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rilzabrutinib

Phase 3

Immunoglobulin G4 Related Disease | Small molecule | Other |Sanofi|Last Updated: Jun 2, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindACTIVE_CONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment151
FDA Designations
ORPHAN_DRUGFAST_TRACK
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07190196A 52-week Study of Rilzabrutinib Efficacy and Safety Compared to Placebo in Adults Diagnosed With IgG4-related DiseasePHASE3 RECRUITING 124Sep 26, 2025Dec 25, 2030Jun 2, 202676 United States, Argentina +17
NCT04520451Open Label Two-Arm Study to Evaluate Rilzabrutinib in IgG4-Related Disease ParticipantsPHASE2 COMPLETED 27Aug 22, 2020Oct 15, 2024Oct 14, 20259 United States, Canada +3
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Study Endpoints
Primary Endpoints
Time to first adjudicated clinical disease flare treated by the investigator during the Blinded Treatment period
Until Week 52

The Adjudication Committee will include internationally recognized independent experts in diagnosis and management of patients with IgG4-RD, blinded to participant, investigator, and site identifiers

Proportion of participants who are without disease flare following the first dose of rilzabrutinib until the end of treatment
Up to 64 weeks

Disease flare is defined as an increase in IgG4-RD responder index (RI) \>2 or initiation of rescue treatment.

Incidence of SAE, AE leading to discontinuation and possible glucocorticoid-related AE
Up to 68 weeks
Number of participants with Potentially clinically significant abnormalities (PCSAs) for clinical laboratory tests, vital signs and ECG
Up to 68 weeks
Secondary Endpoints
Percentage of participants without IgG4-RD adjudicated clinical disease flare and off glucocorticoids and immunomodulators
At Week 52
Percentage of participants without IgG4-RD adjudicated clinical disease flare and off glucocorticoids
At Week 52
Annualized rate of clinical disease flares
At Week 52
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
RilzabrutinibEXPERIMENTALRilzabrutinib
PlaceboPLACEBO_COMPARATORPlacebo
Rilzabrutinib + glucocorticoidsEXPERIMENTALRilzabrutinib tablets, 400 mg twice daily from Week 0 to Week 12 plus glucocorticoids (20 to 40 mg/day prednisone equivalent tapered to 0 mg/day within 2 weeks on study)
GlucocorticoidsACTIVE_COMPARATORGlucocorticoids (20 to 40 mg/day prednisone equivalent tapered to 0 mg/day within 12 weeks on study)
Interventions
NameTypeDescription
RilzabrutinibDRUGPharmaceutical form:Tablet-Route of administration:Oral
PlaceboDRUGPharmaceutical form:Tablet-Route of administration:Oral
GlucocorticoidDRUGPharmaceutical form:Tablet, solution, suspension formulations according to local standard practices-Route of administration:Oral
GlucocorticoidsDRUGoral tablet or capsule
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites76

Inclusion Criteria: * Participants must have an adjudicated clinical diagnosis of IgG4-RD * Participants meeting Step 1 Entry criteria of 2019 ACR/EULAR classification criteria for IgG4-RD and Total inclusion points are ≥20 * Participants with active disease at screening in at least one organ syste...

Countries:United StatesArgentinaBelgiumCanadaChileChinaFranceGermanyIsraelItalyJapanNetherlandsPolandSaudi ArabiaSouth KoreaSpainSwedenTaiwanUnited Kingdom
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Recent Changes (Last 90 Days)
LOWJun 2, 2026NCT07190196lastUpdatePostDate: changed
LOWJun 2, 2026NCT07190196lastUpdatePostDate: changed
LOWJun 2, 2026NCT07190196lastUpdatePostDate: changed
LOWMay 26, 2026NCT07190196primaryCompletionDate: changed
LOWMay 24, 2026NCT07190196studyFirstPostDate: changed