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Venglustat GZ/SAR402671

Phase 1

Healthy Volunteers | Small molecule | Nephrology |Sanofi|Last Updated: Apr 25, 2022

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment24
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03687554Effect of Venglustat in Patients With Renal ImpairmentPHASE1 COMPLETED 24Oct 5, 2018Feb 27, 2019Apr 25, 20221 United States
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Study Endpoints
Primary Endpoints
Assessment of pharmacokinetic (PK) parameters of Venglustat: Area under the curve (AUC)
Day 1 to Day 10

Venglustat area under the plasma concentration versus time curve (AUC)

Secondary Endpoints
Venglustat plasma pharmacokinetic (PK) parameter: Cmax
Day 1
Venglustat plasma pharmacokinetic (PK) parameter: AUClast
Day 1 to Day 10
Venglustat plasma pharmacokinetic (PK) parameter: unbound Cmax
Day 1 to Day 10
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
VenglustatEXPERIMENTALSingle dose of Venglustat is given, orally under fasting conditions
Interventions
NameTypeDescription
Venglustat GZ/SAR402671DRUGPharmaceutical form: Hard Capsule Route of administration: Oral
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Eligibility Criteria
Age Range18 Years — 79 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion criteria: For all Subjects: * Male and/or female subjects, between 18 and 79 years of age, inclusive. * Body weight between 50.0 and 115.0 kg, inclusive, if male, and between 40.0 and 100.0 kg, inclusive, if female, body mass index between 18.0 and 34.9 kg/m2, inclusive * Normal electroc...

Countries:United States
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