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Riliprubart

Phase 3

Chronic Inflammatory Demyelinating Polyradiculoneuropathy | Small molecule | Neurology |Sanofi|Last Updated: Aug 26, 2026

Target and mechanism

ModalitySmall molecule

Also known as Riliprubart Prefilled Pen (PFP), Riliprubart Prefilled Pen

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment109

FDA Designations

ORPHAN_DRUG

Clinical trial landscape

Riliprubart · 2 trials · 3 indications

Phase 3 2
NCT06290141A Study to Test the Efficacy and Safety of Riliprubart Against the Usual Treatment of Intravenous Immunoglobulin (IVIg) in People With Chronic Inflammatory Demyelinating Polyneuropathy (CIDP)Chronic Inflammatory Demyelinating Polyneuropathy
RECRUITING160 Analytics
NCT06290128A Study to Test the Effects and Safety of Riliprubart in People With Chronic Inflammatory Demyelinating Polyneuropathy (CIDP) for Which the Usual Treatments do Not WorkChronic Inflammatory Demyelinating Polyradiculoneuropathy
ACTIVE NOT_RECRUITING109 Analytics
PHASE3RECRUITING
A Study to Test the Efficacy and Safety of Riliprubart Against the Usual Treatment of Intravenous Immunoglobulin (IVIg) in People With Chronic Inflammatory Demyelinating Polyneuropathy (CIDP)
Chronic Inflammatory Demyelinating PolyneuropathyUnlock trial analytics
PHASE3ACTIVE NOT_RECRUITING
A Study to Test the Effects and Safety of Riliprubart in People With Chronic Inflammatory Demyelinating Polyneuropathy (CIDP) for Which the Usual Treatments do Not Work
Chronic Inflammatory Demyelinating PolyradiculoneuropathyUnlock trial analytics

Study Endpoints

Primary Endpoints

Percentage of participants experiencing a response
Baseline to week 24

A response is defined as decrease of ≥1 point from baseline in adjusted INCAT disability score at Week 24

Percentage of participants randomized to riliprubart who responded during part A and had a lasting response during the open-label treatment extension period
Baseline to week 48

Lasting response is defined as a decrease of ≥1 point in adjusted INCAT disability score

Percentage of participants randomized to riliprubart with lasting response
Baseline to week 48

Lasting response is defined as a decrease of ≥1 point in adjusted INCAT disability score at week 48 versus baseline.

Percentage of participants randomized to placebo who experience a response
Week 24 to week 48

A response is defined as a decrease of ≥1 point in adjusted INCAT disability score at Week 48 versus week 24.

Secondary Endpoints

Change from baseline in Rasch-built Overall Disability Scale (I-RODS) score
Baseline to week 24
Change from baseline in adjusted inflammatory neuropathy cause and treatment (INCAT) disability score
Baseline to week 24
Change from baseline in grip strength (kilopascals, dominant hand)
Baseline to week 24
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Riliprubart ArmEXPERIMENTALRiliprubart + Placebo IVIg for 24 weeks followed by open-label extension phase with riliprubart for 24 weeks
IVIg ArmACTIVE_COMPARATORIVIg (IVIg continuation) + Placebo riliprubart for 24 weeks followed by open-label extension phase with riliprubart for 24 weeks
Placebo ArmPLACEBO_COMPARATORPlacebo for 24 weeks followed by open-label extension phase with riliprubart for 24 weeks

Interventions

NameTypeDescription
riliprubartDRUGPharmaceutical form: Solution Route of administration: IV solution
PlaceboDRUGPharmaceutical form: Solution Route of administration: IV solution
IVIgDRUGPharmaceutical form: Concentrate for solution for infusion (or any other formulation approved locally) Route of administration: IV solution
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites135

Inclusion Criteria: Participants are eligible to be included in the study only if all of the following criteria apply: * Participant must have CIDP or possible CIDP criteria, based on European Academy of Neurology (EAN)/Peripheral Nerve Society (PNS) Task Force CIDP guidelines, second revision (20...

Countries:United StatesArgentinaBelgiumBrazilCanadaChinaCzechiaDenmarkFranceGermanyGreeceHungaryIsraelItalyJapanMexicoNorwayPortugalSpainSwedenSwitzerlandTaiwanTurkey (Türkiye)United KingdomBulgariaChileNetherlandsPolandSouth Korea
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Recent Changes (Last 90 Days)

LOWAug 26, 2026NCT06290141lastUpdatePostDate: changed
LOWAug 26, 2026NCT06290141lastUpdatePostDate: changed
HIGHAug 11, 2026NCT06290128Status: RECRUITING → ACTIVE_NOT_RECRUITING
HIGHAug 11, 2026NCT06290128Status: RECRUITING → ACTIVE_NOT_RECRUITING
HIGHAug 11, 2026NCT06290128Status: RECRUITING → ACTIVE_NOT_RECRUITING
LOWJul 29, 2026NCT06290141lastUpdatePostDate: changed
LOWJul 29, 2026NCT06290141lastUpdatePostDate: changed
LOWJul 13, 2026NCT06290141lastUpdatePostDate: changed
LOWJul 13, 2026NCT06290141lastUpdatePostDate: changed
LOWJun 16, 2026NCT06290141lastUpdatePostDate: changed
LOWJun 16, 2026NCT06290141lastUpdatePostDate: changed
LOWJun 16, 2026NCT06290141lastUpdatePostDate: changed
LOWJun 16, 2026NCT06290141lastUpdatePostDate: changed
LOWJun 12, 2026NCT06290128lastUpdatePostDate: changed
LOWJun 12, 2026NCT06290128lastUpdatePostDate: changed

Frequently asked questions about Riliprubart

What is Riliprubart used for?

Riliprubart is an investigational small molecule being developed for chronic inflammatory demyelinating polyneuropathy (CIDP), also known as chronic inflammatory demyelinating polyradiculoneuropathy. It is being studied in adults aged 18 years and older whose usual treatments do not work, as well as in comparison to standard intravenous immunoglobulin (IVIg) therapy.

Who is developing Riliprubart?

Riliprubart is being developed by Sanofi, a global biopharmaceutical company listed on the stock exchange under the ticker SNY. The drug is currently in Phase 3 clinical development for chronic inflammatory demyelinating polyneuropathy (CIDP).

What phase is Riliprubart in?

Riliprubart is in Phase 3 clinical development. It is an investigational drug, meaning it has not been approved by regulatory authorities. It has received orphan drug designation from the FDA for the treatment of chronic inflammatory demyelinating polyneuropathy (CIDP).

What clinical trials is Riliprubart in?

Riliprubart is being studied in three Phase 3 trials. NCT06290128 is an active, not recruiting study in CIDP patients for whom usual treatments do not work. NCT06290141 is recruiting and compares Riliprubart to IVIg. NCT06859099 is an enrolling-by-invitation long-term safety and efficacy study. All trials are randomized, double-blind, and placebo-controlled.

Is Riliprubart the same as Riliprubart Prefilled Pen?

Yes, Riliprubart is also known as Riliprubart Prefilled Pen (PFP) or Riliprubart Prefilled Pen. These names refer to the same drug product, which is being developed by Sanofi for chronic inflammatory demyelinating polyneuropathy (CIDP).

What is the enrollment and design of Riliprubart trials?

The Riliprubart Phase 3 program includes trials with enrollment of 109, 160, and 300 participants across multiple countries including the United States, Canada, Japan, and European nations. The trials are randomized, double-blind, and placebo-controlled, with a minimum participant age of 18 years.