Recent Updates
Recently added Catalysts

SAR103168

Phase 1

Acute Myelogenous Leukemia | Small molecule | Oncology |Sanofi|Last Updated: Mar 27, 2012

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment30
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00981240Dose Escalation, Safety and Pharmacokinetic Study of SAR103168 in Patients Refractory/ Relapsed Acute Leukemias or High-risk Myelodysplastic SyndromesPHASE1 COMPLETED 30Sep 1, 2009Feb 1, 2012Mar 27, 20123 United States
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Incidence of DLTs during the initial 4-week period of treatment
4 weeks
Pharmacokinetic parameters of SAR103168
First course: Days 1, 2, 5, 6, and 8; Second and subsequent courses: Day 5 only
Secondary Endpoints
Global safety profile of SAR103168 based on treatment emergent adverse events (TEAEs), serious adverse events (SAEs), deaths, laboratory abnormalities
Treatment period up to 1 year
Preliminary evidence of anti-leukemia activity
Treatment period up to 1 year
Pharmacokinetic parameters of midazolam in the absence and the presence of SAR103168.
During second (Day-1 and Day 5) and forth course (Day 5)
Unlock Study Endpoints
Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Dose escalationEXPERIMENTALCohorts of 3 to 6 patients will be included at each dose level. The starting dose is 1.2mg/m2/day. The dose will be increased in new cohorts of patients according to toxicities observed during the first 4-week treatment period. The escalation process will continue until the MTD is determined. Additional 15 patients will be included at the MTD.
Interventions
NameTypeDescription
SAR103168DRUGPharmaceutical form: Concentrate for solution for infusion Route of administration: Intravenous infusion
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites3

Inclusion Criteria: * Patients with refractory/relapsed acute leukemias or high-risk myelodysplastic syndromes with no curative option available including any of the following: * Patients with de novo or secondary acute myelogenous leukemia (AML) (except acute promyelocytic leukemia), meeting on...

Countries:United States
Unlock Eligibility Criteria