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Co-ArgI-PEG

Phase 1

Advanced Cancers | Small molecule | Oncology |Spyre Therapeutics, Inc.|Last Updated: Nov 5, 2021

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDBiomarker
Total Trials1
Total Enrollment98
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02561234A Multiple Dose, Dose Escalation Trial of AEB1102 in Patients With Advanced Solid TumorsPHASE1 COMPLETED 98Oct 1, 2015May 1, 2019Nov 5, 202111 United States
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Study Endpoints
Primary Endpoints
maximum tolerated dose
4 weeks

the dose level at which no more than 1/6 patients experiences dose-limiting toxicity

Secondary Endpoints
safety profile (changes in physical exam, laboratory measures, reported adverse events)
4 weeks +
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
AEB1102 Dose Escalation Cohort 1EXPERIMENTAL3 patients dosed at 0.01 mg/kg until MTD determined
AEB1102 Dose Escalation Cohort 2EXPERIMENTAL4 patients dosed at 0.02 mg/kg until MTD determined
AEB1102 Dose Escalation Cohort 3EXPERIMENTAL4 patients dosed at 0.04 mg/kg until MTD determined
AEB1102 Dose Escalation Cohort 4EXPERIMENTAL4 patients dosed at 0.08 mg/kg until MTD determined
AEB1102 Dose Escalation Cohort 5EXPERIMENTAL3 patients dosed at 0.12 mg/kg until MTD determined
AEB1102 Dose Escalation Cohort 6EXPERIMENTAL4 patients dosed at 0.18 mg/kg until MTD determined
AEB1102 Dose Escalation Cohort 7EXPERIMENTAL5 patients dosed at 0.27 mg/kg until MTD determined
AEB1102 Dose Escalation Cohort 8EXPERIMENTAL7 patients dosed at 0.40 mg/kg until MTD determined
AEB1102 Dose Escalation Cohort 9EXPERIMENTAL7 patients dosed at 0.33 mg/kg until MTD determined MTD determined at 0.33 mg/kg
AEB1102 ExpansionEXPERIMENTALUveal: 11 patients dosed at 0.33 mg/kg Cutaneous Melanoma: 11 dosed at 0.33 mg/kg SCLC: 13 patients dosed at 0.33 mg/kg
Interventions
NameTypeDescription
Co-ArgI-PEGDRUGAdministered IV
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites11

Inclusion Criteria: For patients participating in any part of the trial: * has an advanced solid tumor previously treated with, or inability to tolerate, standard therapy for the disease, or for which a standard therapy does not exist, and as such is considered a candidate for Phase 1 treatment * ...

Countries:United States
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