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ASCs

Phase 3

Anal Fistula | Small molecule | Other |Takeda Pharmaceutical Company Limited|Last Updated: Apr 12, 2019

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLEDBiomarker
Total Trials1
Total Enrollment214

FDA Designations

No designations recorded

Clinical trial landscape

ASCs · 1 trial · 1 indication

Phase 3 1
NCT00475410Efficacy and Safety of Adipose Stem Cells to Treat Complex Perianal Fistulas Not Associated to Crohn´s DiseaseAnal Fistula
COMPLETED214 Analytics
PHASE3COMPLETED
Efficacy and Safety of Adipose Stem Cells to Treat Complex Perianal Fistulas Not Associated to Crohn´s Disease
Anal FistulaUnlock trial analytics

Study Endpoints

Primary Endpoints

Closure of fistulas defined as absence of suppuration and re-epithelization of the external opening and absence of collections>2 cm directly related to the fistula tract treated, as measured by MRI (healing)
weeks 1, 4, 12 and 24. Week 26 in patients with a second dose

Secondary Endpoints

• Clinical complexity of fistula (complexity of fistula score) • Safety: Cumulative incidence of adverse effects. • Quality of life (SF-36 score) • Degree of anal incontinence (Wexner incontinence score)
weeks 1, 4, 12 and 24. Week 26 in patients with a second dose
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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
ASCsEXPERIMENTAL -
ASCs+fibrin glueEXPERIMENTAL -
Fibrin glueACTIVE_COMPARATOR -

Interventions

NameTypeDescription
ASCs (Cx401, company code)DRUGExperimental: ASCs: Subjects will be treated with a dose of 20 million ASCs and evaluated after 12 weeks. If needed a second dose of 40 million ASCs will be applied then. Experimental: ASCs+fibrin glue: Subjects will be treated with a dose of 20 million ASCs plus fibrin glue and evaluated after 12 weeks. If needed a second dose of 40 million ASCs plus fibrin glue will be applied then.
Fibrin adhesiveDRUGExperimental: Fibrin glue: Subjects will be treated with a dose fibrin glue and evaluated after 12 weeks. If needed a second dose of fibrin glue will be applied then.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites10

Inclusion Criteria: 1. Patient with a complex perianal fistula. A complex perianal fistula must meet one of the following: * No fistula tract is palpated under the perianal skin or tract parallel to the rectum on examination with a stylet. * Associated anal incontinence in transsphincteric f...

Countries:GermanySpainUnited Kingdom
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Competitive Landscape -Fistula Disorders 2 trials (matched to "Anal Fistula")

Frequently asked questions about ASCs

What is ASCs used for in Anal Fistula?

ASCs are used to treat complex perianal fistulas not associated with Crohn's disease. The therapy is being developed as a treatment for anal fistula, a condition involving an abnormal tract between the anal canal and the perianal skin. ASCs are administered to promote healing and closure of the fistula tract.

What does ASCs target?

ASCs, or adipose-derived stem cells, are a cell-based therapy that targets the local inflammatory and tissue repair processes in anal fistula. The stem cells are derived from adipose tissue and are intended to modulate the immune response and promote tissue regeneration at the fistula site, aiding in closure and healing.

Who makes ASCs?

ASCs are being developed by Takeda Pharmaceutical Company Limited, a global biopharmaceutical company headquartered in Japan. Takeda's stock is traded under the ticker symbol TAK on the New York Stock Exchange. The company is conducting clinical development of ASCs for the treatment of anal fistula.

What phase is ASCs in?

ASCs are in Phase 3 clinical development for the treatment of anal fistula. The therapy is investigational and has not yet been approved by regulatory authorities. A Phase 3 trial has been completed to evaluate the efficacy and safety of ASCs in patients with complex perianal fistulas not associated with Crohn's disease.

What clinical trials is ASCs in?

ASCs have been studied in one completed Phase 3 clinical trial, identified by the National Clinical Trial number NCT00475410. The trial, titled 'Efficacy and Safety of Adipose Stem Cells to Treat Complex Perianal Fistulas Not Associated to Crohn´s Disease,' enrolled 214 participants across Germany, Spain, and the United Kingdom. The study was randomized, double-blind, and active-controlled.

Is ASCs the same as adipose-derived stem cells?

Yes, ASCs is an abbreviation for adipose-derived stem cells. In the context of this therapy, ASCs refer to stem cells derived from adipose tissue that are being investigated for the treatment of anal fistula. The clinical trial NCT00475410 specifically evaluates the efficacy and safety of adipose stem cells for complex perianal fistulas.