Recent Updates
Recently added Catalysts

TN-401

Phase 1

Arrhythmogenic Right Ventricular Cardiomyopathy | Gene therapy | Cardiovascular |Tenaya Therapeutics, Inc.|Last Updated: Feb 6, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment15
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT06228924Open-label, Dose Escalation Study of Safety and Preliminary Efficacy of TN-401 in Adults With PKP2 Mutation-associated ARVCPHASE1 RECRUITING 15Mar 26, 2024Oct 1, 2029Feb 6, 20257 United States
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Number and severity of Adverse Events over the course of the study.
52 weeks
Number of Serious Adverse Events related to study drug.
5 years
Secondary Endpoints
To assess changes in daily PVC and NSVT counts
Week 52
To assess frequency of ICD therapy administration
Week 52
To assess frequency of sustained VT
Week 52
Unlock Study Endpoints
Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Cohort 1EXPERIMENTALDose for Cohort 1 will be 3E13 vg/kg
Cohort 2EXPERIMENTALDose for Cohort 2 will be 6E13 vg/kg
Interventions
NameTypeDescription
TN-401GENETICTN-401 is a recombinant adeno-associated virus serotype 9 (AAV9) gene therapy containing Plakophilin-2 (PKP2) transgene. It is a single (one-time) intravenous dose.
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — 65 Years
SexALL
Healthy VolunteersNo
Study Sites7

Inclusion Criteria: * PKP2 mutation (pathogenic or likely pathogenic) * Arrhythmogenic Right Ventricular Cardiomyopathy as defined by the 2010 revised Task Force Criteria * Left Ventricular Ejection Fraction ≥50% * Functioning Implantable Cardiac Defibrillator with remote integration capabilities a...

Countries:United States
Unlock Eligibility Criteria
Competitive Landscape -Arrhythmogenic Right Ventricular Cardiomyopathy 3 trials
CompanyTickerTrialsLead PhaseDrugs
Lexeo Therapeutics, Inc.LXEO3PHASE1LX2020
Unlock Competitive Intelligence
Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT06228924primaryCompletionDate: changed
LOWMay 24, 2026NCT06228924studyFirstPostDate: changed