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Post-transplant Cyclophosphamide

Phase 2

Allogeneic Stem Cell Transplant Recipient | Small molecule | Other |Meridian Bioscience Inc|Last Updated: Mar 23, 2026

Target and mechanism

ModalitySmall molecule

Also known as Post-transplant Cyclophosphamide (PTCy)

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment209

FDA Designations

No designations recorded

Clinical trial landscape

Post-transplant Cyclophosphamide · 1 trial · 1 indication

Phase 2 1
NCT07214688Fludarabine and Intermediate-dose TBI Followed by PTCy in Patients Undergoing Allo Transplant for Heme MalignanciesAllogeneic Stem Cell Transplant Recipient
RECRUITING209 Analytics
PHASE2RECRUITING
Fludarabine and Intermediate-dose TBI Followed by PTCy in Patients Undergoing Allo Transplant for Heme Malignancies
Allogeneic Stem Cell Transplant RecipientUnlock trial analytics

Study Endpoints

Primary Endpoints

Overall survival (OS) at 1-year following treatment with fludarabine plus intermediate-dose total body irradiation (TBI 800 cGy) with post-transplant cyclophosphamide (PTCy)
Patient status (dead or alive) will be reviewed (e.g., through patient chart review,patient phone call, etc.) up through a period of 1 year

OS is defined as the time from the first dose of study treatment to the time of death due to any cause. Patients who are still alive will be censored at the date last known alive of the data cut-off date (if applicable), whichever is earlier.

Secondary Endpoints

Transplant-related mortality (TRM) at 1-year following treatment with fludarabine plus intermediate-dose total body irradiation (TBI 800 cGy) with post-transplant cyclophosphamide (PTCy)
Patient status (dead or alive) will be reviewed (e.g., through patient chart review,patient phone call, etc.) up through a period of 1 year
Incidence of grade III-IV acute GVHD following treatment with fludarabine plus intermediate-dose total body irradiation (TBI 800 cGy) with post-transplant cyclophosphamide (PTCy)
Patients will be assessed for acute GVHD symptoms weekly from day +7 until day +100. If acute GVHD symptoms remain active after day +100, weekly GVHD documentation will be encouraged until symptom(s) resolution, up through a period of 1 year
Incidence of chronic GVHD at 1-year following treatment with fludarabine plus intermediate-dose total body irradiation (TBI 800 cGy) with post-transplant cyclophosphamide (PTCy)
Patients will be assessed for chronic GVHD signs and/or symptoms at a minimum of every three months for the first year post-transplant.
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
ExperimentalEXPERIMENTALFludarabine and Intermediate-dose Total Body Irradiation (800 cGy) Followed by Post-transplant Cyclophosphamide

Interventions

NameTypeDescription
FludarabineDRUGPatients will receive fludarabine administered at the dose of 30 mg/m2 intravenously daily on Days -6 to -2
Intermediate-dose Total Body Irradiation (TBI)RADIATIONPatients will receive intermediate-dose total body irradiation (TBI) administered at the dose of 800 cGy in 4 total fractions, 2 fractions per day on Days -2 to -1
Post-transplant Cyclophosphamide (PTCy)DRUGPatients will receive post-transplant cyclophosphamide (PTCy) administered at the dose of 40 mg/kg intravenously on Days +3 to +4.
TacrolimusDRUGPatients will receive tacrolimus administered at a dose adjusted to maintain trough levels between 5-15 ng/mL orally starting on Days +5.
Mycophenolate mofetil (MMF)DRUGPatients will receive mycophenolate mofetil (MMF) administered at the standard dose of 15 mg/kg orally three times daily starting on Day +5 to Day +35 or per institutional guidelines.
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Eligibility Criteria

Age Range18 Years to 65 Years
SexALL
Healthy VolunteersNo
Study Sites3

Inclusion Criteria: * Patients ages 18-65 years. * Patients with a diagnosis of one of the following hematologic malignancies: * Acute myeloid leukemia or chronic myeloid leukemia with no circulating blasts and less than 5% blasts in the bone marrow; * Myelodysplastic syndrome with less than 5% bla...

Countries:United States
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Frequently asked questions about Post-transplant Cyclophosphamide

What is Post-transplant Cyclophosphamide used for?

Post-transplant Cyclophosphamide (PTCy) is used in allogeneic stem cell transplant recipients. It is being studied as part of a conditioning regimen for patients with hematologic malignancies undergoing allogeneic stem cell transplantation. The drug is currently in Phase 2 clinical development for this indication.

What does Post-transplant Cyclophosphamide target?

Post-transplant Cyclophosphamide is a small molecule that targets rapidly dividing cells, including activated T cells that cause graft-versus-host disease after allogeneic stem cell transplantation. By selectively depleting these cells, it helps prevent transplant rejection and reduce the risk of graft-versus-host disease.

Who makes Post-transplant Cyclophosphamide?

Post-transplant Cyclophosphamide is being developed by Meridian Bioscience Inc, which trades under the ticker VIVO. The company is conducting clinical trials to evaluate the drug's safety and efficacy in allogeneic stem cell transplant recipients.

What phase is Post-transplant Cyclophosphamide in?

Post-transplant Cyclophosphamide is in Phase 2 clinical development. It is an investigational drug and has not been approved by the FDA. The ongoing Phase 2 trial is currently recruiting participants to further evaluate its use in allogeneic stem cell transplantation.

What clinical trials is Post-transplant Cyclophosphamide in?

Post-transplant Cyclophosphamide is being studied in a Phase 2 clinical trial with the identifier NCT07214688. The trial, titled 'Fludarabine and Intermediate-dose TBI Followed by PTCy in Patients Undergoing Allo Transplant for Heme Malignancies,' is recruiting 209 participants in the United States. The study is uncontrolled and not blinded.

Is Post-transplant Cyclophosphamide the same as PTCy?

Yes, Post-transplant Cyclophosphamide is also known as PTCy. The abbreviation PTCy is commonly used in clinical research and medical literature to refer to this drug, particularly in the context of its use in allogeneic stem cell transplantation.