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Vosaroxin

Phase 3

Acute Myeloid Leukemia | Small molecule | Oncology |Viracta Therapeutics, Inc.|Last Updated: Oct 28, 2020

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment720
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01191801Study of Vosaroxin or Placebo in Combination With Cytarabine in Patients With First Relapsed or Refractory AMLPHASE3 COMPLETED 711Dec 17, 2010Mar 1, 2017Aug 22, 2018124 United States, Australia +13
NCT03338348Study of Vosaroxin With Azacitidine in Patients With Newly Diagnosed Acute Myeloid Leukemia or Myelodysplastic Syndrome With Excess Blasts-2PHASE2 COMPLETED 9Apr 19, 2018Oct 31, 2019Oct 28, 20203 Germany
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Study Endpoints
Primary Endpoints
Overall Survival
Up to 5 years or duration of study

Vosaroxin + cytarabine patient survival versus placebo + cytarabine patient survival

Rate of complete remission (CR) and CR with incomplete blood count recovery (CRi)
2 months

Efficacy assessments

Secondary Endpoints
Complete Remission (CR) Rate Based on Modified International Working Group (IWG) Criteria.
Up to 5 years or duration of study
All Cause Mortality
30 Days
CR and CRi in a pre-defined subgroup analysis in patients with complex karyotype
2 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Group A: vosaroxin + cytarabineEXPERIMENTALvosaroxin (short IV infusion within 10 minutes) on days 1 and 4: cytarabine on days 1 through 5; a maximum of 2 cycles of Induction and 2 cycles for Consolidation
Group B: placebo + cytarabinePLACEBO_COMPARATORplacebo (short IV infusion within 10 minutes and volume matched to vosaroxin) on days 1 and 4: cytarabine on days 1 through 5; a maximum of 2 cycles of Induction and 2 cycles for Consolidation
Azacitidine + VosaroxinOTHERCycle 1-8: Azacitidine: 75 mg/m²/d subcutaneously, d 1-7; Vosaroxin: Dose Level 0: 70mg/m², Dose Level -1: 50mg/m², Dose Level -2: 40mg/m², IV over ten minutes, d 1+4 . Patients who have completed 8 cycles of azacitidine and vosaroxin are scheduled to maintenance with single agent azacitidine at 75 mg/m²/d on days 1-7 until relapse or progression.
Interventions
NameTypeDescription
vosaroxin + cytarabineDRUGVosaroxin days 1 and 4: 90 mg/m2 for induction 1; 70 mg/m2 for all other cycles Cytarabine 1 g/m2 daily on days 1-5 (IDAC)
placebo + cytarabineDRUGPlacebo days 1 and 4: volume matched to vosaroxin Cytarabine 1 g/m2 daily on days 1-5 (IDAC)
VosaroxinDRUGCycle 1-8: Dose Level 0: 70mg/m², Dose Level -1: 50mg/m², Dose Level -2: 40mg/m², IV over ten minutes, d 1+4 .
AzacitidineDRUGCycle 1-8 Azacitidine: 75 mg/m²/d subcutaneously, d 1-7; Maintenance with single agent azacitidine at 75 mg/m²/d on days 1-7 until relapse or progression.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites124

Inclusion Criteria: * Provided signed, written informed consent * At least 18 years of age * Had a diagnosis of AML according to World Health Organization (WHO) classification * First relapsed or refractory AML (refractory to initial induction therapy) with at least 5% blasts by bone marrow or aspi...

Countries:United StatesAustraliaAustriaBelgiumCanadaCzechiaFranceGermanyHungaryItalyNew ZealandPolandSouth KoreaSpainUnited Kingdom
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