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riferminogene pecaplasmid

Phase 3

Peripheral Vascular Diseases | Monoclonal antibody | Other |Sanofi|Last Updated: May 2, 2016

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment525
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00566657Efficacy and Safety of XRP0038/NV1FGF in Critical Limb Ischemia Patients With Skin LesionsPHASE3 COMPLETED 525Nov 1, 2007Aug 1, 2012May 2, 201632 United States, Argentina +30
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Study Endpoints
Primary Endpoints
Time to major amputation of the treated leg or death from any cause, whichever comes first
From randomization up to 12 months
Secondary Endpoints
Time to first major amputation of the treated leg
From randomization up to 12 months
Time to death from any cause
From randomization up to 12 months
Number of participants with adverse events as a measure of safety
From 1st treatment administration up to death, or the earliest of Day 360 or last contact/assessment
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Riferminogene pecaplasmidEXPERIMENTAL4 administrations of riferminogene pecaplasmid 4 mg at 2-week intervals
PlaceboPLACEBO_COMPARATOR4 administrations of placebo (for riferminogene pecaplasmid) at 2-week intervals
Interventions
NameTypeDescription
riferminogene pecaplasmidBIOLOGICALFormulation: 5 ml glass vials containing 2,5 ml riferminogene pecaplasmid Route: intramuscular (IM) injection of 2.5 mL in the ischemic leg to be treated
Placebo (for riferminogene pecaplasmid)BIOLOGICALFormulation: 5 ml glass vials containing 2,5 ml placebo Route: IM injection of 2.5 mL in the ischemic leg to be treated
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Eligibility Criteria
Age Range50 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites32

Inclusion Criteria: * Having peripheral artery disease at the stage of Critical Limb Ischemia (CLI) with skin lesions (either ulcer(s) or gangrene); * With objective evidence of CLI such as ankle systolic pressure \<70 mmHg and/or toe systolic pressure \<50 mmHg or transcutaneous oxygen pressure (T...

Countries:United StatesArgentinaAustraliaAustriaBelarusBelgiumBrazilCanadaChileCzechiaDenmarkEstoniaFinlandFranceGermanyGreeceHong KongHungaryItalyJapanMexicoPolandRussiaSingaporeSouth AfricaSouth KoreaSpainSwedenSwitzerlandTurkey (Türkiye)UkraineUnited Kingdom
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