (Combination with binimetinib)
BinimetinibDRUGDose: 45 mg twice a day (BID) (Combination with encorafenib)
NiraparibDRUGDose: 200 mg QD or 300 mg QD
CisplatinDRUGDose: 25 mg/m2 IV on days 1 and 8 Q3W (CISGEM)
GemcitabineDRUGDose: 1000 mg/m2 IV on days 1 and 8 Q3W (CISGEM)
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites69

SCREENING PHASE Inclusion Criteria: 1. Signed a written informed consent form prior to any trial specific procedures (Consent #1) 2. Histologically-proven intrahepatic, perihilar or distal cholangiocarcinoma, or gallbladder carcinoma (ampullary carcinoma excluded) 3. De novo or recurrent, locally ...

Countries:BelgiumFranceUnited Kingdom
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Frequently asked questions about Futibatinib

What is Futibatinib used for in Biliary Tract Neoplasms?

Futibatinib is an investigational small molecule being studied for the treatment of Biliary Tract Neoplasms, which are cancers of the bile ducts and gallbladder. It is currently in Phase 3 clinical development as part of a personalized medicine approach for advanced biliary cancer patients.

What does Futibatinib target?

Futibatinib targets fibroblast growth factor receptors (FGFR), specifically FGFR1, FGFR2, FGFR3, and FGFR4. It acts as an inhibitor of these receptors, which are involved in cell growth and proliferation. By inhibiting FGFR signaling, Futibatinib aims to slow or stop the growth of biliary tract cancer cells.

Who is developing Futibatinib?

Futibatinib is being developed by Zymeworks Inc., a biopharmaceutical company listed on the stock exchange under the ticker symbol ZYME. The company is conducting clinical trials to evaluate the drug's safety and efficacy in patients with biliary tract cancers.

What phase is Futibatinib in?

Futibatinib is currently in Phase 3 clinical development. It is an investigational drug, meaning it has not yet been approved by regulatory authorities. The ongoing Phase 3 trial is designed to assess its effectiveness compared to an active control in patients with advanced biliary cancer.

What clinical trials is Futibatinib in?

Futibatinib is being evaluated in a Phase 3 clinical trial registered as NCT05615818, titled 'Personalized Medicine for Advanced Biliary Cancer Patients.' This randomized, active-controlled study is recruiting 800 participants across Belgium, France, and the United Kingdom. The trial is open to adults aged 18 years and older.

Is Futibatinib the same as any other drug?

No alternative names for Futibatinib have been reported. It is identified by its chemical name and the ChEMBL identifier CHEMBL3701238. The drug is being developed under the name Futibatinib by Zymeworks Inc. and is not known to be marketed under any other brand name.