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alemtuzumab GZ402673

Phase 1

Progressive Multiple Sclerosis | Small molecule | Immunology |Sanofi|Last Updated: Mar 10, 2021

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDBiomarker
Total Trials1
Total Enrollment24
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02583594A Study to Characterize Subcutaneous or Intravenous Alemtuzumab in Patients With Progressive Multiple SclerosisPHASE1 COMPLETED 24Dec 6, 2015Mar 1, 2021Mar 10, 20211 Spain
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Study Endpoints
Primary Endpoints
Change from baseline in the CD3+ lymphocyte subset after alemtuzumab administration
Baseline, 30 days after each treatment course
Secondary Endpoints
Change from baseline in lymphocyte subsets after alemtuzumab administration
Baseline, 30 days after each treatment course
Change from baseline in total lymphocyte count after alemtuzumab administration
Baseline, 30 days after each treatment course
Change from baseline in helper/suppressor ratio after alemtuzumab administration
Baseline, 30 days after each treatment course
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
alemtuzumab (subcutaneous injection)EXPERIMENTALDose 1 (initial course) of alemtuzumab will be administered subcutaneously on 5 consecutive days, followed by Dose 2 (second course) on 3 consecutive days administered 12 months after initial course. Pre-medications (methylprednisolone, antihistamine \[loratadine, cetirizine, dexchlorpheniramine\], paracetamol, acyclovir) will be administered prior alemtuzumab administration.
alemtuzumab (intravenous infusion)EXPERIMENTALDose 1 (initial course) of alemtuzumab will be administered intravenously on 5 consecutive days, followed by Dose 2 (second course) on 3 consecutive days administered 12 months after initial course. Pre-medications (methylprednisolone, antihistamine \[loratadine, cetirizine, dexchlorpheniramine\], paracetamol, acyclovir) will be administered prior alemtuzumab administration.
Interventions
NameTypeDescription
AcyclovirDRUGPharmaceutical form:tablet Route of administration: oral
MethylprednisoloneDRUGPharmaceutical form:tablet Route of administration: oral
alemtuzumab GZ402673DRUGPharmaceutical form:solution for infusion Route of administration: intravenous
ParacetamolDRUGPharmaceutical form:tablet Route of administration: oral
LoratadineDRUGPharmaceutical form:tablet Route of administration: oral
CeterizineDRUGPharmaceutical form:tablet Route of administration: oral
DexchlorpheniramineDRUGPharmaceutical form:tablet Route of administration: oral
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion criteria: * Male or female adults with a diagnosis of Multiple Sclerosis (MS) based on 2010 revision of McDonald criteria. * Diagnosis of progressive MS including primary progressive MS and secondary progressive MS. * Age ≥18 years. * Signed informed consent form. * Covered by a health in...

Countries:Spain
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